JPWO2020214668A5 - - Google Patents
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- Publication number
- JPWO2020214668A5 JPWO2020214668A5 JP2021561742A JP2021561742A JPWO2020214668A5 JP WO2020214668 A5 JPWO2020214668 A5 JP WO2020214668A5 JP 2021561742 A JP2021561742 A JP 2021561742A JP 2021561742 A JP2021561742 A JP 2021561742A JP WO2020214668 A5 JPWO2020214668 A5 JP WO2020214668A5
- Authority
- JP
- Japan
- Prior art keywords
- seq
- raav
- variant
- polynucleotide
- medicament
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Granted
Links
Applications Claiming Priority (7)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201962833972P | 2019-04-15 | 2019-04-15 | |
| US62/833,972 | 2019-04-15 | ||
| US201962926308P | 2019-10-25 | 2019-10-25 | |
| US62/926,308 | 2019-10-25 | ||
| US202062967214P | 2020-01-29 | 2020-01-29 | |
| US62/967,214 | 2020-01-29 | ||
| PCT/US2020/028264 WO2020214668A1 (en) | 2019-04-15 | 2020-04-15 | Compositions and methods for treatment of cystic fibrosis |
Publications (4)
| Publication Number | Publication Date |
|---|---|
| JP2022529457A JP2022529457A (ja) | 2022-06-22 |
| JPWO2020214668A5 true JPWO2020214668A5 (https=) | 2023-04-18 |
| JP2022529457A5 JP2022529457A5 (https=) | 2023-04-18 |
| JP7731801B2 JP7731801B2 (ja) | 2025-09-01 |
Family
ID=70847479
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021561742A Active JP7731801B2 (ja) | 2019-04-15 | 2020-04-15 | 嚢胞性線維症の治療のための組換えアデノ随伴ウイルス |
Country Status (14)
| Country | Link |
|---|---|
| US (1) | US20220241436A1 (https=) |
| EP (1) | EP3955971A1 (https=) |
| JP (1) | JP7731801B2 (https=) |
| KR (1) | KR20220044899A (https=) |
| CN (1) | CN114641318A (https=) |
| AU (1) | AU2020260076A1 (https=) |
| BR (1) | BR112021020708A2 (https=) |
| CA (1) | CA3137015A1 (https=) |
| CL (1) | CL2021002702A1 (https=) |
| IL (1) | IL287260A (https=) |
| MX (1) | MX2021012681A (https=) |
| PH (1) | PH12021552610A1 (https=) |
| SG (1) | SG11202111334SA (https=) |
| WO (1) | WO2020214668A1 (https=) |
Families Citing this family (8)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2017139381A1 (en) | 2016-02-08 | 2017-08-17 | University Of Iowa Research Foundation | Methods to produce chimeric adeno-associated virus/bocavirus parvovirus |
| CA3198936A1 (en) | 2016-03-07 | 2017-09-14 | University Of Iowa Research Foundation | Aav-mediated expression using a synthetic promoter and enhancer |
| US12173305B2 (en) | 2016-05-26 | 2024-12-24 | University Of Iowa Research Foundation | cis and trans requirements for terminal resolution of human bocavirus 1 |
| US11142775B2 (en) | 2017-01-13 | 2021-10-12 | University Of Iowa Research Foundation | Bocaparvovirus small noncoding RNA and uses thereof |
| EP3955970A1 (en) * | 2019-04-15 | 2022-02-23 | University Of Iowa Research Foundation | Methods and compositions for transgene expression |
| US20230242941A1 (en) * | 2020-06-30 | 2023-08-03 | Eric Yuen | Methods and compositions for administering recombinant viral vectors |
| US20240115738A1 (en) | 2021-04-15 | 2024-04-11 | Spirovant Sciences, Inc. | Methods and compositions for treatment of cystic fibrosis |
| WO2026072721A1 (en) * | 2024-09-25 | 2026-04-02 | Carbon Biosciences, Inc. | Parvovirus compositions and methods for gene therapy |
