JPWO2022178298A5 - - Google Patents

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Publication number
JPWO2022178298A5
JPWO2022178298A5 JP2023550062A JP2023550062A JPWO2022178298A5 JP WO2022178298 A5 JPWO2022178298 A5 JP WO2022178298A5 JP 2023550062 A JP2023550062 A JP 2023550062A JP 2023550062 A JP2023550062 A JP 2023550062A JP WO2022178298 A5 JPWO2022178298 A5 JP WO2022178298A5
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JP
Japan
Prior art keywords
pharmaceutical composition
nucleic acid
acid vector
subject
otof
Prior art date
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Pending
Application number
JP2023550062A
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English (en)
Japanese (ja)
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JP2024507837A (ja
JP2024507837A5 (https=
Publication date
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Priority claimed from PCT/US2022/017058 external-priority patent/WO2022178298A1/en
Publication of JP2024507837A publication Critical patent/JP2024507837A/ja
Publication of JPWO2022178298A5 publication Critical patent/JPWO2022178298A5/ja
Publication of JP2024507837A5 publication Critical patent/JP2024507837A5/ja
Pending legal-status Critical Current

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JP2023550062A 2021-02-19 2022-02-18 オトフェリン二重ベクター系を使用して、感音難聴を治療するための組成物 Pending JP2024507837A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163151589P 2021-02-19 2021-02-19
US63/151,589 2021-02-19
PCT/US2022/017058 WO2022178298A1 (en) 2021-02-19 2022-02-18 Methods for treating sensorineural hearing loss using otoferlin dual vector systems

Publications (3)

Publication Number Publication Date
JP2024507837A JP2024507837A (ja) 2024-02-21
JPWO2022178298A5 true JPWO2022178298A5 (https=) 2025-02-25
JP2024507837A5 JP2024507837A5 (https=) 2025-02-25

Family

ID=82931783

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023550062A Pending JP2024507837A (ja) 2021-02-19 2022-02-18 オトフェリン二重ベクター系を使用して、感音難聴を治療するための組成物

Country Status (7)

Country Link
US (1) US20240148905A1 (https=)
EP (1) EP4294460A4 (https=)
JP (1) JP2024507837A (https=)
KR (1) KR20240004253A (https=)
CN (1) CN117295529A (https=)
MX (1) MX2023009714A (https=)
WO (1) WO2022178298A1 (https=)

Families Citing this family (10)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CN119410636A (zh) 2018-04-27 2025-02-11 分贝治疗公司 肌球蛋白15启动子及其用途
WO2020123713A1 (en) * 2018-12-11 2020-06-18 Decibel Therapeutics, Inc. Compositions and methods for the delivery of therapeutic agents across the round window membrane
EP3921032A4 (en) 2019-02-08 2022-11-30 Decibel Therapeutics, Inc. COMPOSITIONS AND METHODS FOR TREATMENT OF SENSORINEURAL HEARING LOSS USING OTOFERLIN DOUBLE VECTOR SYSTEMS
AU2020218547A1 (en) 2019-02-08 2021-08-26 Decibel Therapeutics, Inc. Myosin 15 promoters and uses thereof
CA3159549A1 (en) 2019-10-30 2021-05-06 Decibel Therapeutics, Inc. Compositions and methods for treating sensorineural hearing loss using otoferlin dual vector systems
JP7807380B2 (ja) 2020-02-21 2026-01-27 アコーオス インコーポレイテッド ヒト対象において非加齢関連聴力障害を処置するための組成物および方法
WO2023036966A1 (en) * 2021-09-10 2023-03-16 Institut Pasteur Dual recombinant aav8 vector system encoding isoform 5 of otoferlin and uses thereof
CN117305367A (zh) * 2023-08-21 2023-12-29 复旦大学附属眼耳鼻喉科医院 一种表达全长耳畸蛋白的双aav载体系统及其应用
WO2025201333A1 (zh) * 2024-03-28 2025-10-02 苏州星奥拓维生物技术有限公司 递送Otof基因的双载体系统和其用途
WO2025221253A1 (en) * 2024-04-17 2025-10-23 Decibel Therapeutics, Inc. Methods for treating sensorineural hearing loss using otoferlin dual vector systems

Family Cites Families (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
JP2019530737A (ja) * 2016-08-23 2019-10-24 アコーオス インコーポレイテッド ヒト対象において非加齢性聴力障害を治療するための組成物および方法
IL325122A (en) * 2018-02-22 2026-02-01 Akouos Inc Compositions and methods for treating non-age-related hearing impairment in humans
US11660353B2 (en) * 2018-04-27 2023-05-30 Decibel Therapeutics, Inc. Compositions and methods for treating sensorineural hearing loss using otoferlin dual vector systems
US12188041B2 (en) * 2018-11-01 2025-01-07 University Of Florida Research Foundation, Incorporated Codon optimized otoferlin AAV dual vector gene therapy
WO2020148458A1 (en) * 2019-01-18 2020-07-23 Institut Pasteur Aav-mediated gene therapy restoring the otoferlin gene
EP3921032A4 (en) * 2019-02-08 2022-11-30 Decibel Therapeutics, Inc. COMPOSITIONS AND METHODS FOR TREATMENT OF SENSORINEURAL HEARING LOSS USING OTOFERLIN DOUBLE VECTOR SYSTEMS

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