JP2023538524A5 - - Google Patents

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Publication number
JP2023538524A5
JP2023538524A5 JP2023508065A JP2023508065A JP2023538524A5 JP 2023538524 A5 JP2023538524 A5 JP 2023538524A5 JP 2023508065 A JP2023508065 A JP 2023508065A JP 2023508065 A JP2023508065 A JP 2023508065A JP 2023538524 A5 JP2023538524 A5 JP 2023538524A5
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JP
Japan
Prior art keywords
compound
item
pharmaceutically acceptable
compound according
acceptable salt
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Granted
Application number
JP2023508065A
Other languages
English (en)
Japanese (ja)
Other versions
JP7895554B2 (ja
JP2023538524A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2021/044528 external-priority patent/WO2022031838A1/en
Publication of JP2023538524A publication Critical patent/JP2023538524A/ja
Publication of JP2023538524A5 publication Critical patent/JP2023538524A5/ja
Application granted granted Critical
Publication of JP7895554B2 publication Critical patent/JP7895554B2/ja
Active legal-status Critical Current
Anticipated expiration legal-status Critical

Links

JP2023508065A 2020-08-05 2021-08-04 スプライシングを調節する組成物 Active JP7895554B2 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202063061742P 2020-08-05 2020-08-05
US63/061,742 2020-08-05
PCT/US2021/044528 WO2022031838A1 (en) 2020-08-05 2021-08-04 Compositions for modulating splicing

Publications (3)

Publication Number Publication Date
JP2023538524A JP2023538524A (ja) 2023-09-08
JP2023538524A5 true JP2023538524A5 (enExample) 2024-08-13
JP7895554B2 JP7895554B2 (ja) 2026-07-28

Family

ID=80117649

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023508065A Active JP7895554B2 (ja) 2020-08-05 2021-08-04 スプライシングを調節する組成物

Country Status (13)

Country Link
US (1) US20230331718A1 (enExample)
EP (1) EP4192454B1 (enExample)
JP (1) JP7895554B2 (enExample)
KR (1) KR20230048106A (enExample)
CN (1) CN116171153B (enExample)
AR (1) AR123150A1 (enExample)
AU (1) AU2021320763A1 (enExample)
CA (1) CA3188104A1 (enExample)
IL (1) IL300352B1 (enExample)
MX (1) MX2023001558A (enExample)
TW (1) TW202216697A (enExample)
UY (1) UY39368A (enExample)
WO (1) WO2022031838A1 (enExample)

Families Citing this family (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2020163248A1 (en) 2019-02-04 2020-08-13 Skyhawk Therapeutics, Inc. Methods and compositions for modulating splicing
WO2020163541A1 (en) 2019-02-05 2020-08-13 Skyhawk Therapeutics, Inc. Methods and compositions for modulating splicing
KR102913697B1 (ko) * 2019-02-05 2026-01-15 스카이호크 테라퓨틱스, 인코포레이티드 스플라이싱을 조절하는 방법 및 조성물
KR102925385B1 (ko) 2019-02-06 2026-02-11 스카이호크 테라퓨틱스, 인코포레이티드 스플라이싱을 조절하는 방법 및 조성물
JP7603594B2 (ja) 2019-02-06 2024-12-20 スカイホーク・セラピューティクス・インコーポレーテッド スプライシングを調節するための方法および組成物
GB202106871D0 (en) * 2021-05-13 2021-06-30 Addex Pharmaceuticals Sa Novel compounds

Family Cites Families (8)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
ES2579949T3 (es) 2010-02-05 2016-08-17 Heptares Therapeutics Limited Derivados de 1,2,4-triazin-4-amina
MX2020001425A (es) * 2017-08-04 2020-08-06 Skyhawk Therapeutics Inc Metodos y composiciones para modular el empalme.
BR112020019373A2 (pt) 2018-03-27 2020-12-29 Ptc Therapeutics, Inc. Compostos para o tratamento da doença de hutington
JP2021521200A (ja) * 2018-04-10 2021-08-26 スカイホーク・セラピューティクス・インコーポレーテッド 癌の処置のための化合物
WO2020163248A1 (en) * 2019-02-04 2020-08-13 Skyhawk Therapeutics, Inc. Methods and compositions for modulating splicing
EP3920918A4 (en) 2019-02-05 2022-11-16 Skyhawk Therapeutics, Inc. METHODS AND COMPOSITIONS FOR MODULATION OF SPLICING
KR102913697B1 (ko) * 2019-02-05 2026-01-15 스카이호크 테라퓨틱스, 인코포레이티드 스플라이싱을 조절하는 방법 및 조성물
WO2022031998A2 (en) * 2020-08-05 2022-02-10 Skyhawk Therapeutics, Inc. Process for the preparation of intermediates useful in the preparation of compounds that modulate splicing

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