TW202110486A - 使用糖苷水解酶改善基因療法載體向視網膜細胞的遞送 - Google Patents

使用糖苷水解酶改善基因療法載體向視網膜細胞的遞送 Download PDF

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TW202110486A
TW202110486A TW109112715A TW109112715A TW202110486A TW 202110486 A TW202110486 A TW 202110486A TW 109112715 A TW109112715 A TW 109112715A TW 109112715 A TW109112715 A TW 109112715A TW 202110486 A TW202110486 A TW 202110486A
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composition
cells
gene therapy
glycoside hydrolase
gene
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TW109112715A
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凱瑟琳 克莉絲汀 梅爾
許畢 萊凱特
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美國全美兒童醫院之研究學會
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    • C12Y302/01129—Endo-alpha-sialidase (3.2.1.129)
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    • C12N2750/00011—Details
    • C12N2750/14011—Parvoviridae
    • C12N2750/14111—Dependovirus, e.g. adenoassociated viruses
    • C12N2750/14171—Demonstrated in vivo effect

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  • Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
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TW109112715A 2019-05-17 2020-04-15 使用糖苷水解酶改善基因療法載體向視網膜細胞的遞送 TW202110486A (zh)

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US201962849794P 2019-05-17 2019-05-17
US62/849,794 2019-05-17

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US (2) US20220233655A1 (enExample)
EP (2) EP3969060A1 (enExample)
JP (2) JP2022533645A (enExample)
KR (1) KR20220009427A (enExample)
CN (1) CN114126667A (enExample)
AR (1) AR118696A1 (enExample)
AU (2) AU2020278960A1 (enExample)
CA (2) CA3141017A1 (enExample)
TW (1) TW202110486A (enExample)
WO (2) WO2020236351A1 (enExample)

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KR20260045918A (ko) * 2019-12-25 2026-04-03 루머스 리미티드 도광 광학 엘리먼트와 연관된 광학 배열체를 사용하여 눈으로부터 광을 방향 전환시키는 것에 기초한 시선 추적을 위한 광학계 및 방법
CN114516901B (zh) * 2022-03-11 2023-01-17 上海勉亦生物科技有限公司 一种神经系统高亲和性的aav载体及其应用
CN115323001B (zh) * 2022-07-28 2024-11-26 深圳先进技术研究院 一种靶向视网膜的基因递送系统及其应用

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EP3969060A1 (en) 2022-03-23
AR118696A1 (es) 2021-10-27
JP7707081B2 (ja) 2025-07-14
JP2022533645A (ja) 2022-07-25
AU2020278499A1 (en) 2022-01-06
KR20220009427A (ko) 2022-01-24
WO2020236351A1 (en) 2020-11-26
EP3969059A1 (en) 2022-03-23
US20220233655A1 (en) 2022-07-28
CN114126667A (zh) 2022-03-01
CA3141017A1 (en) 2020-11-26
WO2020236352A1 (en) 2020-11-26
CA3141020A1 (en) 2020-11-26
AU2020278960A1 (en) 2021-12-23
JP2022533983A (ja) 2022-07-27
US20220226507A1 (en) 2022-07-21

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