JP2024056832A5 - - Google Patents
Info
- Publication number
- JP2024056832A5 JP2024056832A5 JP2024019140A JP2024019140A JP2024056832A5 JP 2024056832 A5 JP2024056832 A5 JP 2024056832A5 JP 2024019140 A JP2024019140 A JP 2024019140A JP 2024019140 A JP2024019140 A JP 2024019140A JP 2024056832 A5 JP2024056832 A5 JP 2024056832A5
- Authority
- JP
- Japan
- Prior art keywords
- gnptab
- raav
- amino acid
- acid sequence
- particle
- Prior art date
Links
Applications Claiming Priority (5)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201562267502P | 2015-12-15 | 2015-12-15 | |
| US62/267,502 | 2015-12-15 | ||
| JP2018531240A JP7347932B2 (ja) | 2015-12-15 | 2016-12-14 | ムコリピドーシスｉｉ型を治療するためのアデノ随伴ウイルスベクター |
| PCT/US2016/066611 WO2017106313A1 (en) | 2015-12-15 | 2016-12-14 | Adeno-associated viral vectors for treating mucolipidosis type ii |
| JP2021210071A JP2022046635A (ja) | 2015-12-15 | 2021-12-24 | ムコリピドーシスｉｉ型を治療するためのアデノ随伴ウイルスベクター |
Related Parent Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021210071A Division JP2022046635A (ja) | 2015-12-15 | 2021-12-24 | ムコリピドーシスｉｉ型を治療するためのアデノ随伴ウイルスベクター |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2024056832A JP2024056832A (ja) | 2024-04-23 |
| JP2024056832A5 true JP2024056832A5 (enExample) | 2025-09-25 |
Family
ID=57737987
Family Applications (3)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2018531240A Active JP7347932B2 (ja) | 2015-12-15 | 2016-12-14 | ムコリピドーシスｉｉ型を治療するためのアデノ随伴ウイルスベクター |
| JP2021210071A Pending JP2022046635A (ja) | 2015-12-15 | 2021-12-24 | ムコリピドーシスｉｉ型を治療するためのアデノ随伴ウイルスベクター |
| JP2024019140A Pending JP2024056832A (ja) | 2015-12-15 | 2024-02-13 | ムコリピドーシスｉｉ型を治療するためのアデノ随伴ウイルスベクター |
Family Applications Before (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2018531240A Active JP7347932B2 (ja) | 2015-12-15 | 2016-12-14 | ムコリピドーシスｉｉ型を治療するためのアデノ随伴ウイルスベクター |
| JP2021210071A Pending JP2022046635A (ja) | 2015-12-15 | 2021-12-24 | ムコリピドーシスｉｉ型を治療するためのアデノ随伴ウイルスベクター |
Country Status (13)
| Country | Link |
|---|---|
| US (1) | US20200261598A1 (enExample) |
| EP (1) | EP3390644B1 (enExample) |
| JP (3) | JP7347932B2 (enExample) |
| KR (1) | KR102833376B1 (enExample) |
| CN (1) | CN108603199A (enExample) |
| AU (2) | AU2016372035B2 (enExample) |
| CA (1) | CA3008268A1 (enExample) |
| ES (1) | ES2991277T3 (enExample) |
| IL (1) | IL259964B (enExample) |
| MX (1) | MX2018007330A (enExample) |
| RU (1) | RU2742612C2 (enExample) |
| SG (2) | SG10201912935WA (enExample) |
| WO (1) | WO2017106313A1 (enExample) |
Families Citing this family (4)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US11491241B2 (en) | 2017-11-07 | 2022-11-08 | The University Of North Carolina At Chapel Hill | Optimized AGA genes and expression cassettes and their use |
| TW202039533A (zh) * | 2018-11-21 | 2020-11-01 | 美商史崔德生物公司 | 重組病毒載體及用於生產其之核酸 |
| US20220389453A1 (en) * | 2019-10-18 | 2022-12-08 | Research Institute At Nationwide Children's Hospital | Materials and methods for the treatment of disorders associated with the irf2bpl gene |
| MX2022009883A (es) * | 2020-02-13 | 2022-10-03 | Tenaya Therapeutics Inc | Vectores de genoterapia para tratar enfermedades cardíacas. |
Family Cites Families (20)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US5478745A (en) * | 1992-12-04 | 1995-12-26 | University Of Pittsburgh | Recombinant viral vector system |
| US6989264B2 (en) | 1997-09-05 | 2006-01-24 | Targeted Genetics Corporation | Methods for generating high titer helper-free preparations of released recombinant AAV vectors |
| US6566118B1 (en) | 1997-09-05 | 2003-05-20 | Targeted Genetics Corporation | Methods for generating high titer helper-free preparations of released recombinant AAV vectors |
