CA3005246A1 - Compositions and methods for treatment of central nervous system diseases - Google Patents
Compositions and methods for treatment of central nervous system diseases Download PDFInfo
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- CA3005246A1 CA3005246A1 CA3005246A CA3005246A CA3005246A1 CA 3005246 A1 CA3005246 A1 CA 3005246A1 CA 3005246 A CA3005246 A CA 3005246A CA 3005246 A CA3005246 A CA 3005246A CA 3005246 A1 CA3005246 A1 CA 3005246A1
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| GB201410693D0 (en) | 2014-06-16 | 2014-07-30 | Univ Southampton | Splicing modulation |
| CN107109411B (zh) | 2014-10-03 | 2022-07-01 | 冷泉港实验室 | 核基因输出的定向增加 |
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| US4866042A (en) | 1987-11-18 | 1989-09-12 | Neuwelt Edward A | Method for the delivery of genetic material across the blood brain barrier |
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| US20140128449A1 (en) * | 2011-04-07 | 2014-05-08 | The Board Of Regents Of The University Of Texas System | Oligonucleotide modulation of splicing |
| AU2012272656A1 (en) * | 2011-06-23 | 2014-02-06 | Cold Spring Harbor Laboratory | Phenocopy model of disease |
| ES2626488T3 (es) | 2011-07-19 | 2017-07-25 | Wave Life Sciences Pte. Ltd. | Procedimientos para la síntesis de ácidos nucleicos funcionalizados |
| PL3041958T3 (pl) | 2013-09-04 | 2020-11-02 | Cold Spring Harbor Laboratory | Redukcja rozpadu mRNA mediowanego sekwencjami nonsensownymi |
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| EP3389725A1 (en) | 2018-10-24 |
| EP3389725A4 (en) | 2019-04-10 |
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