JP2021534818A5 - - Google Patents

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Publication number
JP2021534818A5
JP2021534818A5 JP2021533393A JP2021533393A JP2021534818A5 JP 2021534818 A5 JP2021534818 A5 JP 2021534818A5 JP 2021533393 A JP2021533393 A JP 2021533393A JP 2021533393 A JP2021533393 A JP 2021533393A JP 2021534818 A5 JP2021534818 A5 JP 2021534818A5
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JP
Japan
Prior art keywords
cells
approximately
cell line
sequence encoding
viral vector
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JP2021533393A
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English (en)
Japanese (ja)
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JP7470119B2 (ja
JP2021534818A (ja
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Priority claimed from PCT/US2019/047800 external-priority patent/WO2020041647A1/en
Publication of JP2021534818A publication Critical patent/JP2021534818A/ja
Publication of JP2021534818A5 publication Critical patent/JP2021534818A5/ja
Application granted granted Critical
Publication of JP7470119B2 publication Critical patent/JP7470119B2/ja
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JP2021533393A 2018-08-24 2019-08-23 無血清培地におけるベクター産生 Active JP7470119B2 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201862722784P 2018-08-24 2018-08-24
US62/722,784 2018-08-24
PCT/US2019/047800 WO2020041647A1 (en) 2018-08-24 2019-08-23 Vector production in serum free media

Publications (3)

Publication Number Publication Date
JP2021534818A JP2021534818A (ja) 2021-12-16
JP2021534818A5 true JP2021534818A5 (https=) 2022-08-29
JP7470119B2 JP7470119B2 (ja) 2024-04-17

Family

ID=67874545

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2021533393A Active JP7470119B2 (ja) 2018-08-24 2019-08-23 無血清培地におけるベクター産生

Country Status (9)

Country Link
US (1) US20210238632A1 (https=)
EP (1) EP3841212A1 (https=)
JP (1) JP7470119B2 (https=)
KR (2) KR102944997B1 (https=)
CN (1) CN112639109A (https=)
AU (1) AU2019325609A1 (https=)
CA (1) CA3109924A1 (https=)
SG (1) SG11202101594WA (https=)
WO (1) WO2020041647A1 (https=)

Families Citing this family (6)

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Publication number Priority date Publication date Assignee Title
EP3897745A1 (en) * 2018-12-23 2021-10-27 CSL Behring LLC Haematopoietic stem cell-gene therapy for wiskott-aldrich syndrome
EP4150097A1 (en) * 2020-05-15 2023-03-22 Ivexsol, Inc. Compositions and methods for producing stable viral vector producer cells for cell and gene therapy
CN111808859B (zh) * 2020-07-13 2022-09-13 中国科学院广州生物医药与健康研究院 WAS基因的gRNA及其应用
JP2024539033A (ja) * 2021-10-19 2024-10-28 アムジエン・インコーポレーテツド 組換えレンチウイルス産生のための組成物及び方法
CN114045265A (zh) * 2021-11-17 2022-02-15 深圳知因细胞生物科技有限公司 一种慢病毒体外转染人造血干细胞的试剂和试剂盒
CN114716530B (zh) * 2022-05-05 2023-11-10 明长(上海)生物医药科技有限公司 一种蛋白液、制备方法及应用

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US6013516A (en) 1995-10-06 2000-01-11 The Salk Institute For Biological Studies Vector and method of use for nucleic acid delivery to non-dividing cells
CA2328404C (en) 1998-05-13 2007-07-24 Genetix Pharmaceuticals, Inc. Novel lentiviral packaging cells
WO2008112226A2 (en) 2007-03-13 2008-09-18 Massachusetts Institute Of Technology Cre-lox based gene knockdown constructs and methods of use thereof
WO2012170431A2 (en) 2011-06-06 2012-12-13 Bluebird Bio, Inc. Improved geneswitch systems
JP2015529466A (ja) 2012-09-14 2015-10-08 ザ リージェンツ オブ ザ ユニバーシティ オブ カリフォルニア 鎌状赤血球症の幹細胞遺伝子治療のためのレンチウイルスベクター
CN105940013B (zh) * 2013-12-09 2020-03-27 桑格摩生物科学股份有限公司 用于治疗血友病的方法和组合物
JP6509884B2 (ja) 2014-01-30 2019-05-08 チルドレンズ ホスピタル メディカル センター 鎌状赤血球病の遺伝子的是正のための改善された胎児ヘモグロビン
WO2016118780A1 (en) 2015-01-21 2016-07-28 Fred Hutchinson Cancer Research Center Point-of-care and/or portable platform for gene therapy
PL3294893T3 (pl) * 2015-05-13 2024-04-29 Csl Behring Gene Therapy, Inc. Bioprodukcja wektorów lentiwirusowych
US10214731B2 (en) 2015-05-28 2019-02-26 Cornell University Adeno-associated virus mediated delivery of C1E1 as a therapy for angioedema
CN108463243B (zh) 2015-11-19 2022-06-14 夏尔人类遗传性治疗公司 重组人c1酯酶抑制剂及其用途
EP3389677B1 (en) 2015-12-18 2024-06-26 Sangamo Therapeutics, Inc. Targeted disruption of the t cell receptor
JP2019509738A (ja) 2016-03-11 2019-04-11 ブルーバード バイオ, インコーポレイテッド ゲノム編集された免疫エフェクター細胞
KR102014349B1 (ko) 2016-08-17 2019-08-26 서울대학교 산학협력단 Jak 억제제를 포함하는 면역반응 억제용 조성물
AU2017312132A1 (en) 2016-08-19 2019-03-21 Bluebird Bio, Inc. Genome editing enhancers
US20200325458A1 (en) 2017-04-21 2020-10-15 Seattle Children's Hospital (dba Seattle Children's Research Institute) Optimized lentiviral vector for xla gene therapy
CN111164211B (zh) * 2017-07-18 2024-08-02 杰特贝林基因治疗股份有限公司 用于治疗β-血红蛋白病的组合物和方法

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