JPWO2020069461A5 - - Google Patents

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Publication number
JPWO2020069461A5
JPWO2020069461A5 JP2021517461A JP2021517461A JPWO2020069461A5 JP WO2020069461 A5 JPWO2020069461 A5 JP WO2020069461A5 JP 2021517461 A JP2021517461 A JP 2021517461A JP 2021517461 A JP2021517461 A JP 2021517461A JP WO2020069461 A5 JPWO2020069461 A5 JP WO2020069461A5
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JP
Japan
Prior art keywords
vector genome
aav vector
sequence
seq
aav
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2021517461A
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English (en)
Japanese (ja)
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JP2022500066A (ja
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Application filed filed Critical
Priority claimed from PCT/US2019/053681 external-priority patent/WO2020069461A1/en
Publication of JP2022500066A publication Critical patent/JP2022500066A/ja
Publication of JPWO2020069461A5 publication Critical patent/JPWO2020069461A5/ja
Priority to JP2024021997A priority Critical patent/JP2024073447A/ja
Pending legal-status Critical Current

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JP2021517461A 2018-09-28 2019-09-27 操作されたプロモータを有するフラタキシン発現コンストラクトおよびその使用方法 Pending JP2022500066A (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2024021997A JP2024073447A (ja) 2018-09-28 2024-02-16 操作されたプロモータを有するフラタキシン発現コンストラクトおよびその使用方法

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201862738519P 2018-09-28 2018-09-28
US62/738,519 2018-09-28
US201962901769P 2019-09-17 2019-09-17
US62/901,769 2019-09-17
PCT/US2019/053681 WO2020069461A1 (en) 2018-09-28 2019-09-27 Frataxin expression constructs having engineered promoters and methods of use thereof

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2024021997A Division JP2024073447A (ja) 2018-09-28 2024-02-16 操作されたプロモータを有するフラタキシン発現コンストラクトおよびその使用方法

Publications (2)

Publication Number Publication Date
JP2022500066A JP2022500066A (ja) 2022-01-04
JPWO2020069461A5 true JPWO2020069461A5 (ko) 2022-10-04

Family

ID=68426807

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2021517461A Pending JP2022500066A (ja) 2018-09-28 2019-09-27 操作されたプロモータを有するフラタキシン発現コンストラクトおよびその使用方法
JP2024021997A Pending JP2024073447A (ja) 2018-09-28 2024-02-16 操作されたプロモータを有するフラタキシン発現コンストラクトおよびその使用方法

Family Applications After (1)

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JP2024021997A Pending JP2024073447A (ja) 2018-09-28 2024-02-16 操作されたプロモータを有するフラタキシン発現コンストラクトおよびその使用方法

Country Status (9)

Country Link
US (1) US20210395776A1 (ko)
EP (1) EP3856762A1 (ko)
JP (2) JP2022500066A (ko)
KR (1) KR20210068068A (ko)
CN (1) CN113383010A (ko)
AU (1) AU2019346655A1 (ko)
CA (1) CA3114621A1 (ko)
SG (1) SG11202103151RA (ko)
WO (1) WO2020069461A1 (ko)

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CN116041443B (zh) * 2022-12-30 2023-09-22 广州派真生物技术有限公司 腺相关病毒突变体及其应用
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