PL3675853T3 - Sposoby poprawy i/lub stabilizacji czynności serca u pacjentów z chorobą fabry'ego - Google Patents

Sposoby poprawy i/lub stabilizacji czynności serca u pacjentów z chorobą fabry'ego

Info

Publication number
PL3675853T3
PL3675853T3 PL18766482.6T PL18766482T PL3675853T3 PL 3675853 T3 PL3675853 T3 PL 3675853T3 PL 18766482 T PL18766482 T PL 18766482T PL 3675853 T3 PL3675853 T3 PL 3675853T3
Authority
PL
Poland
Prior art keywords
patients
enhancing
methods
cardiac function
fabry disease
Prior art date
Application number
PL18766482.6T
Other languages
English (en)
Inventor
Jeff Castelli
Jay Barth
Nina SKUBAN
Original Assignee
Amicus Therapeutics, Inc.
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Family has litigation
First worldwide family litigation filed litigation Critical https://patents.darts-ip.com/?family=63528948&utm_source=google_patent&utm_medium=platform_link&utm_campaign=public_patent_search&patent=PL3675853(T3) "Global patent litigation dataset” by Darts-ip is licensed under a Creative Commons Attribution 4.0 International License.
Application filed by Amicus Therapeutics, Inc. filed Critical Amicus Therapeutics, Inc.
Publication of PL3675853T3 publication Critical patent/PL3675853T3/pl

Links

Classifications

    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61KPREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K31/00Medicinal preparations containing organic active ingredients
    • A61K31/33Heterocyclic compounds
    • A61K31/395Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins
    • A61K31/435Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins having six-membered rings with one nitrogen as the only ring hetero atom
    • A61K31/44Non condensed pyridines; Hydrogenated derivatives thereof
    • A61K31/445Non condensed piperidines, e.g. piperocaine
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61PSPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P43/00Drugs for specific purposes, not provided for in groups A61P1/00-A61P41/00
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61PSPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P9/00Drugs for disorders of the cardiovascular system
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61PSPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P9/00Drugs for disorders of the cardiovascular system
    • A61P9/04Inotropic agents, i.e. stimulants of cardiac contraction; Drugs for heart failure
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61KPREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K9/00Medicinal preparations characterised by special physical form
    • A61K9/08Solutions
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61KPREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K9/00Medicinal preparations characterised by special physical form
    • A61K9/20Pills, tablets, discs, rods
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61KPREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K9/00Medicinal preparations characterised by special physical form
    • A61K9/48Preparations in capsules, e.g. of gelatin, of chocolate

Landscapes

  • Health & Medical Sciences (AREA)
  • Pharmacology & Pharmacy (AREA)
  • Medicinal Chemistry (AREA)
  • Life Sciences & Earth Sciences (AREA)
  • Public Health (AREA)
  • General Health & Medical Sciences (AREA)
  • Chemical & Material Sciences (AREA)
  • Animal Behavior & Ethology (AREA)
  • Veterinary Medicine (AREA)
  • Engineering & Computer Science (AREA)
  • Bioinformatics & Cheminformatics (AREA)
  • Chemical Kinetics & Catalysis (AREA)
  • General Chemical & Material Sciences (AREA)
  • Organic Chemistry (AREA)
  • Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
  • Cardiology (AREA)
  • Epidemiology (AREA)
  • Heart & Thoracic Surgery (AREA)
  • Hospice & Palliative Care (AREA)
  • Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
  • Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
  • Medicinal Preparation (AREA)
  • Acyclic And Carbocyclic Compounds In Medicinal Compositions (AREA)
  • Enzymes And Modification Thereof (AREA)
  • Medicines Containing Material From Animals Or Micro-Organisms (AREA)
PL18766482.6T 2017-08-28 2018-08-28 Sposoby poprawy i/lub stabilizacji czynności serca u pacjentów z chorobą fabry'ego PL3675853T3 (pl)

Applications Claiming Priority (2)

Application Number Priority Date Filing Date Title
US201762550984P 2017-08-28 2017-08-28
PCT/US2018/048257 WO2019046244A1 (en) 2017-08-28 2018-08-28 METHODS FOR ENHANCING AND / OR STABILIZING CARDIAC FUNCTION IN PATIENTS WITH FABRY DISEASE

Publications (1)

Publication Number Publication Date
PL3675853T3 true PL3675853T3 (pl) 2022-12-27

Family

ID=63528948

Family Applications (2)

