RU2765826C2 - Векторная система на основе аденоассоциированного вируса - Google Patents
Векторная система на основе аденоассоциированного вируса Download PDFInfo
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| GB201817469D0 (en) * | 2018-10-26 | 2018-12-12 | Univ Oxford Innovation Ltd | Gene therapy for retinal disease |
| WO2020093018A1 (en) | 2018-11-01 | 2020-05-07 | University Of Florida Research Foundation, Incorporated | A codon optimized otoferlin aav dual vector gene therapy |
| EP3921032A4 (en) | 2019-02-08 | 2022-11-30 | Decibel Therapeutics, Inc. | COMPOSITIONS AND METHODS FOR TREATMENT OF SENSORINEURAL HEARING LOSS USING OTOFERLIN DOUBLE VECTOR SYSTEMS |
| US20220267802A1 (en) * | 2019-07-15 | 2022-08-25 | President And Fellows Of Harvard College | Methods and compositions for gene delivery |
| JP7665609B2 (ja) | 2019-10-30 | 2025-04-21 | デシベル セラピューティクス インコーポレイテッド | オトフェリン二重ベクター系及びそれを含む感音難聴を治療するための組成物 |
| CA3174500A1 (en) * | 2020-04-01 | 2021-10-07 | University Of Florida Research Foundation, Incorporated | Dual aav-myo7a vectors with improved safety for the treatment of ush1b |
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| WO2014170480A1 (en) * | 2013-04-18 | 2014-10-23 | Fondazione Telethon | Effective delivery of large genes by dual aav vectors |
| RU2555346C2 (ru) * | 2009-08-07 | 2015-07-10 | Трансген Са | Композиция для лечения инфекции вирусом гепатита в |
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| US20090214478A1 (en) * | 2008-02-21 | 2009-08-27 | Alberto Auricchio | Method of treating ocular diseases by gene therapy |
| WO2013075008A1 (en) * | 2011-11-16 | 2013-05-23 | University Of Florida Research Foundation Inc. | Aav dual vector systems for gene therapy |
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| RU2555346C2 (ru) * | 2009-08-07 | 2015-07-10 | Трансген Са | Композиция для лечения инфекции вирусом гепатита в |
| WO2014170480A1 (en) * | 2013-04-18 | 2014-10-23 | Fondazione Telethon | Effective delivery of large genes by dual aav vectors |
Non-Patent Citations (2)
| Title |
|---|
| IVANA TRAPANI et al., "Effective delivery of large genes to the retina by dual AAV vectors", EMBO MOLECULAR MEDICINE 2014,Vol. 6, No. 2, 16 December 2013 (2013-12-16), page n/a-n/a, XP055127533. * |
| IVANA TRAPANI ET AL: "Effective delivery of large genes to the retina by dual AAV vectors", EMBO MOLECULAR MEDICINE, WILEY-BLACKWELL, US, 1 December 2013 (2013-12-01), US , pages 194 - 211, XP055127533, ISSN: 1757-4676, DOI: 10.1002/emmm.201302948 * |
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