JP2024509792A5 - - Google Patents

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Publication number
JP2024509792A5
JP2024509792A5 JP2023552146A JP2023552146A JP2024509792A5 JP 2024509792 A5 JP2024509792 A5 JP 2024509792A5 JP 2023552146 A JP2023552146 A JP 2023552146A JP 2023552146 A JP2023552146 A JP 2023552146A JP 2024509792 A5 JP2024509792 A5 JP 2024509792A5
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JP
Japan
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JP2023552146A
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Japanese (ja)
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JPWO2022183052A5 (https=
JP2024509792A (ja
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Publication date
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Priority claimed from PCT/US2022/017998 external-priority patent/WO2022183052A1/en
Publication of JP2024509792A publication Critical patent/JP2024509792A/ja
Publication of JP2024509792A5 publication Critical patent/JP2024509792A5/ja
Publication of JPWO2022183052A5 publication Critical patent/JPWO2022183052A5/ja
Withdrawn legal-status Critical Current

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JP2023552146A 2021-02-26 2022-02-25 ファブリー病の治療のための組成物及び方法 Withdrawn JP2024509792A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163154485P 2021-02-26 2021-02-26
US63/154,485 2021-02-26
PCT/US2022/017998 WO2022183052A1 (en) 2021-02-26 2022-02-25 Composition and methods for the treatment of fabry disease

Publications (3)

Publication Number Publication Date
JP2024509792A JP2024509792A (ja) 2024-03-05
JP2024509792A5 true JP2024509792A5 (https=) 2025-03-03
JPWO2022183052A5 JPWO2022183052A5 (https=) 2025-03-03

Family

ID=80786597

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023552146A Withdrawn JP2024509792A (ja) 2021-02-26 2022-02-25 ファブリー病の治療のための組成物及び方法

Country Status (17)

Country Link
US (1) US20240175054A1 (https=)
EP (1) EP4298227A1 (https=)
JP (1) JP2024509792A (https=)
KR (1) KR20230150836A (https=)
CN (1) CN117321212A (https=)
AR (1) AR124981A1 (https=)
AU (1) AU2022227017A1 (https=)
BR (1) BR112023016983A2 (https=)
CA (1) CA3209673A1 (https=)
CL (1) CL2023002530A1 (https=)
CO (1) CO2023011012A2 (https=)
EC (1) ECSP23072174A (https=)
IL (1) IL305440A (https=)
MX (1) MX2023009978A (https=)
PE (1) PE20240806A1 (https=)
TW (1) TW202302855A (https=)
WO (1) WO2022183052A1 (https=)

Families Citing this family (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
JP2025529884A (ja) * 2022-08-25 2025-09-09 武田薬品工業株式会社 ファブリー病の治療に使用するための組成物
CN121002183A (zh) * 2023-04-17 2025-11-21 杭州复因生物科技有限公司 用于基因治疗的组合物和方法
WO2024236544A1 (en) 2023-05-17 2024-11-21 Takeda Pharmaceutical Company Limited Pet tracer compounds for tracing alpha-galactosidase a and reaction intermediates, and methods of use

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US5436146A (en) 1989-09-07 1995-07-25 The Trustees Of Princeton University Helper-free stocks of recombinant adeno-associated virus vectors
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US5869305A (en) 1992-12-04 1999-02-09 The University Of Pittsburgh Recombinant viral vector system
US5478745A (en) 1992-12-04 1995-12-26 University Of Pittsburgh Recombinant viral vector system
US6204059B1 (en) 1994-06-30 2001-03-20 University Of Pittsburgh AAV capsid vehicles for molecular transfer
US6093570A (en) 1995-06-07 2000-07-25 The University Of North Carolina At Chapel Hill Helper virus-free AAV production
US5741683A (en) 1995-06-07 1998-04-21 The Research Foundation Of State University Of New York In vitro packaging of adeno-associated virus DNA
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CN1856576B (zh) 2003-09-30 2011-05-04 宾夕法尼亚州立大学托管会 腺伴随病毒(aav)进化支、序列、含有这些序列的载体及它们的应用
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AU2021356684A1 (en) * 2020-10-09 2023-05-11 The Trustees Of The University Of Pennsylvania Compositions and methods for treatment of fabry disease

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