JP2023534293A5 - - Google Patents

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Publication number
JP2023534293A5
JP2023534293A5 JP2023503074A JP2023503074A JP2023534293A5 JP 2023534293 A5 JP2023534293 A5 JP 2023534293A5 JP 2023503074 A JP2023503074 A JP 2023503074A JP 2023503074 A JP2023503074 A JP 2023503074A JP 2023534293 A5 JP2023534293 A5 JP 2023534293A5
Authority
JP
Japan
Application number
JP2023503074A
Other languages
Japanese (ja)
Other versions
JPWO2022016055A5 (https=
JP2023534293A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2021/041975 external-priority patent/WO2022016055A1/en
Publication of JP2023534293A publication Critical patent/JP2023534293A/ja
Publication of JPWO2022016055A5 publication Critical patent/JPWO2022016055A5/ja
Publication of JP2023534293A5 publication Critical patent/JP2023534293A5/ja
Pending legal-status Critical Current

Links

JP2023503074A 2020-07-17 2021-07-16 脆弱x症候群の治療のための方法及び組成物 Pending JP2023534293A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202063053461P 2020-07-17 2020-07-17
US63/053,461 2020-07-17
PCT/US2021/041975 WO2022016055A1 (en) 2020-07-17 2021-07-16 Methods and compositions for treatment of fragile x syndrome

Publications (3)

Publication Number Publication Date
JP2023534293A JP2023534293A (ja) 2023-08-08
JPWO2022016055A5 JPWO2022016055A5 (https=) 2024-07-24
JP2023534293A5 true JP2023534293A5 (https=) 2024-07-24

Family

ID=79554278

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023503074A Pending JP2023534293A (ja) 2020-07-17 2021-07-16 脆弱x症候群の治療のための方法及び組成物

Country Status (9)

Country Link
US (1) US20230295654A1 (https=)
EP (1) EP4181877A4 (https=)
JP (1) JP2023534293A (https=)
KR (1) KR20230084465A (https=)
CN (1) CN117136077A (https=)
AU (1) AU2021308666A1 (https=)
CA (1) CA3189657A1 (https=)
IL (1) IL299889A (https=)
WO (1) WO2022016055A1 (https=)

Families Citing this family (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US20250195497A1 (en) * 2022-03-22 2025-06-19 Kyoto University Therapeutic or prophylactic medicine for fragile x syndrome
GB202206336D0 (en) * 2022-04-29 2022-06-15 Univ Edinburgh Recombinant therapeutic FMR1 constructs and methods of treating fragile X syndrome and related disorders
AU2024313758A1 (en) 2023-06-23 2026-01-08 Uniqure Biopharma B.V. Novel fragile x constructs

Family Cites Families (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2012056440A1 (en) * 2010-10-28 2012-05-03 Nanodoc Ltd. COMPOSITIONS AND METHODS FOR ACTIVATING EXPRESSION BY A SPECIFIC ENDOGENOUS miRNA
CA3019315A1 (en) * 2015-04-23 2016-10-27 University Of Massachusetts Modulation of aav vector transgene expression
GB2574243A (en) * 2018-05-31 2019-12-04 The Govening Council Of The Univ Of Toronto Adeno-associated viral vector-mediated gene therapy for treating fragile X-associated disorders
US12421524B2 (en) * 2018-09-24 2025-09-23 Merck Sharp & Dohme Llc Expression vectors for eukaryotic expression systems

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