TW202333795A

TW202333795A - 具有一或多個無鹼基單元之反義寡核苷酸

具有一或多個無鹼基單元之反義寡核苷酸 Download PDF

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Publication number: TW202333795A
Authority: TW; Taiwan
Prior art keywords: gaa; seq; ivs1; ctc; conjugate
Prior art date: 2021-09-30

Application number

TW111137310A

Other languages

English (en)

Chinese (zh)

Inventor

萊恩奧利佛

凱文金

梅根艾亨

Original Assignee

美商薩羅塔治療公司

Priority date

2021-09-30

Filing date

2022-09-30

Publication date

2023-09-01

2022-09-30 Application filed by 美商薩羅塔治療公司 filed Critical 美商薩羅塔治療公司

2023-09-01 Publication of TW202333795A publication Critical patent/TW202333795A/zh

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