Application Number Title Priority Date Filing Date
PL18766482.6T PL3675853T3 (pl) 2017-08-28 2018-08-28 Sposoby poprawy i/lub stabilizacji czynności serca u pacjentów z chorobą fabry'ego
PL22194251.9T PL4176877T3 (pl) 2017-08-28 2018-08-28 Sposoby poprawy i/lub stabilizacji czynności serca u pacjentów z chorobą fabry'ego

Family Applications After (1)

Application Number Title Priority Date Filing Date
PL22194251.9T PL4176877T3 (pl) 2017-08-28 2018-08-28 Sposoby poprawy i/lub stabilizacji czynności serca u pacjentów z chorobą fabry'ego

Country Status (26)

Country Link
US (1) US20200222377A1 (pl)
EP (3) EP3675853B1 (pl)
JP (3) JP7755929B2 (pl)
KR (2) KR102790184B1 (pl)
CN (1) CN111770753A (pl)
AR (1) AR112482A1 (pl)
AU (2) AU2018326364B2 (pl)
CA (1) CA3074450C (pl)
CL (1) CL2020000491A1 (pl)
DK (2) DK3675853T3 (pl)
EA (1) EA202090564A1 (pl)
ES (2) ES2931054T3 (pl)
FI (1) FI4176877T3 (pl)
HR (2) HRP20221366T1 (pl)
HU (2) HUE070433T2 (pl)
IL (3) IL310648A (pl)
LT (2) LT4176877T (pl)
MX (2) MX2020002229A (pl)
PL (2) PL3675853T3 (pl)
PT (2) PT4176877T (pl)
RS (2) RS63742B1 (pl)
SG (1) SG11202001707PA (pl)
SI (1) SI4176877T1 (pl)
SM (2) SMT202200459T1 (pl)
TW (1) TWI845479B (pl)
WO (1) WO2019046244A1 (pl)

Families Citing this family (9)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
HUE027569T2 (en) 2006-05-16 2016-10-28 Amicus Therapeutics Inc Preparation for the treatment of Fabry disease
PL2252313T3 (pl) 2008-02-12 2015-09-30 Amicus Therapeutics Inc Sposób przewidywania odpowiedzi na leczenie chorób farmakologicznymi białkami chaperonowymi
CA3065298C (en) 2017-05-30 2025-05-06 Amicus Therapeutics, Inc. Methods of treating fabry patients having renal impairment
ES2931054T3 (es) 2017-08-28 2022-12-23 Amicus Therapeutics Inc Métodos para potenciar y/o estabilizar la función cardíaca en pacientes con enfermedad de Fabry
EP4717319A2 (en) 2018-02-06 2026-04-01 Amicus Therapeutics, Inc. Methods of treating fabry disease in pregnant patients
JP2021024864A (ja) * 2019-08-07 2021-02-22 アミカス セラピューティックス インコーポレイテッド Gla遺伝子に突然変異を有する患者のファブリー病を治療する方法
US11623916B2 (en) 2020-12-16 2023-04-11 Amicus Therapeutics, Inc. Highly purified batches of pharmaceutical grade migalastat and methods of producing the same
WO2026043459A2 (en) 2024-08-23 2026-02-26 Sanovel Ilac Sanayi Ve Ticaret Anonim Sirketi Capsule formulations comprising migalastat
CN119120696A (zh) * 2024-11-12 2024-12-13 北京贝瑞和康生物技术有限公司 检测法布雷病gla基因突变的引物组、试剂盒及其应用

Family Cites Families (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US6274597B1 (en) 1998-06-01 2001-08-14 Mount Sinai School Of Medicine Of New York University Method of enhancing lysosomal α-Galactosidase A
WO2008121826A2 (en) 2007-03-30 2008-10-09 Amicus Therapeutics, Inc. Method for the treatment of fabry disease using pharmacological chaperones
US9999618B2 (en) * 2007-04-26 2018-06-19 Amicus Therapeutics, Inc. Dosing regimens for the treatment of lysosomal storage diseases using pharmacological chaperones
PL2252313T3 (pl) 2008-02-12 2015-09-30 Amicus Therapeutics Inc Sposób przewidywania odpowiedzi na leczenie chorób farmakologicznymi białkami chaperonowymi
ES2931054T3 (es) 2017-08-28 2022-12-23 Amicus Therapeutics Inc Métodos para potenciar y/o estabilizar la función cardíaca en pacientes con enfermedad de Fabry
CN111344912B (zh) 2017-08-28 2021-12-28 约翰·梅扎林瓜联合股份有限公司 同轴电缆连接器的天气防护壳体

