JP2023536902A5 - - Google Patents

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Publication number
JP2023536902A5
JP2023536902A5 JP2023507555A JP2023507555A JP2023536902A5 JP 2023536902 A5 JP2023536902 A5 JP 2023536902A5 JP 2023507555 A JP2023507555 A JP 2023507555A JP 2023507555 A JP2023507555 A JP 2023507555A JP 2023536902 A5 JP2023536902 A5 JP 2023536902A5
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JP
Japan
Prior art keywords
promoter
vector
expression cassette
pharmaceutical composition
identity
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JP2023507555A
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English (en)
Japanese (ja)
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JP2023536902A (ja
JP7853952B2 (ja
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Priority claimed from PCT/US2021/044416 external-priority patent/WO2022031760A1/en
Publication of JP2023536902A publication Critical patent/JP2023536902A/ja
Publication of JP2023536902A5 publication Critical patent/JP2023536902A5/ja
Application granted granted Critical
Publication of JP7853952B2 publication Critical patent/JP7853952B2/ja
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JP2023507555A 2020-08-05 2021-08-03 Glut1発現のためのアデノ随伴ウイルスベクターおよびその使用 Active JP7853952B2 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202063061726P 2020-08-05 2020-08-05
US63/061,726 2020-08-05
PCT/US2021/044416 WO2022031760A1 (en) 2020-08-05 2021-08-03 Adeno-associated viral vector for glut1 expression and uses thereof

Publications (3)

Publication Number Publication Date
JP2023536902A JP2023536902A (ja) 2023-08-30
JP2023536902A5 true JP2023536902A5 (OSRAM) 2024-08-13
JP7853952B2 JP7853952B2 (ja) 2026-04-30

Family

ID=80118621

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023507555A Active JP7853952B2 (ja) 2020-08-05 2021-08-03 Glut1発現のためのアデノ随伴ウイルスベクターおよびその使用

Country Status (11)

Country Link
US (1) US20230272422A1 (OSRAM)
EP (1) EP4192960A4 (OSRAM)
JP (1) JP7853952B2 (OSRAM)
KR (1) KR20230043123A (OSRAM)
CN (1) CN116113700A (OSRAM)
AU (1) AU2021321412A1 (OSRAM)
BR (1) BR112023001418A2 (OSRAM)
CA (1) CA3184233A1 (OSRAM)
IL (1) IL300185A (OSRAM)
MX (1) MX2023001419A (OSRAM)
WO (1) WO2022031760A1 (OSRAM)

Families Citing this family (8)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CN109641063B (zh) 2016-04-20 2022-11-15 能源环境和技术研究中心O.A., M.P. 用于增强pklr的基因表达的组合物和方法
SG11202002263TA (en) 2017-10-16 2020-04-29 Centro De Investigaciones Energeticas Medioambientales Y Tecnologicas Lentiviral vectors for delivery of pklr to treat pyruvate kinase deficiency
JP7576754B2 (ja) 2018-04-11 2024-11-01 スペースクラフト セブン リミテッド ライアビリティ カンパニー 幹細胞移植のための組成物および方法
AU2019261646A1 (en) 2018-04-27 2020-11-12 Spacecraft Seven, Llc Gene therapy for CNS degeneration
IL300263A (en) 2020-08-07 2023-03-01 Spacecraft Seven Llc Plakophilin-2 (PKP2) gene therapy using an AAV vector
CN114457045B (zh) * 2022-02-25 2023-07-14 中国人民解放军军事科学院军事医学研究院 抑制Slc2a1的RNAi腺相关病毒及其制备和应用
CN119857100B (zh) * 2023-10-19 2025-12-09 北京脑科学与类脑研究所 一种小分子药物plx4032在制备脑动静脉畸形疾病治疗的药物中的应用
WO2025137149A1 (en) * 2023-12-19 2025-06-26 The Trustees Of Columbia University In The City Of New York Compositions and methods for therapeutic vectors targeting brain microvasculature

Family Cites Families (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US8071740B2 (en) * 2000-11-17 2011-12-06 Vascular Biogenics Ltd. Promoters exhibiting endothelial cell specificity and methods of using same for regulation of angiogenesis
US20070161031A1 (en) * 2005-12-16 2007-07-12 The Board Of Trustees Of The Leland Stanford Junior University Functional arrays for high throughput characterization of gene expression regulatory elements
ES2836258T3 (es) * 2015-03-10 2021-06-24 Univ Columbia Construcciones de vectores virales adenoasociados de GLUT1 recombinante y métodos relacionados para restaurar la expresión de GLUT1
EP3393523B9 (en) * 2015-12-22 2023-10-04 Vrije Universiteit Brussel Endothelium-specific nucleic acid regulatory elements and methods and use thereof
JP6996728B2 (ja) * 2016-01-07 2022-01-17 学校法人自治医科大学 グルコーストランスポーター1発現用アデノ随伴ウイルスベクター

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