RU2742612C2 - Векторы на основе аденоассоциированного вируса для лечения муколипидоза типа ii - Google Patents

Векторы на основе аденоассоциированного вируса для лечения муколипидоза типа ii Download PDF

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RU2742612C2
RU2742612C2 RU2018124448A RU2018124448A RU2742612C2 RU 2742612 C2 RU2742612 C2 RU 2742612C2 RU 2018124448 A RU2018124448 A RU 2018124448A RU 2018124448 A RU2018124448 A RU 2018124448A RU 2742612 C2 RU2742612 C2 RU 2742612C2
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aav
raav
gnptab
optionally
nucleic acid
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RU2018124448A3 (enExample
RU2018124448A (ru
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Нельсон ЙЮ
Донг-Киу ДЗИН
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Джензим Корпорейшн
Самсунг Лайф Паблик Уэлфэр Фаундейшн
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RU2018124448A 2015-12-15 2016-12-14 Векторы на основе аденоассоциированного вируса для лечения муколипидоза типа ii RU2742612C2 (ru)

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Application Number Priority Date Filing Date Title
US201562267502P 2015-12-15 2015-12-15
US62/267,502 2015-12-15
PCT/US2016/066611 WO2017106313A1 (en) 2015-12-15 2016-12-14 Adeno-associated viral vectors for treating mucolipidosis type ii

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RU2018124448A RU2018124448A (ru) 2020-01-17
RU2018124448A3 RU2018124448A3 (enExample) 2020-08-14
RU2742612C2 true RU2742612C2 (ru) 2021-02-09

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US (1) US20200261598A1 (enExample)
EP (1) EP3390644B1 (enExample)
JP (3) JP7347932B2 (enExample)
KR (1) KR102833376B1 (enExample)
CN (1) CN108603199A (enExample)
AU (2) AU2016372035B2 (enExample)
CA (1) CA3008268A1 (enExample)
ES (1) ES2991277T3 (enExample)
IL (1) IL259964B (enExample)
MX (1) MX2018007330A (enExample)
RU (1) RU2742612C2 (enExample)
SG (2) SG10201912935WA (enExample)
WO (1) WO2017106313A1 (enExample)

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RU2020118342A (ru) 2017-11-07 2021-12-08 Дзе Юниверсити Оф Норт Каролина Эт Чепел Хилл Оптимизированные гены aga и экспрессионные кластеры и их применение
MX2021005997A (es) * 2018-11-21 2021-08-11 Vectores virales recombinantes y acidos nucleicos para producirlos.
JP7781057B2 (ja) * 2019-10-18 2025-12-05 リサーチ インスティチュート アット ネイションワイド チルドレンズ ホスピタル Ｉｒｆ２ｂｐｌ遺伝子の変異に関連する障害の治療のための材料および方法
FI4103214T3 (fi) * 2020-02-13 2026-07-03 Tenaya Therapeutics Inc Geeniterapian vektorit sydänsairauden hoitoon

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