KR102833376B1 - 뮤코지질증 ii형을 치료하기 위한 아데노-관련 바이러스 벡터 - Google Patents

뮤코지질증 ii형을 치료하기 위한 아데노-관련 바이러스 벡터 Download PDF

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KR102833376B1
KR102833376B1 KR1020187019970A KR20187019970A KR102833376B1 KR 102833376 B1 KR102833376 B1 KR 102833376B1 KR 1020187019970 A KR1020187019970 A KR 1020187019970A KR 20187019970 A KR20187019970 A KR 20187019970A KR 102833376 B1 KR102833376 B1 KR 102833376B1
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넬슨 유
동-규 진
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젠자임 코포레이션
사회복지법인 삼성생명공익재단
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KR1020187019970A 2015-12-15 2016-12-14 뮤코지질증 ii형을 치료하기 위한 아데노-관련 바이러스 벡터 Active KR102833376B1 (ko)

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US201562267502P 2015-12-15 2015-12-15
US62/267,502 2015-12-15
PCT/US2016/066611 WO2017106313A1 (en) 2015-12-15 2016-12-14 Adeno-associated viral vectors for treating mucolipidosis type ii

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KR20180098294A KR20180098294A (ko) 2018-09-03
KR102833376B1 true KR102833376B1 (ko) 2025-07-11

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US20220389453A1 (en) * 2019-10-18 2022-12-08 Research Institute At Nationwide Children's Hospital Materials and methods for the treatment of disorders associated with the irf2bpl gene
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