JP2024537711A5 - - Google Patents

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Publication number
JP2024537711A5
JP2024537711A5 JP2024518369A JP2024518369A JP2024537711A5 JP 2024537711 A5 JP2024537711 A5 JP 2024537711A5 JP 2024518369 A JP2024518369 A JP 2024518369A JP 2024518369 A JP2024518369 A JP 2024518369A JP 2024537711 A5 JP2024537711 A5 JP 2024537711A5
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JP
Japan
Prior art keywords
sequence
gaa
conjugate according
ctc
ivs1
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024518369A
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English (en)
Japanese (ja)
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JP2024537711A (ja
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Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/044995 external-priority patent/WO2023055774A1/en
Publication of JP2024537711A publication Critical patent/JP2024537711A/ja
Publication of JP2024537711A5 publication Critical patent/JP2024537711A5/ja
Pending legal-status Critical Current

Links

JP2024518369A 2021-09-30 2022-09-28 1つ以上の脱塩基ユニットを有するアンチセンスオリゴヌクレオチド Pending JP2024537711A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US202163261860P 2021-09-30 2021-09-30
US63/261,860 2021-09-30
US202263408277P 2022-09-20 2022-09-20
US63/408,277 2022-09-20
PCT/US2022/044995 WO2023055774A1 (en) 2021-09-30 2022-09-28 Antisense oligonucleotides having one or more abasic units

Publications (2)

Publication Number Publication Date
JP2024537711A JP2024537711A (ja) 2024-10-16
JP2024537711A5 true JP2024537711A5 (enExample) 2025-09-30

Family

ID=83995343

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024518369A Pending JP2024537711A (ja) 2021-09-30 2022-09-28 1つ以上の脱塩基ユニットを有するアンチセンスオリゴヌクレオチド

Country Status (12)

Country Link
US (1) US20240425864A1 (enExample)
EP (1) EP4392558A1 (enExample)
JP (1) JP2024537711A (enExample)
KR (1) KR20240070615A (enExample)
AU (1) AU2022358322A1 (enExample)
CA (1) CA3233242A1 (enExample)
CL (1) CL2024000863A1 (enExample)
CO (1) CO2024004754A2 (enExample)
IL (1) IL311568A (enExample)
MX (1) MX2024003690A (enExample)
TW (1) TW202333795A (enExample)
WO (1) WO2023055774A1 (enExample)

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