KR102667867B1 - 안구인두근위축증(opmd)의 치료제 및 이의 사용 - Google Patents
안구인두근위축증(opmd)의 치료제 및 이의 사용 Download PDFInfo
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- KR102667867B1 KR102667867B1 KR1020237003441A KR20237003441A KR102667867B1 KR 102667867 B1 KR102667867 B1 KR 102667867B1 KR 1020237003441 A KR1020237003441 A KR 1020237003441A KR 20237003441 A KR20237003441 A KR 20237003441A KR 102667867 B1 KR102667867 B1 KR 102667867B1
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| EP3555294A4 (en) * | 2016-12-14 | 2020-08-26 | Benitec Biopharma Limited | REAGENTS FOR THE TREATMENT OF OCULOPHARYNGEAL MUSCLE DYSTROPHY (PDD) AND THEIR USE |
| CN112867511A (zh) * | 2018-10-17 | 2021-05-28 | 贝尼泰克生物制药有限公司 | 用于治疗眼咽肌营养不良(opmd)的方法 |
| US20220098614A1 (en) | 2019-02-28 | 2022-03-31 | Benitec IP Holdings Inc. | Compositions and Methods for Treating Oculopharyngeal Muscular Dystrophy (OPMD) |
| CN114901822A (zh) * | 2019-12-23 | 2022-08-12 | 维萨梅布有限公司 | 用于同时调节基因表达的组合物和方法 |
| WO2026011009A1 (en) * | 2024-07-02 | 2026-01-08 | Kate Therapeutics, Inc. | Compositions and methods for muscle disorders |
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| WO2010105372A1 (en) | 2009-03-20 | 2010-09-23 | Protiva Biotherapeutics, Inc. | Compositions and methods for silencing hepatitis c virus expression |
| US20110207224A1 (en) | 2001-07-12 | 2011-08-25 | University Of Massachusetts | In vivo production of small interfering rnas that mediate gene silencing |
| US20120171686A1 (en) | 2005-11-08 | 2012-07-05 | Cepheid | Methods for the identification of microrna and their applications in research and human health |
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| US8258286B2 (en) * | 2007-04-26 | 2012-09-04 | University Of Iowa Research Foundation | Reduction of off-target RNA interference toxicity |
| MX356107B (es) * | 2012-02-16 | 2018-05-15 | Atyr Pharma Inc | Histidil-arnt sintetasas para tratar enfermedades autoinmunes e inflamatorias. |
| WO2014077693A1 (en) * | 2012-11-16 | 2014-05-22 | Academisch Ziekenhuis Leiden H.O.D.N. Lumc | Means and methods for reducing an effect of aging in a mammalian cell |
| CN105143450A (zh) * | 2013-01-08 | 2015-12-09 | 贝尼泰克生物制药有限公司 | 年龄相关性黄斑变性治疗 |
| CA3020754C (en) * | 2016-04-14 | 2023-07-25 | Benitec Biopharma Limited | Reagents for treatment of oculopharyngeal muscular dystrophy (opmd) and use thereof |
| EP3555294A4 (en) | 2016-12-14 | 2020-08-26 | Benitec Biopharma Limited | REAGENTS FOR THE TREATMENT OF OCULOPHARYNGEAL MUSCLE DYSTROPHY (PDD) AND THEIR USE |
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| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US20110207224A1 (en) | 2001-07-12 | 2011-08-25 | University Of Massachusetts | In vivo production of small interfering rnas that mediate gene silencing |
| US20120171686A1 (en) | 2005-11-08 | 2012-07-05 | Cepheid | Methods for the identification of microrna and their applications in research and human health |
| WO2010105372A1 (en) | 2009-03-20 | 2010-09-23 | Protiva Biotherapeutics, Inc. | Compositions and methods for silencing hepatitis c virus expression |
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| Aging,제5권,6호,412-426면(2013.06.01.) |
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