JPWO2020069461A5 - - Google Patents

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JPWO2020069461A5
JPWO2020069461A5 JP2021517461A JP2021517461A JPWO2020069461A5 JP WO2020069461 A5 JPWO2020069461 A5 JP WO2020069461A5 JP 2021517461 A JP2021517461 A JP 2021517461A JP 2021517461 A JP2021517461 A JP 2021517461A JP WO2020069461 A5 JPWO2020069461 A5 JP WO2020069461A5
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vector genome
aav vector
sequence
seq
aav
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JP2021517461A
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JP7528066B2 (ja
JP2022500066A (ja
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Priority claimed from PCT/US2019/053681 external-priority patent/WO2020069461A1/en
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JP2021517461A 2018-09-28 2019-09-27 操作されたプロモータを有するフラタキシン発現コンストラクトおよびその使用方法 Active JP7528066B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2024021997A JP2024073447A (ja) 2018-09-28 2024-02-16 操作されたプロモータを有するフラタキシン発現コンストラクトおよびその使用方法

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201862738519P 2018-09-28 2018-09-28
US62/738,519 2018-09-28
US201962901769P 2019-09-17 2019-09-17
US62/901,769 2019-09-17
PCT/US2019/053681 WO2020069461A1 (en) 2018-09-28 2019-09-27 Frataxin expression constructs having engineered promoters and methods of use thereof

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JP2024021997A Division JP2024073447A (ja) 2018-09-28 2024-02-16 操作されたプロモータを有するフラタキシン発現コンストラクトおよびその使用方法

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JP2022500066A JP2022500066A (ja) 2022-01-04
JPWO2020069461A5 true JPWO2020069461A5 (es) 2022-10-04
JP7528066B2 JP7528066B2 (ja) 2024-08-05

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JP2021517461A Active JP7528066B2 (ja) 2018-09-28 2019-09-27 操作されたプロモータを有するフラタキシン発現コンストラクトおよびその使用方法
JP2024021997A Pending JP2024073447A (ja) 2018-09-28 2024-02-16 操作されたプロモータを有するフラタキシン発現コンストラクトおよびその使用方法

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Country Status (9)

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US (1) US20210395776A1 (es)
EP (1) EP3856762A1 (es)
JP (2) JP7528066B2 (es)
KR (1) KR20210068068A (es)
CN (1) CN113383010A (es)
AU (1) AU2019346655A1 (es)
CA (1) CA3114621A1 (es)
SG (1) SG11202103151RA (es)
WO (1) WO2020069461A1 (es)

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CN116041443B (zh) * 2022-12-30 2023-09-22 广州派真生物技术有限公司 腺相关病毒突变体及其应用
CN117624311B (zh) * 2023-11-29 2024-05-28 广州译码基因科技有限公司 可提高aav病毒神经靶向性的衣壳蛋白突变体及其应用
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