JP2025515159A5 - - Google Patents

Info

Publication number
JP2025515159A5
JP2025515159A5 JP2024565157A JP2024565157A JP2025515159A5 JP 2025515159 A5 JP2025515159 A5 JP 2025515159A5 JP 2024565157 A JP2024565157 A JP 2024565157A JP 2024565157 A JP2024565157 A JP 2024565157A JP 2025515159 A5 JP2025515159 A5 JP 2025515159A5
Authority
JP
Japan
Prior art keywords
pharmaceutical composition
weight
rhgaa
miglustat
kit according
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024565157A
Other languages
English (en)
Japanese (ja)
Other versions
JP2025515159A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2023/066657 external-priority patent/WO2023215865A1/en
Publication of JP2025515159A publication Critical patent/JP2025515159A/ja
Publication of JP2025515159A5 publication Critical patent/JP2025515159A5/ja
Pending legal-status Critical Current

Links

JP2024565157A 2022-05-05 2023-05-05 ポンペ病の治療方法 Pending JP2025515159A (ja)

Applications Claiming Priority (19)

Application Number Priority Date Filing Date Title
US202263338601P 2022-05-05 2022-05-05
US63/338,601 2022-05-05
US202263399498P 2022-08-19 2022-08-19
US202263399491P 2022-08-19 2022-08-19
US63/399,498 2022-08-19
US63/399,491 2022-08-19
US202263404475P 2022-09-07 2022-09-07
US63/404,475 2022-09-07
US202263414897P 2022-10-10 2022-10-10
US63/414,897 2022-10-10
US202263428970P 2022-11-30 2022-11-30
US63/428,970 2022-11-30
US202263431920P 2022-12-12 2022-12-12
US63/431,920 2022-12-12
US202263434791P 2022-12-22 2022-12-22
US63/434,791 2022-12-22
US202363447222P 2023-02-21 2023-02-21
US63/447,222 2023-02-21
PCT/US2023/066657 WO2023215865A1 (en) 2022-05-05 2023-05-05 Methods for treating pompe disease

Publications (2)

Publication Number Publication Date
JP2025515159A JP2025515159A (ja) 2025-05-13
JP2025515159A5 true JP2025515159A5 (enExample) 2026-05-15

Family

ID=86692686

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024565157A Pending JP2025515159A (ja) 2022-05-05 2023-05-05 ポンペ病の治療方法

Country Status (13)

Country Link
US (1) US20260041744A1 (enExample)
EP (1) EP4518885A1 (enExample)
JP (1) JP2025515159A (enExample)
KR (1) KR20250007602A (enExample)
CN (1) CN119343147A (enExample)
AU (1) AU2023265155A1 (enExample)
CA (1) CA3252291A1 (enExample)
CL (1) CL2024003377A1 (enExample)
CO (1) CO2024016724A2 (enExample)
IL (1) IL316776A (enExample)
MX (1) MX2024013673A (enExample)
TW (1) TW202400212A (enExample)
WO (1) WO2023215865A1 (enExample)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2026006625A1 (en) 2024-06-26 2026-01-02 Amicus Therapeutics, Inc. Miglustat formulations comprising nitrosamine for use in the treatment of pompe disease

Family Cites Families (10)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US6534300B1 (en) 1999-09-14 2003-03-18 Genzyme Glycobiology Research Institute, Inc. Methods for producing highly phosphorylated lysosomal hydrolases
WO2009102895A2 (en) 2008-02-12 2009-08-20 Amicus Therapeutics, Inc. Method to predict response to pharmacological chaperone treatment of diseases
US11382980B2 (en) 2013-10-08 2022-07-12 Taiyo Kagaku Co., Ltd. Oil/fat composition containing polyunsaturated fatty acid
JP6851964B2 (ja) * 2014-09-30 2021-03-31 アミカス セラピューティックス インコーポレイテッド 炭水化物が増大している非常に強力な酸性アルファ−グルコシダーゼ
IL299470B2 (en) * 2015-12-30 2026-05-01 Amicus Therapeutics Inc Improved acid alpha-glucosidase for the treatment of Pompe disease
CA3019354A1 (en) 2016-03-30 2017-10-05 Amicus Therapeutics, Inc. Method for selection of high m6p recombinant proteins
KR102618519B1 (ko) * 2016-03-30 2023-12-28 아미쿠스 세라퓨틱스, 인코포레이티드 재조합 산 알파-글루코시다제를 포함하는 제형
CN119113091A (zh) * 2017-05-15 2024-12-13 阿米库斯治疗学公司 重组人类酸性α-葡萄糖苷酶
WO2020163480A1 (en) 2019-02-05 2020-08-13 Amicus Therapeutics, Inc. Recombinant human acid alpha-glucosidase and uses thereof
JP2024506346A (ja) * 2021-02-11 2024-02-13 アミカス セラピューティックス インコーポレイテッド 組換えヒト酸性アルファグルコシダーゼ及びその使用

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