JP7690401B2 - 新規ａａｖカプシドおよびそれを含む組成物 - Google Patents

新規ａａｖカプシドおよびそれを含む組成物 Download PDF

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JP7690401B2
JP7690401B2 JP2021564269A JP2021564269A JP7690401B2 JP 7690401 B2 JP7690401 B2 JP 7690401B2 JP 2021564269 A JP2021564269 A JP 2021564269A JP 2021564269 A JP2021564269 A JP 2021564269A JP 7690401 B2 JP7690401 B2 JP 7690401B2
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aavrh
aav
capsid
nucleic acid
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ナンビアー，カリヤニ
ウイルソン，ジェームス・エム
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ザ・トラステイーズ・オブ・ザ・ユニバーシテイ・オブ・ペンシルベニア
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JP2021564269A 2019-04-29 2020-04-28 新規ａａｖカプシドおよびそれを含む組成物 Active JP7690401B2 (ja)

Applications Claiming Priority (7)

Application Number Priority Date Filing Date Title
US201962840184P 2019-04-29 2019-04-29
US62/840,184 2019-04-29
US201962913314P 2019-10-10 2019-10-10
US62/913,314 2019-10-10
US201962924095P 2019-10-21 2019-10-21
US62/924,095 2019-10-21
PCT/US2020/030273 WO2020223232A1 (en) 2019-04-29 2020-04-28 Novel aav capsids and compositions containing same

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JP2022530633A JP2022530633A (ja) 2022-06-30
JP2022530633A5 JP2022530633A5 (https=) 2023-04-18
JPWO2020223232A5 JPWO2020223232A5 (https=) 2023-04-18
JP7690401B2 true JP7690401B2 (ja) 2025-06-10

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JP2021564269A Active JP7690401B2 (ja) 2019-04-29 2020-04-28 新規ａａｖカプシドおよびそれを含む組成物
JP2021564543A Pending JP2022530656A (ja) 2019-04-29 2020-04-28 新規ａａｖカプシドおよびそれを含む組成物
JP2021564542A Active JP7644026B2 (ja) 2019-04-29 2020-04-28 新規ａａｖカプシドおよびそれを含む組成物

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JP2021564542A Active JP7644026B2 (ja) 2019-04-29 2020-04-28 新規ａａｖカプシドおよびそれを含む組成物

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US (3) US12516352B2 (https=)
EP (3) EP3976077A4 (https=)
JP (3) JP7690401B2 (https=)
KR (3) KR20220004695A (https=)
CN (3) CN113853207A (https=)
AU (3) AU2020264976A1 (https=)
BR (3) BR112021020054A2 (https=)
CA (3) CA3134379A1 (https=)
CL (3) CL2021002768A1 (https=)
CO (3) CO2021015928A2 (https=)
IL (3) IL287492A (https=)
MX (3) MX2021013267A (https=)
PE (3) PE20220014A1 (https=)
PH (3) PH12021552607A1 (https=)
SG (3) SG11202111102SA (https=)
WO (3) WO2020223231A1 (https=)

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TW202237850A (zh) 2020-12-01 2022-10-01 賓州大學委員會 具有組織特異性靶向基序的新穎構成物及含有其之組成物
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WO2025102034A1 (en) 2023-11-10 2025-05-15 The Trustees Of The University Of Pennsylvania Gene therapy for barth syndrome
WO2025106661A1 (en) 2023-11-14 2025-05-22 The Trustees Of The University Of Pennsylvania Compositions with cardiac and skeletal musclespecific targeting motifs and uses thereof
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