JP7347933B2 - 血友病ａ治療に対する遺伝子療法 - Google Patents
血友病ａ治療に対する遺伝子療法 Download PDFInfo
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| JP2022062121A (ja) * | 2016-04-15 | 2022-04-19 | ザ・トラステイーズ・オブ・ザ・ユニバーシテイ・オブ・ペンシルベニア | 血友病ａ治療に対する遺伝子療法 |
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| WO2017180861A1 (en) | 2016-04-15 | 2017-10-19 | The Trustees Of The University Of Pennsulvania | Gene therapy for treating hemophilia b |
| KR102824021B1 (ko) | 2018-01-31 | 2025-06-24 | 더 리서치 인스티튜트 앳 네이션와이드 칠드런스 하스피탈 | 2c형 지대근이영양증에 대한 유전자 치료 |
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| BR112021007229A2 (pt) | 2018-10-16 | 2021-08-10 | Blueallele, Llc | métodos para inserção dirigida de dna em genes |
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