RU2765826C2 - Векторная система на основе аденоассоциированного вируса - Google Patents
Векторная система на основе аденоассоциированного вируса Download PDFInfo
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| CN115666658A (zh) * | 2020-04-01 | 2023-01-31 | 佛罗里达州大学研究基金会 | 具有提高的治疗ush1b的安全性的双aav-myo7a载体 |
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| RU2555346C2 (ru) * | 2009-08-07 | 2015-07-10 | Трансген Са | Композиция для лечения инфекции вирусом гепатита в |
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| US20090214478A1 (en) * | 2008-02-21 | 2009-08-27 | Alberto Auricchio | Method of treating ocular diseases by gene therapy |
| WO2013075008A1 (en) * | 2011-11-16 | 2013-05-23 | University Of Florida Research Foundation Inc. | Aav dual vector systems for gene therapy |
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| WO2014170480A1 (en) * | 2013-04-18 | 2014-10-23 | Fondazione Telethon | Effective delivery of large genes by dual aav vectors |
Non-Patent Citations (2)
| Title |
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| IVANA TRAPANI et al., "Effective delivery of large genes to the retina by dual AAV vectors", EMBO MOLECULAR MEDICINE 2014,Vol. 6, No. 2, 16 December 2013 (2013-12-16), page n/a-n/a, XP055127533. * |
| IVANA TRAPANI ET AL: "Effective delivery of large genes to the retina by dual AAV vectors", EMBO MOLECULAR MEDICINE, WILEY-BLACKWELL, US, 1 December 2013 (2013-12-01), US , pages 194 - 211, XP055127533, ISSN: 1757-4676, DOI: 10.1002/emmm.201302948 * |
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