JP2024500786A - Ｃｌｒｎ１関連難聴及び／または視力低下を治療するための組成物及び方法 - Google Patents

Ｃｌｒｎ１関連難聴及び／または視力低下を治療するための組成物及び方法 Download PDF

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JP2024500786A
JP2024500786A JP2023537130A JP2023537130A JP2024500786A JP 2024500786 A JP2024500786 A JP 2024500786A JP 2023537130 A JP2023537130 A JP 2023537130A JP 2023537130 A JP2023537130 A JP 2023537130A JP 2024500786 A JP2024500786 A JP 2024500786A
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ジョン シモンズ，エマニュエル
ング，ロバート
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アコーオス インコーポレイテッド
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    • A61K48/00—Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy
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    • C12N2750/14151—Methods of production or purification of viral material
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    • C12N2840/00—Vectors comprising a special translation-regulating system
    • C12N2840/44—Vectors comprising a special translation-regulating system being a specific part of the splice mechanism, e.g. donor, acceptor
    • C12N2840/445—Vectors comprising a special translation-regulating system being a specific part of the splice mechanism, e.g. donor, acceptor for trans-splicing, e.g. polypyrimidine tract, branch point splicing

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JP2023537130A 2020-12-29 2021-12-22 Ｃｌｒｎ１関連難聴及び／または視力低下を治療するための組成物及び方法 Pending JP2024500786A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202063131413P 2020-12-29 2020-12-29
US63/131,413 2020-12-29
PCT/US2021/064924 WO2022146839A1 (en) 2020-12-29 2021-12-22 Compositions and methods for treating clrn1-associated hearing loss and/or vision loss

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JP2024500786A true JP2024500786A (ja) 2024-01-10
JP2024500786A5 JP2024500786A5 (OSRAM) 2024-12-27

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US (1) US20240139344A1 (OSRAM)
EP (1) EP4271419A1 (OSRAM)
JP (1) JP2024500786A (OSRAM)
KR (1) KR20230127263A (OSRAM)
CN (1) CN117157108A (OSRAM)
AU (1) AU2021412962A1 (OSRAM)
CA (1) CA3203373A1 (OSRAM)
CL (1) CL2023001896A1 (OSRAM)
CO (1) CO2023007325A2 (OSRAM)
DO (2) DOP2023000132A (OSRAM)
EC (1) ECSP23057004A (OSRAM)
IL (1) IL304006A (OSRAM)
JO (1) JOP20230151A1 (OSRAM)
MX (1) MX2023007800A (OSRAM)
PE (1) PE20240012A1 (OSRAM)
WO (1) WO2022146839A1 (OSRAM)

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CN120285151B (zh) * 2025-04-14 2026-03-31 山东第一医科大学(山东省医学科学院) HuR及其编码基因在制备治疗老年性耳聋药物中的应用

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CA3203373A1 (en) 2022-07-07
CN117157108A (zh) 2023-12-01
MX2023007800A (es) 2023-07-11
IL304006A (en) 2023-08-01
EP4271419A1 (en) 2023-11-08
US20240139344A1 (en) 2024-05-02
DOP2025000286A (es) 2025-12-30
WO2022146839A1 (en) 2022-07-07
DOP2023000132A (es) 2023-07-31
JOP20230151A1 (ar) 2023-06-25
KR20230127263A (ko) 2023-08-31
AU2021412962A1 (en) 2023-08-17
PE20240012A1 (es) 2024-01-04
CL2023001896A1 (es) 2023-12-15
ECSP23057004A (es) 2023-08-31
CO2023007325A2 (es) 2023-06-20

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