SG11202001707PA - Methods of enhancing and/or stabilizing cardiac function in patients with fabry disease - Google Patents

Methods of enhancing and/or stabilizing cardiac function in patients with fabry disease

Info

Publication number
SG11202001707PA
SG11202001707PA SG11202001707PA SG11202001707PA SG11202001707PA SG 11202001707P A SG11202001707P A SG 11202001707PA SG 11202001707P A SG11202001707P A SG 11202001707PA SG 11202001707P A SG11202001707P A SG 11202001707PA SG 11202001707P A SG11202001707P A SG 11202001707PA
Authority
SG
Singapore
Prior art keywords
patients
enhancing
methods
cardiac function
fabry disease
Prior art date
Application number
SG11202001707PA
Other languages
English (en)
Inventor
Jeff Castelli
Jay Barth
Nina Skuban
Original Assignee
Amicus Therapeutics Inc
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Amicus Therapeutics Inc filed Critical Amicus Therapeutics Inc
Publication of SG11202001707PA publication Critical patent/SG11202001707PA/en

Links

Classifications

    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61KPREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K31/00Medicinal preparations containing organic active ingredients
    • A61K31/33Heterocyclic compounds
    • A61K31/395Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins
    • A61K31/435Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins having six-membered rings with one nitrogen as the only ring hetero atom
    • A61K31/44Non condensed pyridines; Hydrogenated derivatives thereof
    • A61K31/445Non condensed piperidines, e.g. piperocaine
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61PSPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P43/00Drugs for specific purposes, not provided for in groups A61P1/00-A61P41/00
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61PSPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P9/00Drugs for disorders of the cardiovascular system
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61PSPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P9/00Drugs for disorders of the cardiovascular system
    • A61P9/04Inotropic agents, i.e. stimulants of cardiac contraction; Drugs for heart failure
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61KPREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K9/00Medicinal preparations characterised by special physical form
    • A61K9/08Solutions
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61KPREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K9/00Medicinal preparations characterised by special physical form
    • A61K9/20Pills, tablets, discs, rods
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61KPREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K9/00Medicinal preparations characterised by special physical form
    • A61K9/48Preparations in capsules, e.g. of gelatin, of chocolate

Landscapes

  • Health & Medical Sciences (AREA)
  • General Health & Medical Sciences (AREA)
  • Animal Behavior & Ethology (AREA)
  • Chemical & Material Sciences (AREA)
  • Public Health (AREA)
  • Medicinal Chemistry (AREA)
  • Veterinary Medicine (AREA)
  • Pharmacology & Pharmacy (AREA)
  • Life Sciences & Earth Sciences (AREA)
  • Bioinformatics & Cheminformatics (AREA)
  • Engineering & Computer Science (AREA)
  • General Chemical & Material Sciences (AREA)
  • Organic Chemistry (AREA)
  • Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
  • Chemical Kinetics & Catalysis (AREA)
  • Cardiology (AREA)
  • Epidemiology (AREA)
  • Heart & Thoracic Surgery (AREA)
  • Hospice & Palliative Care (AREA)
  • Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
  • Medicinal Preparation (AREA)
  • Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
  • Acyclic And Carbocyclic Compounds In Medicinal Compositions (AREA)
  • Enzymes And Modification Thereof (AREA)
  • Medicines Containing Material From Animals Or Micro-Organisms (AREA)
SG11202001707PA 2017-08-28 2018-08-28 Methods of enhancing and/or stabilizing cardiac function in patients with fabry disease SG11202001707PA (en)

Applications Claiming Priority (2)

Application Number Priority Date Filing Date Title
US201762550984P 2017-08-28 2017-08-28
PCT/US2018/048257 WO2019046244A1 (en) 2017-08-28 2018-08-28 METHODS FOR ENHANCING AND / OR STABILIZING CARDIAC FUNCTION IN PATIENTS WITH FABRY DISEASE

Publications (1)

Publication Number Publication Date
SG11202001707PA true SG11202001707PA (en) 2020-03-30

Family

ID=63528948

Family Applications (1)

Application Number Title Priority Date Filing Date
SG11202001707PA SG11202001707PA (en) 2017-08-28 2018-08-28 Methods of enhancing and/or stabilizing cardiac function in patients with fabry disease

Country Status (24)

