JPWO2023214512A5 - - Google Patents

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Publication number
JPWO2023214512A5
JPWO2023214512A5 JP2024519192A JP2024519192A JPWO2023214512A5 JP WO2023214512 A5 JPWO2023214512 A5 JP WO2023214512A5 JP 2024519192 A JP2024519192 A JP 2024519192A JP 2024519192 A JP2024519192 A JP 2024519192A JP WO2023214512 A5 JPWO2023214512 A5 JP WO2023214512A5
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JP
Japan
Prior art keywords
sequence
rna molecule
mrna
polynucleotide
artificial rna
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024519192A
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English (en)
Japanese (ja)
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JPWO2023214512A1 (https=
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Publication date
Application filed filed Critical
Priority claimed from PCT/JP2023/015828 external-priority patent/WO2023214512A1/ja
Publication of JPWO2023214512A1 publication Critical patent/JPWO2023214512A1/ja
Publication of JPWO2023214512A5 publication Critical patent/JPWO2023214512A5/ja
Pending legal-status Critical Current

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JP2024519192A 2022-05-06 2023-04-20 Pending JPWO2023214512A1 (https=)

Applications Claiming Priority (2)

Application Number Priority Date Filing Date Title
JP2022076674 2022-05-06
PCT/JP2023/015828 WO2023214512A1 (ja) 2022-05-06 2023-04-20 人工rna分子

Publications (2)

Publication Number Publication Date
JPWO2023214512A1 JPWO2023214512A1 (https=) 2023-11-09
JPWO2023214512A5 true JPWO2023214512A5 (https=) 2025-01-20

Family

ID=88646433

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024519192A Pending JPWO2023214512A1 (https=) 2022-05-06 2023-04-20

Country Status (4)

Country Link
US (1) US20250297253A1 (https=)
EP (1) EP4520825A1 (https=)
JP (1) JPWO2023214512A1 (https=)
WO (1) WO2023214512A1 (https=)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2025217551A1 (en) * 2024-04-12 2025-10-16 University Of Miami Microrna-mediated obstruction of stem-loop alternative splicing

Family Cites Families (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US9080170B2 (en) * 2010-03-17 2015-07-14 Association Institut De Myologie Modified U7 snRNAs for treatment of neuromuscular diseases
TWI541024B (zh) 2010-09-01 2016-07-11 日本新藥股份有限公司 反義核酸
MX2018007987A (es) 2015-12-28 2019-01-10 Novartis Ag Composiciones y metodos para el tratamiento de hemoglobinopatias.
KR20240056729A (ko) * 2016-05-18 2024-04-30 보이저 테라퓨틱스, 인크. 조절성 폴리뉴클레오티드
US20230059753A1 (en) * 2019-12-09 2023-02-23 Astellas Pharma Inc. Antisense guide rna with added functional region for editing target rna

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