Also Published As

Publication number Publication date
MX2023005628A (es) 2023-05-24
SMT202500073T1 (it) 2025-03-12
EP4588476A1 (en) 2025-07-23
BR112020003974A2 (pt) 2020-09-01
ES3013820T3 (en) 2025-04-15
JP2020531550A (ja) 2020-11-05
KR20200044908A (ko) 2020-04-29
JP7755929B2 (ja) 2025-10-17
KR102790184B1 (ko) 2025-04-01
AR112482A1 (es) 2019-10-30
HRP20250064T1 (hr) 2025-03-14
RS66515B1 (sr) 2025-03-31
HUE060287T2 (hu) 2023-02-28
DK4176877T3 (da) 2025-02-24
HRP20221366T1 (hr) 2023-01-06
PL4176877T3 (pl) 2025-04-07
TWI845479B (zh) 2024-06-21
IL272893B1 (en) 2024-03-01
IL310648A (en) 2024-04-01
SMT202200459T1 (it) 2023-01-13
SG11202001707PA (en) 2020-03-30
US20200222377A1 (en) 2020-07-16
AU2018326364B2 (en) 2024-08-29
EP4176877A1 (en) 2023-05-10
FI4176877T3 (fi) 2025-03-06
SI4176877T1 (sl) 2025-03-31
KR20250049561A (ko) 2025-04-11
CA3074450A1 (en) 2019-03-07
LT4176877T (lt) 2025-02-10
EA202090564A1 (ru) 2020-06-15
EP3675853B1 (en) 2022-09-07
IL324182A (en) 2025-12-01
WO2019046244A1 (en) 2019-03-07
AU2018326364A1 (en) 2020-04-09
MX2020002229A (es) 2020-07-20
ES2931054T3 (es) 2022-12-23
EP4176877B1 (en) 2024-12-04
EP3675853A1 (en) 2020-07-08
JP2025138638A (ja) 2025-09-25
CL2020000491A1 (es) 2020-09-11
CN111770753A (zh) 2020-10-13
AU2024266945A1 (en) 2024-12-19
HUE070433T2 (hu) 2025-06-28
LT3675853T (lt) 2022-12-12
JP2023051998A (ja) 2023-04-11
TW201919619A (zh) 2019-06-01
RS63742B1 (sr) 2022-12-30
PT3675853T (pt) 2022-11-28
PT4176877T (pt) 2025-02-24
IL272893A (en) 2020-04-30
IL272893B2 (en) 2024-07-01
CA3074450C (en) 2024-10-01
DK3675853T3 (da) 2022-11-28

Similar Documents

Publication Publication Date Title
IL272893A (en) Methods for increasing and/or stabilizing cardiac functions in patients with Fabry disease
IL264301A (en) Treatment of Fabry disease in ert-naive and ert-experienced patients
IL253351A0 (en) Cardiac stimulation of conduction pathways between the atria and ventricles and of tissues associated with these pathways
IL249580A0 (en) Methods for anesthetizing nerve tissue in the trigeminal nerve pathway and their medical uses
EP3319683A4 (en) Implantable nerve stimulator having internal electronics without asic and methods of use
HUE065152T2 (hu) Fluor-fenil-béta-hidroxietilaminok és alkalmazásuk hiperglikémia kezelésében
SG11202000423XA (en) Treatment of fabry disease in ert-naïve and ert-experienced patients
IL269083A (en) Methods for preventing and treating heart disease
GB201709840D0 (en) Methods and medical uses
IL273470A (en) Semaglutide in medical treatment
GB201710822D0 (en) Methods and medical uses relating to the treatment of hypoglycaemia
PT3749308T (pt) Tratamento de pacientes com doença de fabry clássica com migalastato
HUE057216T2 (hu) Genotípus-rétegzés cukorbetegség kezelésében és megelõzésében
IL274773A (en) A pyrimidine sulfamide derivative and a method of its preparation and medical application
EP3681410A4 (en) HEART TREATMENT SYSTEM AND METHOD
ZA201906964B (en) Prevention and/or treatment of inflammatory skin disease
EP3346935A4 (en) Recovery and processing of human embryos formed in vivo
HK40029560A (en) Methods and medical uses relating to the treatment of hypoglycaemia
Thongcharoen Acharn Dr. Somchai-A Good Person of Thai and Global Academic Societies
GB201709837D0 (en) Methods and medical uses
EP3288562A4 (en) Method for improving kidney and/or heart function in patients with kidney disease