JP2023518980A5 - - Google Patents

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Publication number
JP2023518980A5
JP2023518980A5 JP2022558098A JP2022558098A JP2023518980A5 JP 2023518980 A5 JP2023518980 A5 JP 2023518980A5 JP 2022558098 A JP2022558098 A JP 2022558098A JP 2022558098 A JP2022558098 A JP 2022558098A JP 2023518980 A5 JP2023518980 A5 JP 2023518980A5
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JP
Japan
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JP2022558098A
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Japanese (ja)
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JPWO2021195591A5 (https=
JP2023518980A (ja
JP7749577B2 (ja
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Priority claimed from PCT/US2021/024525 external-priority patent/WO2021195591A2/en
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Priority to JP2025157795A priority Critical patent/JP2026001073A/ja
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JP2022558098A 2020-03-27 2021-03-26 非神経脳細胞での遺伝子発現を選択的に調節する人工発現構築物 Active JP7749577B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2025157795A JP2026001073A (ja) 2020-03-27 2025-09-24 非神経脳細胞での遺伝子発現を選択的に調節する人工発現構築物

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202063001159P 2020-03-27 2020-03-27
US63/001,159 2020-03-27
PCT/US2021/024525 WO2021195591A2 (en) 2020-03-27 2021-03-26 Artificial expression constructs for selectively modulating gene expression in non-neuronal brain cells

Related Child Applications (1)

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JP2025157795A Division JP2026001073A (ja) 2020-03-27 2025-09-24 非神経脳細胞での遺伝子発現を選択的に調節する人工発現構築物

Publications (4)

Publication Number Publication Date
JP2023518980A JP2023518980A (ja) 2023-05-09
JPWO2021195591A5 JPWO2021195591A5 (https=) 2024-02-27
JP2023518980A5 true JP2023518980A5 (https=) 2024-02-27
JP7749577B2 JP7749577B2 (ja) 2025-10-06

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JP2022558098A Active JP7749577B2 (ja) 2020-03-27 2021-03-26 非神経脳細胞での遺伝子発現を選択的に調節する人工発現構築物
JP2025157795A Pending JP2026001073A (ja) 2020-03-27 2025-09-24 非神経脳細胞での遺伝子発現を選択的に調節する人工発現構築物

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JP2025157795A Pending JP2026001073A (ja) 2020-03-27 2025-09-24 非神経脳細胞での遺伝子発現を選択的に調節する人工発現構築物

Country Status (6)

Country Link
US (1) US20230117172A1 (https=)
EP (1) EP4127182A4 (https=)
JP (2) JP7749577B2 (https=)
AU (1) AU2021242353A1 (https=)
CA (1) CA3173609A1 (https=)
WO (1) WO2021195591A2 (https=)

Families Citing this family (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CA3207224A1 (en) * 2021-02-02 2022-08-11 Bryan GORE Artificial expression constructs for modulating gene expression in gabaergic neurons and astrocytes
WO2023060112A1 (en) * 2021-10-05 2023-04-13 Allen Institute Artificial expression constructs for modulating gene expression in the cerebellum and a secondary cell type
JP2025520385A (ja) * 2022-06-13 2025-07-03 アレン インスティテュート 中枢神経系の非神経細胞において遺伝子発現を調節するための人工発現コンストラクト

Family Cites Families (9)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US6602680B2 (en) 2000-07-14 2003-08-05 The Regents Of The University Of California Production of gabaergic cells
US20060127358A1 (en) 2002-05-01 2006-06-15 Nicholas Muzyczka Raav expression systems and methods for enhancing transduction of mammalian neural cells
US20080039413A1 (en) * 2003-10-21 2008-02-14 Morris David W Novel compositions and methods in cancer
EP4154903A1 (en) * 2008-04-22 2023-03-29 Vib Vzw Liver-specific nucleic acid regulatory elements and methods and use thereof
WO2013155222A2 (en) * 2012-04-10 2013-10-17 The Regents Of The University Of California Brain-specific enhancers for cell-based therapy
CN110546257B (zh) * 2017-03-17 2024-03-01 阿德夫拉姆生物技术股份有限公司 用于增强基因表达的组合物和方法
WO2019068854A1 (en) * 2017-10-06 2019-04-11 Ospedale San Raffaele S.R.L. GENE THERAPY OF NEURODEGENERATIVE DISEASES USING VAA VECTORS
US11364309B2 (en) 2017-11-10 2022-06-21 Norwegian University Of Science And Technology (Ntnu) Neuronal enhancers
AU2019253700B2 (en) * 2018-04-09 2025-08-14 Allen Institute Rescuing voltage-gated sodium channel function in inhibitory neurons

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