JPWO2021016032A5 - - Google Patents
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- Publication number
- JPWO2021016032A5 JPWO2021016032A5 JP2022500671A JP2022500671A JPWO2021016032A5 JP WO2021016032 A5 JPWO2021016032 A5 JP WO2021016032A5 JP 2022500671 A JP2022500671 A JP 2022500671A JP 2022500671 A JP2022500671 A JP 2022500671A JP WO2021016032 A5 JPWO2021016032 A5 JP WO2021016032A5
- Authority
- JP
- Japan
- Prior art keywords
- antisense compound
- administered
- salt
- human subject
- composition
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Granted
Links
Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2023077805A JP2023100911A (ja) | 2019-07-19 | 2023-05-10 | 脊髄性筋萎縮症を処置または予防する方法 |
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201962876360P | 2019-07-19 | 2019-07-19 | |
| US62/876,360 | 2019-07-19 | ||
| PCT/US2020/042312 WO2021016032A1 (en) | 2019-07-19 | 2020-07-16 | Methods of treating or preventing spinal muscular atrophy |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023077805A Division JP2023100911A (ja) | 2019-07-19 | 2023-05-10 | 脊髄性筋萎縮症を処置または予防する方法 |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2022540993A JP2022540993A (ja) | 2022-09-21 |
| JPWO2021016032A5 true JPWO2021016032A5 (es) | 2023-03-10 |
| JP7279253B2 JP7279253B2 (ja) | 2023-05-22 |
Family
ID=71995097
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022500671A Active JP7279253B2 (ja) | 2019-07-19 | 2020-07-16 | 脊髄性筋萎縮症を処置または予防する方法 |
| JP2023077805A Pending JP2023100911A (ja) | 2019-07-19 | 2023-05-10 | 脊髄性筋萎縮症を処置または予防する方法 |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023077805A Pending JP2023100911A (ja) | 2019-07-19 | 2023-05-10 | 脊髄性筋萎縮症を処置または予防する方法 |
Country Status (31)
| Country | Link |
|---|---|
| US (1) | US20220325282A1 (es) |
| EP (2) | EP4335503A3 (es) |
| JP (2) | JP7279253B2 (es) |
| KR (1) | KR20220042113A (es) |
| CN (1) | CN114302727A (es) |
| AR (1) | AR119430A1 (es) |
| AU (1) | AU2020316997A1 (es) |
| BR (1) | BR112022000870A2 (es) |
| CA (1) | CA3149906A1 (es) |
| CL (1) | CL2021003602A1 (es) |
| CO (1) | CO2022001354A2 (es) |
| CR (1) | CR20220071A (es) |
| DK (1) | DK3999643T5 (es) |
| ES (1) | ES2966791T3 (es) |
| FI (1) | FI3999643T3 (es) |
| HR (1) | HRP20231515T1 (es) |
| HU (1) | HUE064071T2 (es) |
| IL (1) | IL289745A (es) |
| JO (1) | JOP20220007A1 (es) |
| LT (1) | LT3999643T (es) |
| MA (1) | MA62935B1 (es) |
| MD (1) | MD3999643T2 (es) |
| MX (1) | MX2022000441A (es) |
| PE (1) | PE20220941A1 (es) |
| PL (1) | PL3999643T3 (es) |
| PT (1) | PT3999643T (es) |
| RS (1) | RS64879B1 (es) |
| SI (1) | SI3999643T1 (es) |
| TW (1) | TWI841762B (es) |
| UY (1) | UY38790A (es) |
| WO (1) | WO2021016032A1 (es) |
Families Citing this family (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2015161170A2 (en) | 2014-04-17 | 2015-10-22 | Isis Pharmaceuticals, Inc. | Compositions and methods for modulation of smn2 splicing in a subject |
| BR112017004056A2 (pt) | 2014-09-12 | 2017-12-05 | Biogen Ma Inc | composições e métodos para detecção da proteína smn em um indivíduo e tratamento de um indivíduo |
| WO2024138018A1 (en) * | 2022-12-23 | 2024-06-27 | University Of Pittsburgh - Of The Commonwealth System Of Higher Education | Treatment of gemin5-mediated disorders |
Family Cites Families (12)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| PL3308788T3 (pl) | 2005-06-23 | 2019-05-31 | Biogen Ma Inc | Kompozycje i sposoby modulacji splicingu smn2 |
