JPWO2019241206A5 - - Google Patents
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- Publication number
- JPWO2019241206A5 JPWO2019241206A5 JP2020569147A JP2020569147A JPWO2019241206A5 JP WO2019241206 A5 JPWO2019241206 A5 JP WO2019241206A5 JP 2020569147 A JP2020569147 A JP 2020569147A JP 2020569147 A JP2020569147 A JP 2020569147A JP WO2019241206 A5 JPWO2019241206 A5 JP WO2019241206A5
- Authority
- JP
- Japan
- Prior art keywords
- seq
- aav2 vector
- recombinant aav2
- vector according
- sequence
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Granted
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201862683501P | 2018-06-11 | 2018-06-11 | |
| US62/683,501 | 2018-06-11 | ||
| PCT/US2019/036487 WO2019241206A1 (en) | 2018-06-11 | 2019-06-11 | Recombinant aav vectors and methods of using the same |
Publications (4)
| Publication Number | Publication Date |
|---|---|
| JP2021526834A JP2021526834A (ja) | 2021-10-11 |
| JP2021526834A5 JP2021526834A5 (https=) | 2022-06-15 |
| JPWO2019241206A5 true JPWO2019241206A5 (https=) | 2022-06-15 |
| JP7470057B2 JP7470057B2 (ja) | 2024-04-17 |
Family
ID=67138055
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2020569147A Active JP7470057B2 (ja) | 2018-06-11 | 2019-06-11 | 組み換えａａｖベクター及びその使用方法 |
Country Status (8)
| Country | Link |
|---|---|
| US (1) | US20210189424A1 (https=) |
| EP (1) | EP3802840A1 (https=) |
| JP (1) | JP7470057B2 (https=) |
| KR (1) | KR102946006B1 (https=) |
| CN (1) | CN112384625A (https=) |
| AU (1) | AU2019286386B2 (https=) |
| CA (1) | CA3103231A1 (https=) |
| WO (1) | WO2019241206A1 (https=) |
Families Citing this family (4)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| KR20240014102A (ko) | 2018-06-29 | 2024-01-31 | 우한 뉴로프스 바이오테크놀로지 리미티드 컴퍼니 | 레버 유전성 시신경병증의 치료를 위한 조성물 및 방법 |
| CA3109432A1 (en) * | 2018-08-20 | 2020-02-27 | Wuhan Neurophth Biotechnology Limited Company | Compositions and methods for treating leber's hereditary optic neuropathy |
| CN113025633B (zh) | 2019-12-09 | 2024-08-27 | 武汉纽福斯生物科技有限公司 | 编码人nadh脱氢酶亚单位1蛋白的核酸及其应用 |
| CN115710585B (zh) * | 2021-08-23 | 2025-03-28 | 纽福斯(苏州)生物科技有限公司 | 编码nd4的核酸及其用途 |
Family Cites Families (8)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US6218117B1 (en) * | 1998-06-15 | 2001-04-17 | Mitokor | Compositions and methods for identifying agents that quantitatively alter detectable extramitochondrial DNA:mitochondrial DNA ratios |
| ES2541771T3 (es) | 2005-05-03 | 2015-07-24 | INSERM (Institut National de la Santé et de la Recherche Médicale) | Expresión de una proteína mitocondrial mediante un enfoque alotópico mejorado |
| EP2121914B1 (en) * | 2007-02-16 | 2014-08-20 | John Guy | Mitochondrial nucleic acid delivery systems |
| DE102010013829A1 (de) * | 2010-03-26 | 2011-09-29 | Carl Zeiss Microlmaging Gmbh | Mikroskop und Verfahren zur Erfassung von Probenlicht |
| CN102634527B (zh) * | 2012-04-11 | 2013-11-06 | 华中科技大学同济医学院附属同济医院 | 重组人nadh脱氢酶亚单位4基因及其表达载体构建方法 |
| TWI775096B (zh) * | 2012-05-15 | 2022-08-21 | 澳大利亞商艾佛蘭屈澳洲私營有限公司 | 使用腺相關病毒(aav)sflt-1治療老年性黃斑部退化(amd) |
| KR102244434B1 (ko) * | 2014-08-11 | 2021-04-23 | 삼성전자주식회사 | 재조합 벡터 및 이를 이용한 목적 폴리펩타이드의 생산 방법 |
| CN104450747B (zh) * | 2014-09-23 | 2018-02-09 | 武汉纽福斯生物科技有限公司 | 用于治疗Leber遗传性视神经病变的重组腺相关病毒‑NADH脱氢酶亚单位4基因全长以及药剂 |
-
2019
- 2019-06-11 CN CN201980039197.0A patent/CN112384625A/zh active Pending
- 2019-06-11 WO PCT/US2019/036487 patent/WO2019241206A1/en not_active Ceased
- 2019-06-11 US US16/973,900 patent/US20210189424A1/en active Pending
- 2019-06-11 JP JP2020569147A patent/JP7470057B2/ja active Active
- 2019-06-11 EP EP19734988.9A patent/EP3802840A1/en active Pending
- 2019-06-11 CA CA3103231A patent/CA3103231A1/en active Pending
- 2019-06-11 AU AU2019286386A patent/AU2019286386B2/en active Active
- 2019-06-11 KR KR1020217000782A patent/KR102946006B1/ko active Active
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