JPWO2022246276A5 - - Google Patents
Download PDFInfo
- Publication number
- JPWO2022246276A5 JPWO2022246276A5 JP2023572122A JP2023572122A JPWO2022246276A5 JP WO2022246276 A5 JPWO2022246276 A5 JP WO2022246276A5 JP 2023572122 A JP2023572122 A JP 2023572122A JP 2023572122 A JP2023572122 A JP 2023572122A JP WO2022246276 A5 JPWO2022246276 A5 JP WO2022246276A5
- Authority
- JP
- Japan
- Prior art keywords
- seq
- sequence
- composition
- expression construct
- set forth
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202163191832P | 2021-05-21 | 2021-05-21 | |
| US63/191,832 | 2021-05-21 | ||
| PCT/US2022/030371 WO2022246276A2 (en) | 2021-05-21 | 2022-05-20 | Artificial expression constructs for modulating gene expression in neurons within the thalamus |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2024519955A JP2024519955A (ja) | 2024-05-21 |
| JP2024519955A5 JP2024519955A5 (https=) | 2025-05-27 |
| JPWO2022246276A5 true JPWO2022246276A5 (https=) | 2025-05-27 |
Family
ID=84141881
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023572122A Pending JP2024519955A (ja) | 2021-05-21 | 2022-05-20 | 視床内ニューロンにおいて遺伝子発現を調節するための人工発現コンストラクト |
Country Status (6)
| Country | Link |
|---|---|
| US (1) | US20240254514A1 (https=) |
| EP (1) | EP4341410A4 (https=) |
| JP (1) | JP2024519955A (https=) |
| AU (1) | AU2022276538A1 (https=) |
| CA (1) | CA3219142A1 (https=) |
| WO (1) | WO2022246276A2 (https=) |
Families Citing this family (1)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2023060112A1 (en) * | 2021-10-05 | 2023-04-13 | Allen Institute | Artificial expression constructs for modulating gene expression in the cerebellum and a secondary cell type |
Family Cites Families (4)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| CA3052290A1 (en) * | 2017-02-10 | 2018-08-16 | The Rockefeller University | Methods for cell-type specific profiling to identify drug targets |
| US20210395780A1 (en) * | 2018-11-05 | 2021-12-23 | Allen Institute | Artificial expression constructs for selectively modulating gene expression in excitatory cortical neurons |
| EP3923995A4 (en) * | 2019-02-15 | 2023-05-17 | Allen Institute | ARTIFICIAL EXPRESSION RECOMBINANTS FOR THE SELECTIVE MODULATION OF GENE EXPRESSION IN SELECTED NEURON CELL POPULATIONS |
| JP2026509974A (ja) * | 2023-02-02 | 2026-03-26 | アレン インスティテュート | 脊髄内の細胞の遺伝子発現を調節するための人工発現コンストラクト |
-
2022
- 2022-05-20 US US18/563,252 patent/US20240254514A1/en active Pending
- 2022-05-20 CA CA3219142A patent/CA3219142A1/en active Pending
- 2022-05-20 JP JP2023572122A patent/JP2024519955A/ja active Pending
- 2022-05-20 WO PCT/US2022/030371 patent/WO2022246276A2/en not_active Ceased
- 2022-05-20 EP EP22805632.1A patent/EP4341410A4/en active Pending
- 2022-05-20 AU AU2022276538A patent/AU2022276538A1/en active Pending
Similar Documents
| Publication | Publication Date | Title |
|---|---|---|
| JP7707261B2 (ja) | 筋疾患の治療のための改変aavカプシドポリペプチド | |
| KR102649543B1 (ko) | 캡시드-변형된 raav3 벡터 조성물, 및 인간 간암의 유전자 요법에서의 용도 | |
| JP2025023947A5 (https=) | ||
| JP2026021360A5 (https=) | ||
| AU2025263840A1 (en) | Rescuing voltage-gated sodium channel function in inhibitory neurons | |
| US20230048025A1 (en) | Adeno associated viral vectors | |
| RU2018120736A (ru) | Нацеливающие пептиды для направленной доставки аденоассоциированных вирусов (aav) | |
| CN109844124A (zh) | 年龄相关疾病和病症的基因治疗方法 | |
| JPWO2017122789A1 (ja) | てんかん治療のためのアデノ随伴ウイルスビリオン | |
| KR20240110849A (ko) | Aadc/gdnf 폴리뉴클레오티드 및 이의 파킨슨병 치료에 있어서의 용도 | |
| TW202509226A (zh) | 用於治療與ataxin-2相關之病症的組合物及方法 | |
| TW202507009A (zh) | 用於治療與突觸融合蛋白(syntaxin)結合蛋白1缺乏相關之病症之組合物及方法 | |
| TW202507008A (zh) | 用於治療與葡萄糖神經醯胺酶β1缺陷相關之病症的組合物及方法 | |
| JP7334996B2 (ja) | グルコーストランスポーター1発現用アデノ随伴ウイルスベクター | |
| CN121488045A (zh) | Aav衣壳变体及其用途 | |
| CN114276419B (zh) | 肌肉高亲和性的新型腺相关病毒衣壳蛋白及其应用 | |
| WO2004035779A1 (ja) | ウイルスエンベロープを用いた生体分子の導入方法ならびにそのための組成物およびシステム | |
| JP2004099471A (ja) | 心筋梗塞および心不全の治療薬 | |
| JPWO2022246276A5 (https=) | ||
| JPWO2020076614A5 (https=) | ||
| CN113121654B (zh) | 腺相关病毒衣壳蛋白及包含其的腺相关病毒载体 | |
| CN112353940B (zh) | 一种用于预防或治疗抑郁症的药物及其应用 | |
| JPWO2021195591A5 (https=) | ||
| CN109069669A (zh) | 载体 | |
| ES2624659T3 (es) | Composiciones terapéuticas de SERCA2 y métodos de uso |