JP7838779B2 - フェニルケトン尿症を処置するための、プロモーターとエンハンサーの組み合わせを有するベクター - Google Patents

フェニルケトン尿症を処置するための、プロモーターとエンハンサーの組み合わせを有するベクター

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JP7838779B2
JP7838779B2 JP2020518812A JP2020518812A JP7838779B2 JP 7838779 B2 JP7838779 B2 JP 7838779B2 JP 2020518812 A JP2020518812 A JP 2020518812A JP 2020518812 A JP2020518812 A JP 2020518812A JP 7838779 B2 JP7838779 B2 JP 7838779B2
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vector
lentiviral
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JP2020535828A5 (enExample
JP2020535828A (ja
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テイラー ラフーゼン，
チャールズ デイビッド パウザ，
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アメリカン ジーン テクノロジーズ インターナショナル インコーポレイテッド
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JP2020518812A 2017-10-02 2018-10-02 フェニルケトン尿症を処置するための、プロモーターとエンハンサーの組み合わせを有するベクター Active JP7838779B2 (ja)

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JP2023101880A JP2023115125A (ja) 2017-10-02 2023-06-21 フェニルケトン尿症を処置するための、プロモーターとエンハンサーの組み合わせを有するベクター

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US201762566979P 2017-10-02 2017-10-02
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PCT/US2018/053919 WO2019070674A2 (en) 2017-10-02 2018-10-02 VECTORS COMPRISING PROMOTER AND ACTIVATOR COMBINATIONS FOR THE TREATMENT OF PHENYLCETONURIA

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JP2023101880A Pending JP2023115125A (ja) 2017-10-02 2023-06-21 フェニルケトン尿症を処置するための、プロモーターとエンハンサーの組み合わせを有するベクター

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Families Citing this family (18)

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WO2010045659A1 (en) 2008-10-17 2010-04-22 American Gene Technologies International Inc. Safe lentiviral vectors for targeted delivery of multiple therapeutic molecules
US11980663B2 (en) 2015-07-08 2024-05-14 American Gene Technologies International Inc. HIV pre-immunization and immunotherapy
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