Country Link
US (1) US20200222377A1 (lt)
EP (2) EP4176877A1 (lt)
JP (2) JP2020531550A (lt)
KR (1) KR20200044908A (lt)
CN (1) CN111770753A (lt)
AR (1) AR112482A1 (lt)
AU (1) AU2018326364B2 (lt)
BR (1) BR112020003974A2 (lt)
CA (1) CA3074450A1 (lt)
CL (1) CL2020000491A1 (lt)
DK (1) DK3675853T3 (lt)
EA (1) EA202090564A1 (lt)
ES (1) ES2931054T3 (lt)
HR (1) HRP20221366T1 (lt)
HU (1) HUE060287T2 (lt)
IL (2) IL310648A (lt)
LT (1) LT3675853T (lt)
MX (2) MX2020002229A (lt)
PL (1) PL3675853T3 (lt)
PT (1) PT3675853T (lt)
RS (1) RS63742B1 (lt)
SG (1) SG11202001707PA (lt)
TW (1) TWI845479B (lt)
WO (1) WO2019046244A1 (lt)

Families Citing this family (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
AU2007253900A1 (en) 2006-05-16 2007-11-29 Amicus Therapeutics, Inc. Assays for diagnosing and evaluating treatment options for fabry disease
AU2009214648B2 (en) 2008-02-12 2014-11-13 Amicus Therapeutics, Inc. Method to predict response to pharmacological chaperone treatment of diseases
AU2018277756A1 (en) 2017-05-30 2020-01-23 Amicus Therapeutics, Inc. Methods of treating fabry patients having renal impairment
JP7555818B2 (ja) 2018-02-06 2024-09-25 アミカス セラピューティックス インコーポレイテッド 妊娠患者におけるファブリー病の治療のためのミガラスタットの使用
EP3895708A3 (en) * 2019-08-07 2022-01-19 Amicus Therapeutics, Inc. Methods of treating fabry disease in patients having a mutation in the gla gene
US11623916B2 (en) 2020-12-16 2023-04-11 Amicus Therapeutics, Inc. Highly purified batches of pharmaceutical grade migalastat and methods of producing the same

Family Cites Families (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US6274597B1 (en) 1998-06-01 2001-08-14 Mount Sinai School Of Medicine Of New York University Method of enhancing lysosomal α-Galactosidase A
US20100113517A1 (en) 2007-03-30 2010-05-06 Amicus Therapeutics, Inc. Method for the treatment of fabry disease using pharmacological chaperones
US9999618B2 (en) * 2007-04-26 2018-06-19 Amicus Therapeutics, Inc. Dosing regimens for the treatment of lysosomal storage diseases using pharmacological chaperones
AU2009214648B2 (en) 2008-02-12 2014-11-13 Amicus Therapeutics, Inc. Method to predict response to pharmacological chaperone treatment of diseases

Also Published As

Publication number Publication date
PL3675853T3 (pl) 2022-12-27
CN111770753A (zh) 2020-10-13
CA3074450A1 (en) 2019-03-07
MX2023005628A (es) 2023-05-24
IL272893A (en) 2020-04-30
TW201919619A (zh) 2019-06-01
AU2018326364A1 (en) 2020-04-09
CL2020000491A1 (es) 2020-09-11
HRP20221366T1 (hr) 2023-01-06
EP3675853B1 (en) 2022-09-07
JP2023051998A (ja) 2023-04-11
DK3675853T3 (da) 2022-11-28
KR20200044908A (ko) 2020-04-29
TWI845479B (zh) 2024-06-21
HUE060287T2 (hu) 2023-02-28
WO2019046244A1 (en) 2019-03-07
LT3675853T (lt) 2022-12-12
MX2020002229A (es) 2020-07-20
IL272893B1 (en) 2024-03-01
ES2931054T3 (es) 2022-12-23
EP4176877A1 (en) 2023-05-10
RS63742B1 (sr) 2022-12-30
BR112020003974A2 (pt) 2020-09-01
IL272893B2 (en) 2024-07-01
AU2018326364B2 (en) 2024-08-29
IL310648A (en) 2024-04-01
JP2020531550A (ja) 2020-11-05
EA202090564A1 (ru) 2020-06-15
AR112482A1 (es) 2019-10-30
PT3675853T (pt) 2022-11-28
US20200222377A1 (en) 2020-07-16
EP3675853A1 (en) 2020-07-08

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