TW202313975A - 反義核酸 - Google Patents

反義核酸 Download PDF

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Publication number
TW202313975A
TW202313975A TW111119953A TW111119953A TW202313975A TW 202313975 A TW202313975 A TW 202313975A TW 111119953 A TW111119953 A TW 111119953A TW 111119953 A TW111119953 A TW 111119953A TW 202313975 A TW202313975 A TW 202313975A
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TW
Taiwan
Prior art keywords
oligonucleotide
acceptable salt
pharmaceutically acceptable
base sequence
aforementioned
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TW111119953A
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English (en)
Chinese (zh)
Inventor
満智秋
浅野成宏
日野恭介
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日商住友製藥股份有限公司
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Publication of TW202313975A publication Critical patent/TW202313975A/zh

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    • C12N9/16Hydrolases (3) acting on ester bonds (3.1)
    • AHUMAN NECESSITIES
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    • C12N15/09Recombinant DNA-technology
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    • C12N15/113Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides; Antisense DNA or RNA; Triplex- forming oligonucleotides; Catalytic nucleic acids, e.g. ribozymes; Nucleic acids used in co-suppression or gene silencing
    • C12N15/1137Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides; Antisense DNA or RNA; Triplex- forming oligonucleotides; Catalytic nucleic acids, e.g. ribozymes; Nucleic acids used in co-suppression or gene silencing against enzymes
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    • C12Y306/00Hydrolases acting on acid anhydrides (3.6)
    • C12Y306/04Hydrolases acting on acid anhydrides (3.6) acting on acid anhydrides; involved in cellular and subcellular movement (3.6.4)
    • C12Y306/04012DNA helicase (3.6.4.12)

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  • Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
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TW111119953A 2021-05-28 2022-05-27 反義核酸 TW202313975A (zh)

Applications Claiming Priority (2)

Application Number Priority Date Filing Date Title
JP2021090359 2021-05-28
JP2021-090359 2021-05-28

Publications (1)

Publication Number Publication Date
TW202313975A true TW202313975A (zh) 2023-04-01

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ID=84228935

Family Applications (1)

Application Number Title Priority Date Filing Date
TW111119953A TW202313975A (zh) 2021-05-28 2022-05-27 反義核酸

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US (1) US20250084411A1 (https=)
EP (1) EP4349987A1 (https=)
JP (1) JPWO2022250155A1 (https=)
KR (1) KR20240013202A (https=)
CN (1) CN117500925A (https=)
AU (1) AU2022279820A1 (https=)
CA (1) CA3221758A1 (https=)
MX (1) MX2023014092A (https=)
TW (1) TW202313975A (https=)
WO (1) WO2022250155A1 (https=)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP4342498A4 (en) * 2021-05-13 2025-01-08 National University Corporation Chiba University ANTISENSE OLIGOMER

Family Cites Families (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
JP3398378B2 (ja) 1989-12-20 2003-04-21 アンチビラルス・インコーポレイテツド リン含有キラルインターサブユニットリンケージを有する非電荷モルホリノ―基体ポリマー
MX2010004955A (es) 2007-11-15 2010-06-30 Avi Biopharma Inc Metodo de sintesis de oligomeros de morfolina.
CN112574988A (zh) * 2008-10-24 2021-03-30 萨雷普塔治疗公司 用于dmd的多外显子跳跃组合物
AU2010312751B2 (en) 2009-10-29 2014-07-24 Osaka University Bridged artificial nucleoside and nucleotide
US10377789B2 (en) 2012-09-21 2019-08-13 Osaka University Oligonucleotide and artificial nucleoside having guanidine bridge
WO2015125783A1 (ja) 2014-02-18 2015-08-27 国立大学法人大阪大学 架橋型ヌクレオシドおよびヌクレオチド

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JPWO2022250155A1 (https=) 2022-12-01
AU2022279820A1 (en) 2023-12-14
EP4349987A1 (en) 2024-04-10
CN117500925A (zh) 2024-02-02
KR20240013202A (ko) 2024-01-30
CA3221758A1 (en) 2022-12-01
WO2022250155A1 (ja) 2022-12-01
MX2023014092A (es) 2023-12-11
AU2022279820A9 (en) 2024-01-04
US20250084411A1 (en) 2025-03-13

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