AU2017286623A1 - Dual overlapping adeno-associated viral vector system for expressing ABC4A - Google Patents
Dual overlapping adeno-associated viral vector system for expressing ABC4A Download PDFInfo
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- AU2017286623A1 AU2017286623A1 AU2017286623A AU2017286623A AU2017286623A1 AU 2017286623 A1 AU2017286623 A1 AU 2017286623A1 AU 2017286623 A AU2017286623 A AU 2017286623A AU 2017286623 A AU2017286623 A AU 2017286623A AU 2017286623 A1 AU2017286623 A1 AU 2017286623A1
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- nucleic acid
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- aav vector
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| US12359221B2 (en) | 2017-05-05 | 2025-07-15 | The Regents Of The University Of California | Compositions and methods for expressing otoferlin |
| US20210147870A1 (en) * | 2018-04-05 | 2021-05-20 | Nightstarx Limited | Compositions and methods for the treatment of stargardt disease |
| CN113348249B (zh) * | 2018-10-15 | 2025-09-23 | 特莱索恩基金会 | 内蛋白及其用途 |
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| EP3921032A4 (en) | 2019-02-08 | 2022-11-30 | Decibel Therapeutics, Inc. | Compositions and methods for treating sensorineural hearing loss using otoferlin dual vector systems |
| US20220267802A1 (en) * | 2019-07-15 | 2022-08-25 | President And Fellows Of Harvard College | Methods and compositions for gene delivery |
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