Family Cites Families (15)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US5478745A (en) | 1992-12-04 | 1995-12-26 | University Of Pittsburgh | Recombinant viral vector system |
| PT728214E (pt) | 1993-11-09 | 2004-11-30 | Ohio Med College | Linhas celulares estaveis capazes de expressar o gene de replicacao do virus adeno-associado |
| PT733103E (pt) | 1993-11-09 | 2004-07-30 | Targeted Genetics Corp | Criacao de elevados titulos de vectores de aav recombinantes |
| US5656785A (en) | 1995-08-07 | 1997-08-12 | The Charles Stark Draper Laboratory, Inc. | Micromechanical contact load force sensor for sensing magnitude and distribution of loads and tool employing micromechanical contact load force sensor |
| AU5445998A (en) | 1996-11-19 | 1998-06-10 | Surgx Corporation | A transient voltage protection device and method of making same |
| AU741605B2 (en) | 1996-12-18 | 2001-12-06 | Targeted Genetics Corporation | AAV split-packaging genes and cell lines comprising such genes for use in the production of recombinant AAV vectors |
| JP2007524379A (ja) | 2003-03-31 | 2007-08-30 | ユニバーシテイ・オブ・アイオワ・リサーチ・フアウンデーシヨン | 上皮ナトリウムチャンネル関連障害のＰｈａｒｍｉｃｏ−遺伝子治療 |
| US9233131B2 (en) * | 2003-06-30 | 2016-01-12 | The Regents Of The University Of California | Mutant adeno-associated virus virions and methods of use thereof |
| WO2005056762A2 (en) * | 2003-12-05 | 2005-06-23 | University Of Iowa Research Foundation | Truncated cmv promoters and vectors containing same |
| KR20210122917A (ko) * | 2013-03-14 | 2021-10-12 | 샤이어 휴먼 지네틱 테라피즈 인크. | Cftr mrna 조성물 및 관련 방법 및 사용 |
| AU2014251099B2 (en) * | 2013-04-08 | 2019-01-17 | The University Of Kansas | Chimeric adeno-associated virus/ bocavirus parvovirus vector |
| US11000597B2 (en) * | 2015-01-21 | 2021-05-11 | University Of Florida Research Foundation, Incorporated | Engineered receptor/ligand system for delivery of therapeutic agents |
| CA3198936A1 (en) * | 2016-03-07 | 2017-09-14 | University Of Iowa Research Foundation | Aav-mediated expression using a synthetic promoter and enhancer |
| US10550405B2 (en) * | 2017-03-15 | 2020-02-04 | The University Of North Carolina At Chapel Hill | Rational polyploid adeno-associated virus vectors and methods of making and using the same |
| EP3955970A1 (en) * | 2019-04-15 | 2022-02-23 | University Of Iowa Research Foundation | Methods and compositions for transgene expression |
-
2020
- 2020-04-15 US US17/603,831 patent/US20220241436A1/en not_active Abandoned
- 2020-04-15 JP JP2021561742A patent/JP7731801B2/ja active Active
- 2020-04-15 WO PCT/US2020/028264 patent/WO2020214668A1/en not_active Ceased
- 2020-04-15 PH PH1/2021/552610A patent/PH12021552610A1/en unknown
- 2020-04-15 KR KR1020217037210A patent/KR20220044899A/ko not_active Ceased
- 2020-04-15 MX MX2021012681A patent/MX2021012681A/es unknown
- 2020-04-15 SG SG11202111334SA patent/SG11202111334SA/en unknown
- 2020-04-15 AU AU2020260076A patent/AU2020260076A1/en active Pending
- 2020-04-15 BR BR112021020708A patent/BR112021020708A2/pt unknown
- 2020-04-15 CN CN202080043595.2A patent/CN114641318A/zh active Pending
- 2020-04-15 CA CA3137015A patent/CA3137015A1/en active Pending
- 2020-04-15 EP EP20728248.4A patent/EP3955971A1/en active Pending
-
2021
- 2021-10-14 IL IL287260A patent/IL287260A/en unknown
- 2021-10-15 CL CL2021002702A patent/CL2021002702A1/es unknown
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