JP7612575B2 - 筋萎縮性側索硬化症を治療及び予防するための組成物及び方法 - Google Patents

筋萎縮性側索硬化症を治療及び予防するための組成物及び方法 Download PDF

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JP7612575B2
JP7612575B2 JP2021525191A JP2021525191A JP7612575B2 JP 7612575 B2 JP7612575 B2 JP 7612575B2 JP 2021525191 A JP2021525191 A JP 2021525191A JP 2021525191 A JP2021525191 A JP 2021525191A JP 7612575 B2 JP7612575 B2 JP 7612575B2
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antisense oligonucleotide
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イヴァン アレクサンドロフ ネストロフ,
トビー ファーガソン,
ダニエル エー. ノリス,
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Biogen MA Inc
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    • A61K31/7088Compounds having three or more nucleosides or nucleotides
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JP2021525191A 2018-12-14 2019-12-12 筋萎縮性側索硬化症を治療及び予防するための組成物及び方法 Active JP7612575B2 (ja)

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JP2024213950A JP2025023319A (ja) 2018-12-14 2024-12-06 筋萎縮性側索硬化症を治療及び予防するための組成物及び方法

Applications Claiming Priority (7)

Application Number Priority Date Filing Date Title
US201862779916P 2018-12-14 2018-12-14
US62/779,916 2018-12-14
US201962807603P 2019-02-19 2019-02-19
US62/807,603 2019-02-19
US201962840879P 2019-04-30 2019-04-30
US62/840,879 2019-04-30
PCT/US2019/065936 WO2020123783A1 (en) 2018-12-14 2019-12-12 Compositions and methods for treating and preventing amyotrophic lateral sclerosis

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JP2024213950A Division JP2025023319A (ja) 2018-12-14 2024-12-06 筋萎縮性側索硬化症を治療及び予防するための組成物及び方法

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JP7612575B2 true JP7612575B2 (ja) 2025-01-14

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JP2024213950A Pending JP2025023319A (ja) 2018-12-14 2024-12-06 筋萎縮性側索硬化症を治療及び予防するための組成物及び方法

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US (1) US20220073930A1 (https=)
EP (1) EP3894557A1 (https=)
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KR (2) KR20250090384A (https=)
CN (3) CN118987017A (https=)
AU (1) AU2019396522B2 (https=)
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MY (1) MY209775A (https=)
PH (1) PH12021551365A1 (https=)
SG (1) SG11202103415WA (https=)
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US10436802B2 (en) 2014-09-12 2019-10-08 Biogen Ma Inc. Methods for treating spinal muscular atrophy
CN119679944A (zh) 2018-01-25 2025-03-25 渤健马萨诸塞州股份有限公司 治疗脊髓性肌萎缩症的方法
US12429487B2 (en) 2018-12-06 2025-09-30 Biogen Ma Inc. Neurofilament protein for guiding therapeutic intervention in amyotrophic lateral sclerosis
BR112023019877A2 (pt) * 2021-03-31 2023-11-07 Biogen Ma Inc Tratamento de esclerose lateral amiotrófica
WO2025045130A1 (zh) * 2023-08-29 2025-03-06 石药集团中奇制药技术(石家庄)有限公司 一种抑制sod1基因表达的dsrna分子及其应用

Citations (1)

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JP2017513469A (ja) 2014-04-01 2017-06-01 アイオーニス ファーマシューティカルズ, インコーポレーテッドIonis Pharmaceuticals,Inc. Sod−1発現を調節するための組成物

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CA2452458A1 (en) 2001-07-03 2003-01-16 Isis Pharmaceuticals, Inc. Nuclease resistant chimeric oligonucleotides
WO2013134403A1 (en) * 2012-03-06 2013-09-12 The Washington University Method of treating neurodegenerative diseases with microrna regulators
EP3119888B1 (en) * 2014-03-19 2021-07-28 Ionis Pharmaceuticals, Inc. Compositions for modulating ataxin 2 expression
WO2016077687A1 (en) * 2014-11-14 2016-05-19 Voyager Therapeutics, Inc. Compositions and methods of treating amyotrophic lateral sclerosis (als)
JP2020518258A (ja) * 2017-05-05 2020-06-25 ボイジャー セラピューティクス インコーポレイテッドVoyager Therapeutics,Inc. 筋萎縮性側索硬化症(als)治療組成物および方法
WO2018218219A1 (en) * 2017-05-26 2018-11-29 University Of Miami Determining onset of amyotrophic lateral sclerosis

Patent Citations (1)

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Publication number Priority date Publication date Assignee Title
JP2017513469A (ja) 2014-04-01 2017-06-01 アイオーニス ファーマシューティカルズ, インコーポレーテッドIonis Pharmaceuticals,Inc. Sod−1発現を調節するための組成物

Non-Patent Citations (1)

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Title
Lancet Neurology,2013年,Vol.12,pp.435-442

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Publication number Publication date
US20220073930A1 (en) 2022-03-10
KR20210131992A (ko) 2021-11-03
MX2021005086A (es) 2021-08-16
KR20250090384A (ko) 2025-06-19
TWI906204B (zh) 2025-12-01
EP3894557A1 (en) 2021-10-20
JOP20210143A1 (ar) 2023-01-30
CN118987017A (zh) 2024-11-22
UY38506A (es) 2020-06-30
CN113330116A (zh) 2021-08-31
TW202035694A (zh) 2020-10-01
BR112021011334A2 (pt) 2021-09-08
CA3115549A1 (en) 2020-06-18
MY209775A (en) 2025-08-03
CN119185345A (zh) 2024-12-27
KR102821047B1 (ko) 2025-06-16
CL2021001136A1 (es) 2022-01-14
AU2019396522B2 (en) 2026-04-09
JP2022513597A (ja) 2022-02-09
CR20210384A (es) 2021-12-20
SG11202103415WA (en) 2021-06-29
IL283833A (en) 2021-07-29
CO2021008187A2 (es) 2021-09-09
JP2025023319A (ja) 2025-02-14
WO2020123783A1 (en) 2020-06-18
PH12021551365A1 (en) 2021-11-22
AU2019396522A1 (en) 2021-05-06

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