JP6873907B2 - 遺伝性眼疾患を治療するための方法及び組成物 - Google Patents
遺伝性眼疾患を治療するための方法及び組成物 Download PDFInfo
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| CN112424359A (zh) | 2018-05-15 | 2021-02-26 | 沃雅戈治疗公司 | 用于治疗帕金森氏病的组合物和方法 |
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| AU2019354793A1 (en) | 2018-10-05 | 2021-05-13 | Voyager Therapeutics, Inc. | Engineered nucleic acid constructs encoding AAV production proteins |
| US20210371470A1 (en) | 2018-10-12 | 2021-12-02 | Voyager Therapeutics, Inc. | Compositions and methods for delivery of aav |
| WO2020081490A1 (en) | 2018-10-15 | 2020-04-23 | Voyager Therapeutics, Inc. | EXPRESSION VECTORS FOR LARGE-SCALE PRODUCTION OF rAAV IN THE BACULOVIRUS/Sf9 SYSTEM |
| CA3125770A1 (en) | 2019-01-18 | 2020-07-23 | Voyager Therapeutics, Inc. | Methods and systems for producing aav particles |
| EP4667578A3 (en) * | 2019-04-03 | 2026-04-01 | REGENXBIO Inc. | Gene therapy for eye pathologies |
| BR112021020101A2 (pt) * | 2019-04-08 | 2022-02-15 | Childrens Hospital Philadelphia | Tratamento para doença de armazenamento lisossomal no olho através da administração de aavs expressando tpp1 |
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| EP3966227A1 (en) | 2019-05-07 | 2022-03-16 | Voyager Therapeutics, Inc. | Compositions and methods for the vectored augmentation of protein destruction, expression and/or regulation |
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| US20230277685A1 (en) * | 2020-04-08 | 2023-09-07 | President And Fellows Of Harvard College | TGFß THERAPY FOR OCULAR AND NEURODEGENERATIVE DISEASES |
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| AU2021313839A1 (en) * | 2020-07-21 | 2023-03-23 | FTGEN Corp | Composition and method for treating eye diseases |
| BR112023001456A2 (pt) | 2020-07-27 | 2023-04-11 | Voyager Therapeutics Inc | Composições e métodos para o tratamento de distúrbios neurológicos relacionados à deficiência de beta glicosilceramidase |
| US20230285596A1 (en) | 2020-07-27 | 2023-09-14 | Voyager Therapeutics, Inc | Compositions and methods for the treatment of niemann-pick type c1 disease |
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| AU2022266615A1 (en) * | 2021-04-27 | 2023-11-09 | The General Hospital Corporation | Aav capsids and uses thereof |
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| CN114195859B (zh) * | 2021-12-10 | 2022-11-18 | 和元生物技术（上海）股份有限公司 | 一种适用于特异感染u251细胞的腺相关病毒突变体 |
| KR20240152351A (ko) | 2022-02-17 | 2024-10-21 | 스카이라인 테라퓨틱스 리미티드 | 변형된 aav 캡시드 폴리펩티드를 갖는 재조합 아데노-연관 바이러스 |
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| WO2024017387A1 (en) * | 2022-07-22 | 2024-01-25 | Shanghai Vitalgen Biopharma Co., Ltd. | Novel aav capsids for targeting nervous system and uses thereof |
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- 2016-02-22 WO PCT/US2016/018970 patent/WO2016134375A1/en not_active Ceased
- 2016-02-22 JP JP2017543944A patent/JP6873907B2/ja active Active
- 2016-02-22 EP EP16753229.0A patent/EP3261440B1/en active Active
- 2016-02-22 ES ES16753229T patent/ES2920850T3/es active Active
- 2016-02-22 SG SG11201706755SA patent/SG11201706755SA/en unknown
- 2016-02-22 KR KR1020177026037A patent/KR102655319B1/ko active Active
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|---|---|
| EP3261440A1 (en) | 2018-01-03 |
| EP3261440B1 (en) | 2022-04-06 |
| ES2920850T3 (es) | 2022-08-10 |
| CN108347932A (zh) | 2018-07-31 |
| ZA201705628B (en) | 2024-08-28 |
| US20180142259A1 (en) | 2018-05-24 |
| EP3261440A4 (en) | 2018-10-31 |
| AU2016219789A1 (en) | 2017-09-28 |
| KR20180012734A (ko) | 2018-02-06 |
| SG11201706755SA (en) | 2017-09-28 |
| KR102655319B1 (ko) | 2024-04-04 |
| WO2016134375A1 (en) | 2016-08-25 |
| JP2018506980A (ja) | 2018-03-15 |
| CN108347932B (zh) | 2022-09-13 |
| SA517382162B1 (ar) | 2021-11-02 |
| NZ735344A (en) | 2024-09-27 |
| US10472650B2 (en) | 2019-11-12 |
| AU2016219789B2 (en) | 2021-03-25 |
| BR112017017867A2 (pt) | 2018-04-10 |
| CA2977355A1 (en) | 2016-08-25 |
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