JP2025090820A5 - - Google Patents
Info
- Publication number
- JP2025090820A5 JP2025090820A5 JP2025043347A JP2025043347A JP2025090820A5 JP 2025090820 A5 JP2025090820 A5 JP 2025090820A5 JP 2025043347 A JP2025043347 A JP 2025043347A JP 2025043347 A JP2025043347 A JP 2025043347A JP 2025090820 A5 JP2025090820 A5 JP 2025090820A5
- Authority
- JP
- Japan
- Prior art keywords
- seq
- nucleic acid
- acid molecule
- isolated nucleic
- nucleotide sequence
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Granted
Links
Applications Claiming Priority (4)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| CN2021106619 | 2021-07-15 | ||
| CNPCT/CN2021/106619 | 2021-07-15 | ||
| JP2024502112A JP2024524707A (ja) | 2021-07-15 | 2022-07-15 | ビエッティ結晶性ジストロフィー治療のための遺伝子組換アデノ随伴ウイルスベクター |
| PCT/CN2022/106089 WO2023284873A1 (en) | 2021-07-15 | 2022-07-15 | Recombinant adeno-associated viral vectors for treating bietti crystalline dystrophy |
Related Parent Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024502112A Division JP2024524707A (ja) | 2021-07-15 | 2022-07-15 | ビエッティ結晶性ジストロフィー治療のための遺伝子組換アデノ随伴ウイルスベクター |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2025090820A JP2025090820A (ja) | 2025-06-17 |
| JP2025090820A5 true JP2025090820A5 (https=) | 2025-07-23 |
| JP7811415B2 JP7811415B2 (ja) | 2026-02-05 |
Family
ID=84919061
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024502112A Pending JP2024524707A (ja) | 2021-07-15 | 2022-07-15 | ビエッティ結晶性ジストロフィー治療のための遺伝子組換アデノ随伴ウイルスベクター |
| JP2025043347A Active JP7811415B2 (ja) | 2021-07-15 | 2025-03-18 | ビエッティ結晶性ジストロフィー治療のための遺伝子組換アデノ随伴ウイルスベクター |
Family Applications Before (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024502112A Pending JP2024524707A (ja) | 2021-07-15 | 2022-07-15 | ビエッティ結晶性ジストロフィー治療のための遺伝子組換アデノ随伴ウイルスベクター |
Country Status (5)
| Country | Link |
|---|---|
| US (1) | US12371474B2 (https=) |
| EP (1) | EP4370663A4 (https=) |
| JP (2) | JP2024524707A (https=) |
| CN (1) | CN117916365B (https=) |
| WO (1) | WO2023284873A1 (https=) |
Families Citing this family (2)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| SG11202000840YA (en) | 2017-07-31 | 2020-02-27 | Reflection Biotechnologies Ltd | Cellular models of and therapies for ocular diseases |
| CN114381465B (zh) * | 2021-12-22 | 2024-01-16 | 苏州诺洁贝生物技术有限公司 | 优化的cyp4v2基因及其用途 |
Family Cites Families (9)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2017191274A2 (en) * | 2016-05-04 | 2017-11-09 | Curevac Ag | Rna encoding a therapeutic protein |
| SG11202000840YA (en) * | 2017-07-31 | 2020-02-27 | Reflection Biotechnologies Ltd | Cellular models of and therapies for ocular diseases |
| CN109136266B (zh) * | 2018-08-10 | 2022-02-18 | 深圳泓熙生物科技发展有限公司 | 用于治疗或预防结晶样视网膜色素变性的基因载体及其用途 |
| KR20220022107A (ko) * | 2018-12-05 | 2022-02-24 | 아베오나 테라퓨틱스 인코퍼레이티드 | 유전자 전달을 위한 재조합 아데노-연관 바이러스 벡터 |
| US20220154211A1 (en) * | 2019-02-25 | 2022-05-19 | Novartis Ag | Compositions and methods to treat bietti crystalline dystrophy |
| SG11202108044YA (en) * | 2019-02-25 | 2021-09-29 | Novartis Ag | Compositions and methods to treat bietti crystalline dystrophy |
| CN113106124B (zh) * | 2020-06-09 | 2022-09-23 | 北京中因科技有限公司 | 表达cyp4v2的aav载体及其用途 |
| CN111733174B (zh) * | 2020-08-07 | 2021-02-09 | 北京大学第三医院（北京大学第三临床医学院） | 一种分离的核酸分子及其用途 |
| CN114381465B (zh) * | 2021-12-22 | 2024-01-16 | 苏州诺洁贝生物技术有限公司 | 优化的cyp4v2基因及其用途 |
-
2022
- 2022-07-15 WO PCT/CN2022/106089 patent/WO2023284873A1/en not_active Ceased
- 2022-07-15 CN CN202280050016.6A patent/CN117916365B/zh active Active
- 2022-07-15 EP EP22841506.3A patent/EP4370663A4/en active Pending
- 2022-07-15 JP JP2024502112A patent/JP2024524707A/ja active Pending
-
2024
- 2024-01-11 US US18/410,043 patent/US12371474B2/en active Active
-
2025
- 2025-03-18 JP JP2025043347A patent/JP7811415B2/ja active Active
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