JP2024069430A5 - - Google Patents

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Publication number
JP2024069430A5
JP2024069430A5 JP2024038955A JP2024038955A JP2024069430A5 JP 2024069430 A5 JP2024069430 A5 JP 2024069430A5 JP 2024038955 A JP2024038955 A JP 2024038955A JP 2024038955 A JP2024038955 A JP 2024038955A JP 2024069430 A5 JP2024069430 A5 JP 2024069430A5
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JP
Japan
Prior art keywords
vector
aspartic acid
asparagine
amino acids
repeat sequence
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024038955A
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English (en)
Japanese (ja)
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JP7854207B2 (ja
JP2024069430A (ja
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Priority claimed from PCT/JP2022/019038 external-priority patent/WO2022230924A1/ja
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Publication of JP2024069430A publication Critical patent/JP2024069430A/ja
Publication of JP2024069430A5 publication Critical patent/JP2024069430A5/ja
Application granted granted Critical
Publication of JP7854207B2 publication Critical patent/JP7854207B2/ja
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JP2024038955A 2021-04-30 2024-03-13 筋強直性ジストロフィー1型治療薬 Active JP7854207B2 (ja)

Applications Claiming Priority (4)

Application Number Priority Date Filing Date Title
JP2021077262 2021-04-30
JP2021077262 2021-04-30
PCT/JP2022/019038 WO2022230924A1 (ja) 2021-04-30 2022-04-27 筋強直性ジストロフィー1型治療薬
JP2023517588A JP7461687B2 (ja) 2021-04-30 2022-04-27 筋強直性ジストロフィー1型治療薬

Related Parent Applications (1)

Application Number Title Priority Date Filing Date
JP2023517588A Division JP7461687B2 (ja) 2021-04-30 2022-04-27 筋強直性ジストロフィー1型治療薬

Publications (3)

Publication Number Publication Date
JP2024069430A JP2024069430A (ja) 2024-05-21
JP2024069430A5 true JP2024069430A5 (https=) 2025-04-08
JP7854207B2 JP7854207B2 (ja) 2026-05-01

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