| HK1039565B (zh) * | 1998-04-27 | 2005-10-21 | Peter M.C. Wong | 治疗内毒素血症的方法 |
| US6642038B1 (en) * | 1999-09-14 | 2003-11-04 | Genzyme Glycobiology Research Institute, Inc. | GlcNAc phosphotransferase of the lysosomal targeting pathway |
| US6723551B2 (en) | 2001-11-09 | 2004-04-20 | The United States Of America As Represented By The Department Of Health And Human Services | Production of adeno-associated virus in insect cells |
| ATE317916T1 (de) | 2001-11-13 | 2006-03-15 | Univ Pennsylvania | Verfahren zur identifizierung von adeno- assoziiertem virus (aav) sequenzen sowie kit zur ausführung der methode |
| JP2005523942A (ja) * | 2002-04-30 | 2005-08-11 | アヴィオル セラピューティクス インコーポレイテッド | 免疫療法のためのアデノウイルスベクター |
| US7510872B2 (en) | 2003-02-26 | 2009-03-31 | Nationwide Children's Hospital | Recombinant adeno-associated virus production |
| EP1625210B1 (en) | 2003-05-21 | 2010-12-01 | Genzyme Corporation | Methods for producing preparations of recombinant aav virions substantially free of empty capsids |
| US8283151B2 (en) | 2005-04-29 | 2012-10-09 | The United States Of America, As Represented By The Secretary, Department Of Health And Human Services | Isolation, cloning and characterization of new adeno-associated virus (AAV) serotypes |
| US7588772B2 (en) | 2006-03-30 | 2009-09-15 | Board Of Trustees Of The Leland Stamford Junior University | AAV capsid library and AAV capsid proteins |
| PL3252161T3 (pl) * | 2007-06-06 | 2022-03-07 | Genzyme Corporation | Terapia genowa dla lizosomalnych chorób spichrzeniowych |
| HUE054940T2 (hu) | 2009-06-16 | 2021-10-28 | Genzyme Corp | Javított eljárások rekombináns AAV-vektorok tisztítására |
| EP3103469B1 (en) * | 2010-06-25 | 2020-12-09 | Shire Human Genetic Therapies, Inc. | Cns delivery of therapeutic agents |
| US8663624B2 (en) | 2010-10-06 | 2014-03-04 | The Regents Of The University Of California | Adeno-associated virus virions with variant capsid and methods of use thereof |
| SG10201601110VA (en) | 2011-02-17 | 2016-03-30 | Univ Pennsylvania | Compositions and methods for altering tissue specificity and improving aav9-mediated gene transfer |
| WO2014144486A2 (en) * | 2013-03-15 | 2014-09-18 | The Children's Hospital Of Philadelphia | Vectors comprising stuffer/filler polynucleotide sequences and methods of use |
| CN105745326A (zh) * | 2013-10-24 | 2016-07-06 | 优尼科Ip有限公司 | 用于基因治疗神经疾病的aav-5假型载体 |
| AU2015252797C1 (en) * | 2014-05-02 | 2021-04-22 | Genzyme Corporation | AAV vectors for retinal and CNS gene therapy |
-
2016
- 2016-12-14 US US16/061,579 patent/US20200261598A1/en active Pending
- 2016-12-14 EP EP16822578.7A patent/EP3390644B1/en active Active
- 2016-12-14 RU RU2018124448A patent/RU2742612C2/ru active
- 2016-12-14 IL IL259964A patent/IL259964B/en unknown
- 2016-12-14 MX MX2018007330A patent/MX2018007330A/es unknown
- 2016-12-14 ES ES16822578T patent/ES2991277T3/es active Active
- 2016-12-14 SG SG10201912935WA patent/SG10201912935WA/en unknown
- 2016-12-14 JP JP2018531240A patent/JP7347932B2/ja active Active
- 2016-12-14 WO PCT/US2016/066611 patent/WO2017106313A1/en not_active Ceased
- 2016-12-14 CA CA3008268A patent/CA3008268A1/en active Pending
- 2016-12-14 KR KR1020187019970A patent/KR102833376B1/ko active Active
- 2016-12-14 SG SG11201804994QA patent/SG11201804994QA/en unknown
- 2016-12-14 AU AU2016372035A patent/AU2016372035B2/en active Active
- 2016-12-14 CN CN201680081705.8A patent/CN108603199A/zh active Pending
-
2021
- 2021-12-24 JP JP2021210071A patent/JP2022046635A/ja active Pending
-
2023
- 2023-06-28 AU AU2023204116A patent/AU2023204116A1/en active Pending
-
2024
- 2024-02-13 JP JP2024019140A patent/JP2024056832A/ja active Pending
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