JP2023554317A5 - - Google Patents

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Publication number
JP2023554317A5
JP2023554317A5 JP2023535364A JP2023535364A JP2023554317A5 JP 2023554317 A5 JP2023554317 A5 JP 2023554317A5 JP 2023535364 A JP2023535364 A JP 2023535364A JP 2023535364 A JP2023535364 A JP 2023535364A JP 2023554317 A5 JP2023554317 A5 JP 2023554317A5
Authority
JP
Japan
Prior art keywords
optionally substituted
alkyl
hydrogen
independently
pharmaceutically acceptable
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023535364A
Other languages
English (en)
Japanese (ja)
Other versions
JP2023554317A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2021/062974 external-priority patent/WO2022126000A1/en
Publication of JP2023554317A publication Critical patent/JP2023554317A/ja
Publication of JP2023554317A5 publication Critical patent/JP2023554317A5/ja
Pending legal-status Critical Current

Links

JP2023535364A 2020-12-11 2021-12-11 筋強直性ジストロフィー1を調節するための方法及び化合物 Pending JP2023554317A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202063124592P 2020-12-11 2020-12-11
US63/124,592 2020-12-11
PCT/US2021/062974 WO2022126000A1 (en) 2020-12-11 2021-12-11 Methods and compounds for modulating myotonic dystrophy 1

Publications (2)

Publication Number Publication Date
JP2023554317A JP2023554317A (ja) 2023-12-27
JP2023554317A5 true JP2023554317A5 (https=) 2024-12-19

Family

ID=81974018

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023535364A Pending JP2023554317A (ja) 2020-12-11 2021-12-11 筋強直性ジストロフィー1を調節するための方法及び化合物

Country Status (7)

Country Link
US (1) US20240166693A1 (https=)
EP (1) EP4259133A4 (https=)
JP (1) JP2023554317A (https=)
CN (1) CN117279636A (https=)
AU (1) AU2021396454A1 (https=)
CA (1) CA3201756A1 (https=)
WO (1) WO2022126000A1 (https=)

Families Citing this family (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
JP2024502469A (ja) * 2021-01-08 2024-01-19 デザイン セラピューティクス,インク. フリードライヒ運動失調症を治療するための方法及び化合物
US20250120928A1 (en) * 2021-07-14 2025-04-17 University Of Maryland, Baltimore Suberoylanilide hydroxamic acid (saha) drugs, conjugates, and nanoparticles, and methods of use thereof
KR20250016096A (ko) * 2022-04-01 2025-02-03 디자인 테라퓨틱스, 인크. 헌팅턴병을 조절하기 위한 방법 및 화합물
US11976066B1 (en) 2023-10-23 2024-05-07 King Faisal University Substituted 7-amino-3-(substituted benzoyl)indolizine-1-carboxylates as anti-tubercular agents
GB202401731D0 (en) * 2024-02-08 2024-03-27 Univ Strathclyde Polyamides

Family Cites Families (8)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CN1260006A (zh) * 1996-02-26 2000-07-12 加利福尼亚州技术学院 双链dna和杂环低聚物之间复合物的形成
US6506906B1 (en) * 1996-02-26 2003-01-14 California Institute Of Technology Preparation and use of bifunctional molecules having DNA sequence binding specificity
US20060270727A1 (en) * 2005-05-03 2006-11-30 Christian Melander Small molecule therapeutics and uses therefor
GB0722088D0 (en) * 2007-11-09 2007-12-19 Spirogen Ltd Pyrrolobenzodiazepines
WO2010001933A1 (ja) * 2008-07-01 2010-01-07 学校法人日本大学 標的遺伝子特異的ヒストン修飾制御剤
US10517877B2 (en) * 2016-03-30 2019-12-31 Wisconsin Alumni Research Foundation Compounds and methods for modulating frataxin expression
US20190343873A1 (en) * 2018-05-14 2019-11-14 Kyoto University Sequence-selective gene expression regulators
EP4234549A1 (en) * 2018-05-22 2023-08-30 Design Therapeutics, Inc. Methods and compounds for the treatment of genetic disease

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