| WO2008157753A1 (en) * | 2007-06-21 | 2008-12-24 | Sma Foundation | Methods of treatment for spinal muscular atrophy |
| KR20120093138A (ko) * | 2009-06-17 | 2012-08-22 | 콜드스프링하버러보러토리 | 대상에게서 ｓｍｎ２ 스플라이싱을 조정하기 위한 조성물 및 방법 |
| WO2011032109A1 (en) | 2009-09-11 | 2011-03-17 | Sma Foundation | Biomarkers for spinal muscular atrophy |
| EP2714037B1 (en) * | 2011-05-25 | 2016-07-13 | Université Paris Descartes | Erk inhibitors for use in treating spinal muscular atrophy |
| US9926559B2 (en) * | 2013-01-09 | 2018-03-27 | Biogen Ma Inc. | Compositions and methods for modulation of SMN2 splicing in a subject |
| BR112017004056A2 (pt) * | 2014-09-12 | 2017-12-05 | Biogen Ma Inc | composições e métodos para detecção da proteína smn em um indivíduo e tratamento de um indivíduo |
| SG11201900238UA (en) * | 2016-07-15 | 2019-02-27 | Ionis Pharmaceuticals Inc | Compounds and methods for modulation of smn2 |
| TW201927241A (zh) | 2017-12-21 | 2019-07-16 | 瑞士商赫孚孟拉羅股份公司 | 用於肌肉失能之數位生物標記 |
| KR20200112906A (ko) | 2018-01-25 | 2020-10-05 | 바이오젠 엠에이 인코포레이티드 | 척추 근위축증의 치료 방법 |
| IT201800004359A1 (it) | 2018-04-10 | 2019-10-10 | IDENTIFICAZIONE DI miRNA MUSCOLARI COME BIOMARCATORI E TRATTAMENTO CO-ADIUVANTE PER L’ATROFIA MUSCOLARE SPINALE | |
| JP2021534154A (ja) * | 2018-08-15 | 2021-12-09 | バイオジェン・エムエイ・インコーポレイテッドBiogen MA Inc. | 脊髄性筋萎縮症のための併用療法 |
-
2020
- 2020-07-16 DK DK20753556.8T patent/DK3999643T5/da active
- 2020-07-16 UY UY0001038790A patent/UY38790A/es unknown
- 2020-07-16 JO JOP/2022/0007A patent/JOP20220007A1/ar unknown
- 2020-07-16 EP EP23210526.2A patent/EP4335503A3/en active Pending
- 2020-07-16 SI SI202030323T patent/SI3999643T1/sl unknown
- 2020-07-16 MX MX2022000441A patent/MX2022000441A/es unknown
- 2020-07-16 PL PL20753556.8T patent/PL3999643T3/pl unknown
- 2020-07-16 PE PE2021002322A patent/PE20220941A1/es unknown
- 2020-07-16 EP EP20753556.8A patent/EP3999643B1/en active Active
- 2020-07-16 JP JP2022500671A patent/JP7279253B2/ja active Active
- 2020-07-16 WO PCT/US2020/042312 patent/WO2021016032A1/en active Application Filing
- 2020-07-16 US US17/626,324 patent/US20220325282A1/en active Pending
- 2020-07-16 HR HRP20231515TT patent/HRP20231515T1/hr unknown
- 2020-07-16 PT PT207535568T patent/PT3999643T/pt unknown
- 2020-07-16 MA MA62935A patent/MA62935B1/fr unknown
- 2020-07-16 CA CA3149906A patent/CA3149906A1/en active Pending
- 2020-07-16 AU AU2020316997A patent/AU2020316997A1/en active Pending
- 2020-07-16 KR KR1020227001151A patent/KR20220042113A/ko unknown
- 2020-07-16 ES ES20753556T patent/ES2966791T3/es active Active
- 2020-07-16 RS RS20231128A patent/RS64879B1/sr unknown
- 2020-07-16 BR BR112022000870A patent/BR112022000870A2/pt unknown
- 2020-07-16 MD MDE20220574T patent/MD3999643T2/ro unknown
- 2020-07-16 HU HUE20753556A patent/HUE064071T2/hu unknown
- 2020-07-16 CN CN202080049461.1A patent/CN114302727A/zh active Pending
- 2020-07-16 FI FIEP20753556.8T patent/FI3999643T3/fi active
- 2020-07-16 LT LTEPPCT/US2020/042312T patent/LT3999643T/lt unknown
- 2020-07-16 CR CR20220071A patent/CR20220071A/es unknown
- 2020-07-17 AR ARP200102019A patent/AR119430A1/es unknown
- 2020-07-17 TW TW109124224A patent/TWI841762B/zh active
-
2021
- 2021-12-31 CL CL2021003602A patent/CL2021003602A1/es unknown
-
2022
- 2022-01-10 IL IL289745A patent/IL289745A/en unknown
- 2022-02-10 CO CONC2022/0001354A patent/CO2022001354A2/es unknown
-
2023
- 2023-05-10 JP JP2023077805A patent/JP2023100911A/ja active Pending
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