JP2024540108A5 - - Google Patents

Info

Publication number
JP2024540108A5
JP2024540108A5 JP2024525411A JP2024525411A JP2024540108A5 JP 2024540108 A5 JP2024540108 A5 JP 2024540108A5 JP 2024525411 A JP2024525411 A JP 2024525411A JP 2024525411 A JP2024525411 A JP 2024525411A JP 2024540108 A5 JP2024540108 A5 JP 2024540108A5
Authority
JP
Japan
Prior art keywords
lipid
compound
independently
lipid nanoparticles
mol
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024525411A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024540108A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/EP2022/080581 external-priority patent/WO2023078950A1/en
Publication of JP2024540108A publication Critical patent/JP2024540108A/ja
Publication of JP2024540108A5 publication Critical patent/JP2024540108A5/ja
Pending legal-status Critical Current

Links

JP2024525411A 2021-11-02 2022-11-02 オリゴヌクレオチド送達のための脂質ナノ粒子 Pending JP2024540108A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
EP21205904 2021-11-02
EP21205904.2 2021-11-02
EP22179399.5 2022-06-16
EP22179399 2022-06-16
PCT/EP2022/080581 WO2023078950A1 (en) 2021-11-02 2022-11-02 Lipid nanoparticles for oligonucleotide delivery

Publications (2)

Publication Number Publication Date
JP2024540108A JP2024540108A (ja) 2024-10-31
JP2024540108A5 true JP2024540108A5 (https=) 2025-10-31

Family

ID=84364268

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024525411A Pending JP2024540108A (ja) 2021-11-02 2022-11-02 オリゴヌクレオチド送達のための脂質ナノ粒子

Country Status (14)

Country Link
US (1) US20250236599A1 (https=)
EP (2) EP4613741A3 (https=)
JP (1) JP2024540108A (https=)
KR (1) KR20240099377A (https=)
AU (1) AU2022381463A1 (https=)
CA (1) CA3236653A1 (https=)
DK (1) DK4426270T3 (https=)
ES (1) ES3042660T3 (https=)
FI (1) FI4426270T3 (https=)
IL (1) IL312432B1 (https=)
MX (1) MX2024005109A (https=)
PL (1) PL4426270T3 (https=)
WO (1) WO2023078950A1 (https=)
ZA (1) ZA202403360B (https=)

Families Citing this family (10)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US12491261B2 (en) 2016-10-26 2025-12-09 Acuitas Therapeutics, Inc. Lipid nanoparticle formulations
CA3116576A1 (en) 2018-10-18 2020-04-23 Acuitas Therapeutics, Inc. Lipids for lipid nanoparticle delivery of active agents
CN118125994A (zh) * 2022-11-25 2024-06-04 艾斯拓康医药科技(北京)有限公司 可离子化脂质及其应用
WO2024136309A1 (en) * 2022-12-23 2024-06-27 Green Cross Corporation Ionizable lipid and use thereof
CN116514696B (zh) * 2023-06-29 2023-12-01 艾斯拓康医药科技(北京)有限公司 可离子化脂质及其应用
WO2025088152A1 (en) 2023-10-27 2025-05-01 Ziphius Nv MODIFIED 5'UTRs
US12599560B2 (en) 2023-11-02 2026-04-14 Longuide Biopharma Corporation Lipids and lipid nanoparticle formulations
WO2025104023A1 (en) 2023-11-13 2025-05-22 Ziphius Nv MODIFIED ALPHAVIRAL nsP3
WO2025128696A1 (en) * 2023-12-12 2025-06-19 Acuitas Therapeutics, Inc. Cationic lipid compounds for use in lipid nanoparticles
WO2025255534A1 (en) * 2024-06-07 2025-12-11 Innovac Therapeutics Hk Limited Diol-based novel ionizable lipids and their uses thereof

Family Cites Families (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US6451592B1 (en) 1996-04-05 2002-09-17 Chiron Corporation Recombinant alphavirus-based vectors with reduced inhibition of cellular macromolecular synthesis
CN1989250B (zh) 2004-05-18 2013-11-20 阿尔法瓦克斯公司 Tc-83衍生的甲病毒属载体、颗粒和方法
US7332322B2 (en) 2004-09-14 2008-02-19 Ilya Frolov Venezuelan equine encephalitis virus replicons with adaptive mutations in the genome and uses thereof
WO2014028487A1 (en) * 2012-08-13 2014-02-20 Massachusetts Institute Of Technology Amine-containing lipidoids and uses thereof
WO2018232120A1 (en) * 2017-06-14 2018-12-20 Modernatx, Inc. Compounds and compositions for intracellular delivery of agents

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