JPWO2021195591A5 - - Google Patents
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- JPWO2021195591A5 JPWO2021195591A5 JP2022558098A JP2022558098A JPWO2021195591A5 JP WO2021195591 A5 JPWO2021195591 A5 JP WO2021195591A5 JP 2022558098 A JP2022558098 A JP 2022558098A JP 2022558098 A JP2022558098 A JP 2022558098A JP WO2021195591 A5 JPWO2021195591 A5 JP WO2021195591A5
- Authority
- JP
- Japan
- Prior art keywords
- seq
- expression construct
- artificial expression
- composition
- injection
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
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Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2025157795A JP2026001073A (ja) | 2020-03-27 | 2025-09-24 | 非神経脳細胞での遺伝子発現を選択的に調節する人工発現構築物 |
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202063001159P | 2020-03-27 | 2020-03-27 | |
| US63/001,159 | 2020-03-27 | ||
| PCT/US2021/024525 WO2021195591A2 (en) | 2020-03-27 | 2021-03-26 | Artificial expression constructs for selectively modulating gene expression in non-neuronal brain cells |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2025157795A Division JP2026001073A (ja) | 2020-03-27 | 2025-09-24 | 非神経脳細胞での遺伝子発現を選択的に調節する人工発現構築物 |
Publications (4)
| Publication Number | Publication Date |
|---|---|
| JP2023518980A JP2023518980A (ja) | 2023-05-09 |
| JPWO2021195591A5 true JPWO2021195591A5 (https=) | 2024-02-27 |
| JP2023518980A5 JP2023518980A5 (https=) | 2024-02-27 |
| JP7749577B2 JP7749577B2 (ja) | 2025-10-06 |
Family
ID=77890746
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022558098A Active JP7749577B2 (ja) | 2020-03-27 | 2021-03-26 | 非神経脳細胞での遺伝子発現を選択的に調節する人工発現構築物 |
| JP2025157795A Pending JP2026001073A (ja) | 2020-03-27 | 2025-09-24 | 非神経脳細胞での遺伝子発現を選択的に調節する人工発現構築物 |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2025157795A Pending JP2026001073A (ja) | 2020-03-27 | 2025-09-24 | 非神経脳細胞での遺伝子発現を選択的に調節する人工発現構築物 |
Country Status (6)
| Country | Link |
|---|---|
| US (1) | US20230117172A1 (https=) |
| EP (1) | EP4127182A4 (https=) |
| JP (2) | JP7749577B2 (https=) |
| AU (1) | AU2021242353A1 (https=) |
| CA (1) | CA3173609A1 (https=) |
| WO (1) | WO2021195591A2 (https=) |
Families Citing this family (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| CA3207224A1 (en) * | 2021-02-02 | 2022-08-11 | Bryan GORE | Artificial expression constructs for modulating gene expression in gabaergic neurons and astrocytes |
| WO2023060112A1 (en) * | 2021-10-05 | 2023-04-13 | Allen Institute | Artificial expression constructs for modulating gene expression in the cerebellum and a secondary cell type |
| JP2025520385A (ja) * | 2022-06-13 | 2025-07-03 | アレン インスティテュート | 中枢神経系の非神経細胞において遺伝子発現を調節するための人工発現コンストラクト |
Family Cites Families (9)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US6602680B2 (en) | 2000-07-14 | 2003-08-05 | The Regents Of The University Of California | Production of gabaergic cells |
| US20060127358A1 (en) | 2002-05-01 | 2006-06-15 | Nicholas Muzyczka | Raav expression systems and methods for enhancing transduction of mammalian neural cells |
| US20080039413A1 (en) * | 2003-10-21 | 2008-02-14 | Morris David W | Novel compositions and methods in cancer |
| EP4154903A1 (en) * | 2008-04-22 | 2023-03-29 | Vib Vzw | Liver-specific nucleic acid regulatory elements and methods and use thereof |
| WO2013155222A2 (en) * | 2012-04-10 | 2013-10-17 | The Regents Of The University Of California | Brain-specific enhancers for cell-based therapy |
| CN110546257B (zh) * | 2017-03-17 | 2024-03-01 | 阿德夫拉姆生物技术股份有限公司 | 用于增强基因表达的组合物和方法 |
| WO2019068854A1 (en) * | 2017-10-06 | 2019-04-11 | Ospedale San Raffaele S.R.L. | GENE THERAPY OF NEURODEGENERATIVE DISEASES USING VAA VECTORS |
| US11364309B2 (en) | 2017-11-10 | 2022-06-21 | Norwegian University Of Science And Technology (Ntnu) | Neuronal enhancers |
| AU2019253700B2 (en) * | 2018-04-09 | 2025-08-14 | Allen Institute | Rescuing voltage-gated sodium channel function in inhibitory neurons |
-
2021
- 2021-03-26 CA CA3173609A patent/CA3173609A1/en active Pending
- 2021-03-26 US US17/907,385 patent/US20230117172A1/en active Pending
- 2021-03-26 EP EP21774065.3A patent/EP4127182A4/en active Pending
- 2021-03-26 WO PCT/US2021/024525 patent/WO2021195591A2/en not_active Ceased
- 2021-03-26 AU AU2021242353A patent/AU2021242353A1/en active Pending
- 2021-03-26 JP JP2022558098A patent/JP7749577B2/ja active Active
-
2025
- 2025-09-24 JP JP2025157795A patent/JP2026001073A/ja active Pending
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