JP2023518980A5 - - Google Patents

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Publication number
JP2023518980A5
JP2023518980A5 JP2022558098A JP2022558098A JP2023518980A5 JP 2023518980 A5 JP2023518980 A5 JP 2023518980A5 JP 2022558098 A JP2022558098 A JP 2022558098A JP 2022558098 A JP2022558098 A JP 2022558098A JP 2023518980 A5 JP2023518980 A5 JP 2023518980A5
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JP
Japan
Prior art keywords
seq
sequence number
sequence
expression construct
artificial expression
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JP2022558098A
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English (en)
Japanese (ja)
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JP7749577B2 (ja
JP2023518980A (ja
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Priority claimed from PCT/US2021/024525 external-priority patent/WO2021195591A2/en
Publication of JP2023518980A publication Critical patent/JP2023518980A/ja
Publication of JP2023518980A5 publication Critical patent/JP2023518980A5/ja
Priority to JP2025157795A priority Critical patent/JP2026001073A/ja
Application granted granted Critical
Publication of JP7749577B2 publication Critical patent/JP7749577B2/ja
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JP2022558098A 2020-03-27 2021-03-26 非神経脳細胞での遺伝子発現を選択的に調節する人工発現構築物 Active JP7749577B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2025157795A JP2026001073A (ja) 2020-03-27 2025-09-24 非神経脳細胞での遺伝子発現を選択的に調節する人工発現構築物

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202063001159P 2020-03-27 2020-03-27
US63/001,159 2020-03-27
PCT/US2021/024525 WO2021195591A2 (en) 2020-03-27 2021-03-26 Artificial expression constructs for selectively modulating gene expression in non-neuronal brain cells

Related Child Applications (1)

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JP2025157795A Division JP2026001073A (ja) 2020-03-27 2025-09-24 非神経脳細胞での遺伝子発現を選択的に調節する人工発現構築物

Publications (3)

Publication Number Publication Date
JP2023518980A JP2023518980A (ja) 2023-05-09
JP2023518980A5 true JP2023518980A5 (https=) 2024-02-27
JP7749577B2 JP7749577B2 (ja) 2025-10-06

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ID=77890746

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2022558098A Active JP7749577B2 (ja) 2020-03-27 2021-03-26 非神経脳細胞での遺伝子発現を選択的に調節する人工発現構築物
JP2025157795A Pending JP2026001073A (ja) 2020-03-27 2025-09-24 非神経脳細胞での遺伝子発現を選択的に調節する人工発現構築物

Family Applications After (1)

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JP2025157795A Pending JP2026001073A (ja) 2020-03-27 2025-09-24 非神経脳細胞での遺伝子発現を選択的に調節する人工発現構築物

Country Status (6)

Country Link
US (1) US20230117172A1 (https=)
EP (1) EP4127182A4 (https=)
JP (2) JP7749577B2 (https=)
AU (1) AU2021242353A1 (https=)
CA (1) CA3173609A1 (https=)
WO (1) WO2021195591A2 (https=)

Families Citing this family (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
AU2022217778A1 (en) * 2021-02-02 2023-08-31 Allen Institute Artificial expression constructs for modulating gene expression in gabaergic neurons and astrocytes
EP4413142A4 (en) * 2021-10-05 2025-11-05 Allen Inst ARTIFICIAL EXPRESSION CONSTRUCTIONS TO MODULATE GENE EXPRESSION IN THE CEREBELLUM AND IN A SECONDARY CELL TYPE
JP2025520385A (ja) * 2022-06-13 2025-07-03 アレン インスティテュート 中枢神経系の非神経細胞において遺伝子発現を調節するための人工発現コンストラクト

Family Cites Families (9)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US6602680B2 (en) * 2000-07-14 2003-08-05 The Regents Of The University Of California Production of gabaergic cells
WO2003093479A1 (en) * 2002-05-01 2003-11-13 University Of Florida Research Foundation, Inc. Improved raav expression systems and methods for enhancing transduction of mammalian neural cells
US20080039413A1 (en) * 2003-10-21 2008-02-14 Morris David W Novel compositions and methods in cancer
CA2722238C (en) * 2008-04-22 2017-11-28 Life Sciences Research Partners Vzw Liver-specific nucleic acid regulatory elements and methods and use thereof
WO2013155222A2 (en) * 2012-04-10 2013-10-17 The Regents Of The University Of California Brain-specific enhancers for cell-based therapy
EP4653536A3 (en) * 2017-03-17 2026-02-25 Adverum Biotechnologies, Inc. Compositions and methods for enhanced gene expression
WO2019068854A1 (en) * 2017-10-06 2019-04-11 Ospedale San Raffaele S.R.L. GENE THERAPY OF NEURODEGENERATIVE DISEASES USING VAA VECTORS
US11364309B2 (en) * 2017-11-10 2022-06-21 Norwegian University Of Science And Technology (Ntnu) Neuronal enhancers
CA3096407A1 (en) * 2018-04-09 2019-10-17 Allen Institute Rescuing voltage-gated sodium channel function in inhibitory neurons

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