JP2024506346A5 - - Google Patents
Info
- Publication number
- JP2024506346A5 JP2024506346A5 JP2023548587A JP2023548587A JP2024506346A5 JP 2024506346 A5 JP2024506346 A5 JP 2024506346A5 JP 2023548587 A JP2023548587 A JP 2023548587A JP 2023548587 A JP2023548587 A JP 2023548587A JP 2024506346 A5 JP2024506346 A5 JP 2024506346A5
- Authority
- JP
- Japan
- Prior art keywords
- rhgaa
- subject
- mol
- optionally
- treatment
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (5)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202163148596P | 2021-02-11 | 2021-02-11 | |
| US63/148,596 | 2021-02-11 | ||
| US202163162683P | 2021-03-18 | 2021-03-18 | |
| US63/162,683 | 2021-03-18 | ||
| PCT/US2022/016124 WO2022174037A1 (en) | 2021-02-11 | 2022-02-11 | Recombinant human acid alpha-glucosidase and uses thereof |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2024506346A JP2024506346A (ja) | 2024-02-13 |
| JP2024506346A5 true JP2024506346A5 (enExample) | 2025-02-19 |
Family
ID=82837922
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023548587A Pending JP2024506346A (ja) | 2021-02-11 | 2022-02-11 | 組換えヒト酸性アルファグルコシダーゼ及びその使用 |
Country Status (10)
| Country | Link |
|---|---|
| US (1) | US20240197839A1 (enExample) |
| EP (1) | EP4291225A4 (enExample) |
| JP (1) | JP2024506346A (enExample) |
| KR (1) | KR20230155622A (enExample) |
| AU (1) | AU2022218792A1 (enExample) |
| BR (1) | BR112023016212A2 (enExample) |
| CA (1) | CA3207917A1 (enExample) |
| IL (1) | IL305103A (enExample) |
| TW (1) | TW202245830A (enExample) |
| WO (1) | WO2022174037A1 (enExample) |
Families Citing this family (4)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| CA3019354A1 (en) | 2016-03-30 | 2017-10-05 | Amicus Therapeutics, Inc. | Method for selection of high m6p recombinant proteins |
| KR102618519B1 (ko) | 2016-03-30 | 2023-12-28 | 아미쿠스 세라퓨틱스, 인코포레이티드 | 재조합 산 알파-글루코시다제를 포함하는 제형 |
| US12018087B2 (en) | 2018-08-02 | 2024-06-25 | Dyne Therapeutics, Inc. | Muscle-targeting complexes comprising an anti-transferrin receptor antibody linked to an oligonucleotide and methods of delivering oligonucleotide to a subject |
| WO2023215865A1 (en) * | 2022-05-05 | 2023-11-09 | Amicus Therapeutics, Inc. | Methods for treating pompe disease |
Family Cites Families (7)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US8679478B2 (en) * | 2010-10-04 | 2014-03-25 | Duke University | Methods of lysosomal storage disease therapy |
| CA2867237C (en) * | 2012-03-15 | 2024-01-02 | Wouter Vervecken | Methods and materials for treatment of pompe's disease |
| JP6851964B2 (ja) * | 2014-09-30 | 2021-03-31 | アミカス セラピューティックス インコーポレイテッド | 炭水化物が増大している非常に強力な酸性アルファ−グルコシダーゼ |
| IL299470B2 (en) * | 2015-12-30 | 2026-05-01 | Amicus Therapeutics Inc | Improved acid alpha-glucosidase for the treatment of Pompe disease |
| KR102618519B1 (ko) * | 2016-03-30 | 2023-12-28 | 아미쿠스 세라퓨틱스, 인코포레이티드 | 재조합 산 알파-글루코시다제를 포함하는 제형 |
| CN119113091A (zh) * | 2017-05-15 | 2024-12-13 | 阿米库斯治疗学公司 | 重组人类酸性α-葡萄糖苷酶 |
| WO2020163480A1 (en) * | 2019-02-05 | 2020-08-13 | Amicus Therapeutics, Inc. | Recombinant human acid alpha-glucosidase and uses thereof |
-
2022
- 2022-02-11 JP JP2023548587A patent/JP2024506346A/ja active Pending
- 2022-02-11 KR KR1020237031038A patent/KR20230155622A/ko active Pending
- 2022-02-11 CA CA3207917A patent/CA3207917A1/en active Pending
- 2022-02-11 EP EP22753411.2A patent/EP4291225A4/en active Pending
- 2022-02-11 IL IL305103A patent/IL305103A/en unknown
- 2022-02-11 US US18/276,954 patent/US20240197839A1/en active Pending
- 2022-02-11 AU AU2022218792A patent/AU2022218792A1/en active Pending
- 2022-02-11 WO PCT/US2022/016124 patent/WO2022174037A1/en not_active Ceased
- 2022-02-11 TW TW111105104A patent/TW202245830A/zh unknown
- 2022-02-11 BR BR112023016212A patent/BR112023016212A2/pt unknown
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