KR20230143141A - 캡슐화된 rna 폴리뉴클레오타이드 및 사용 방법 - Google Patents

캡슐화된 rna 폴리뉴클레오타이드 및 사용 방법 Download PDF

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KR20230143141A
KR20230143141A KR1020237026655A KR20237026655A KR20230143141A KR 20230143141 A KR20230143141 A KR 20230143141A KR 1020237026655 A KR1020237026655 A KR 1020237026655A KR 20237026655 A KR20237026655 A KR 20237026655A KR 20230143141 A KR20230143141 A KR 20230143141A
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sequence
lnp
lipid
cancer
mir
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로레나 레르너
에드워드 엠. 케네디
크리스토프 쿠에바
제시카 데터링
제프리 데이비드 브라이언트
치-잉 후
투바 에이. 치마
션 에섹스
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온코루스, 인크.
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KR1020237026655A 2021-01-06 2022-01-06 캡슐화된 rna 폴리뉴클레오타이드 및 사용 방법 Pending KR20230143141A (ko)

Applications Claiming Priority (11)

Application Number Priority Date Filing Date Title
US202163134376P 2021-01-06 2021-01-06
US63/134,376 2021-01-06
US202163147959P 2021-02-10 2021-02-10
US63/147,959 2021-02-10
US202163181917P 2021-04-29 2021-04-29
US202163181663P 2021-04-29 2021-04-29
US202163181899P 2021-04-29 2021-04-29
US63/181,899 2021-04-29
US63/181,663 2021-04-29
US63/181,917 2021-04-29
PCT/US2022/011450 WO2022150485A1 (en) 2021-01-06 2022-01-06 Encapsulated rna polynucleotides and methods of use

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KR20230143141A true KR20230143141A (ko) 2023-10-11

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US (1) US20240115636A1 (https=)
EP (1) EP4274591A4 (https=)
JP (1) JP2024503623A (https=)
KR (1) KR20230143141A (https=)
AU (1) AU2022206676A1 (https=)
CA (1) CA3204244A1 (https=)
WO (1) WO2022150485A1 (https=)

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WO2023091490A1 (en) * 2021-11-16 2023-05-25 Senda Biosciences, Inc. Novel ionizable lipids and lipid nanoparticles and methods of using the same
WO2023223183A1 (en) * 2022-05-16 2023-11-23 Crispr Therapeutics Ag Picornaviral vectors for gene editing
WO2024031078A2 (en) * 2022-08-05 2024-02-08 Elevatebio Technologies, Inc. Chimeric oncolytic viruses with tropism for poliovirus receptor
EP4612284A2 (en) 2022-11-04 2025-09-10 Life Edit Therapeutics, Inc. Evolved adenine deaminases and rna-guided nuclease fusion proteins with internal insertion sites and methods of use
WO2024162304A1 (ja) 2023-01-31 2024-08-08 アステラス製薬株式会社 環状アミンを有するカルバモイル脂質又はウレア脂質、それを含む脂質ナノ粒子、及び医薬組成物
WO2024178397A2 (en) 2023-02-24 2024-08-29 Elevatebio Technologies, Inc. Modified immune effector cells and methods of use
WO2024226832A1 (en) * 2023-04-25 2024-10-31 Orgenesis Inc. Ribonucleases for treating viral infections
WO2025022367A2 (en) 2023-07-27 2025-01-30 Life Edit Therapeutics, Inc. Rna-guided nucleases and active fragments and variants thereof and methods of use
WO2025083619A1 (en) 2023-10-18 2025-04-24 Life Edit Therapeutics, Inc. Rna-guided nucleases and acive fragments and variants thereof and methods of use
TW202546224A (zh) 2024-02-12 2025-12-01 美商生命編輯治療學公司 新穎的rna引導之核酸酶及用於聚合酶編輯之蛋白質
WO2026003754A1 (en) 2024-06-25 2026-01-02 Life Edit Therapeutics, Inc. Novel reverse transcriptases and uses thereof
WO2026006491A1 (en) * 2024-06-25 2026-01-02 Cornell University Senecavirus a (sva) vaccine compositions and methods thereof

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Publication number Priority date Publication date Assignee Title
WO2006074526A1 (en) * 2005-01-17 2006-07-20 Viralytics Limited Method and composition for treatment of neoplasms
HRP20220652T1 (hr) * 2015-12-10 2022-06-24 Modernatx, Inc. Pripravci i postupci unosa terapijskih sredstava
AU2018301701A1 (en) * 2017-07-14 2020-02-27 Elevatebio Technologies, Inc. Encapsulated polynucleotides and methods of use
WO2019046809A1 (en) * 2017-08-31 2019-03-07 Modernatx, Inc. METHODS OF MANUFACTURING LIPID NANOPARTICLES
WO2019210394A1 (en) * 2018-04-29 2019-11-07 Precision Nanosystems Inc. Compositions for transfecting resistant cell types
EP3906039A4 (en) * 2019-01-04 2023-01-18 Oncorus, Inc. ENCAPSULATED POLYNUCLEOTIDES AND METHODS OF USE
EP3956459A4 (en) * 2019-04-15 2023-01-11 Precision Nanosystems Inc NONVIRAL MODIFICATION OF T LYMPHOCYTE GENE EXPRESSION

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US20240115636A1 (en) 2024-04-11
JP2024503623A (ja) 2024-01-26
EP4274591A1 (en) 2023-11-15
AU2022206676A9 (en) 2024-05-09
AU2022206676A1 (en) 2023-08-24
CA3204244A1 (en) 2022-07-14
WO2022150485A1 (en) 2022-07-14
EP4274591A4 (en) 2024-12-11

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