JP2024525742A5 - - Google Patents

Info

Publication number
JP2024525742A5
JP2024525742A5 JP2024501820A JP2024501820A JP2024525742A5 JP 2024525742 A5 JP2024525742 A5 JP 2024525742A5 JP 2024501820 A JP2024501820 A JP 2024501820A JP 2024501820 A JP2024501820 A JP 2024501820A JP 2024525742 A5 JP2024525742 A5 JP 2024525742A5
Authority
JP
Japan
Prior art keywords
sequence
expression construct
vector
construct according
pharmaceutical composition
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024501820A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024525742A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/IB2022/056457 external-priority patent/WO2023285986A1/en
Publication of JP2024525742A publication Critical patent/JP2024525742A/ja
Publication of JP2024525742A5 publication Critical patent/JP2024525742A5/ja
Pending legal-status Critical Current

Links

JP2024501820A 2021-07-14 2022-07-13 Ｋｃｎｖ２遺伝子治療 Pending JP2024525742A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163221879P 2021-07-14 2021-07-14
US63/221,879 2021-07-14
PCT/IB2022/056457 WO2023285986A1 (en) 2021-07-14 2022-07-13 Kcnv2 gene therapy

Publications (2)

Publication Number Publication Date
JP2024525742A JP2024525742A (ja) 2024-07-12
JP2024525742A5 true JP2024525742A5 (https=) 2025-07-22

Family

ID=82932641

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024501820A Pending JP2024525742A (ja) 2021-07-14 2022-07-13 Ｋｃｎｖ２遺伝子治療

Country Status (10)

Country Link
US (1) US20240307559A1 (https=)
EP (1) EP4370538A1 (https=)
JP (1) JP2024525742A (https=)
KR (1) KR20240052746A (https=)
CN (1) CN118019757A (https=)
AU (1) AU2022311329A1 (https=)
CA (1) CA3225080A1 (https=)
IL (1) IL310018A (https=)
MX (1) MX2024000748A (https=)
WO (1) WO2023285986A1 (https=)

Family Cites Families (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
DE4345297A1 (de) 1993-11-11 1995-09-28 Nsm Ag Geldspielgerät
US5856152A (en) 1994-10-28 1999-01-05 The Trustees Of The University Of Pennsylvania Hybrid adenovirus-AAV vector and methods of use therefor
CA2346262A1 (en) 1998-09-17 2000-03-23 University Of Florida Methods for treatment of degenerative retinal diseases
MA44546B1 (fr) 2016-06-15 2021-03-31 Univ California Virus adéno-associés variants et procédés d'utilisation
SG11202000840YA (en) * 2017-07-31 2020-02-27 Reflection Biotechnologies Ltd Cellular models of and therapies for ocular diseases

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