JP2023536618A5 - - Google Patents
Info
- Publication number
- JP2023536618A5 JP2023536618A5 JP2023507388A JP2023507388A JP2023536618A5 JP 2023536618 A5 JP2023536618 A5 JP 2023536618A5 JP 2023507388 A JP2023507388 A JP 2023507388A JP 2023507388 A JP2023507388 A JP 2023507388A JP 2023536618 A5 JP2023536618 A5 JP 2023536618A5
- Authority
- JP
- Japan
- Prior art keywords
- promoter
- mlp
- polynucleotide
- vector
- identity
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202063061727P | 2020-08-05 | 2020-08-05 | |
| US63/061,727 | 2020-08-05 | ||
| PCT/US2021/044412 WO2022031756A1 (en) | 2020-08-05 | 2021-08-03 | Csrp3 (cysteine and glycine rich protein 3) gene therapy |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2023536618A JP2023536618A (ja) | 2023-08-28 |
| JP2023536618A5 true JP2023536618A5 (OSRAM) | 2024-08-08 |
Family
ID=80118758
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023507388A Pending JP2023536618A (ja) | 2020-08-05 | 2021-08-03 | Ｃｓｒｐ３（システイン及びグリシンリッチタンパク質３）遺伝子治療 |
Country Status (11)
| Country | Link |
|---|---|
| US (1) | US20230257431A1 (OSRAM) |
| EP (1) | EP4192962A4 (OSRAM) |
| JP (1) | JP2023536618A (OSRAM) |
| KR (1) | KR20230042468A (OSRAM) |
| CN (1) | CN116234916A (OSRAM) |
| AU (1) | AU2021321410A1 (OSRAM) |
| BR (1) | BR112023001336A2 (OSRAM) |
| CA (1) | CA3184983A1 (OSRAM) |
| IL (1) | IL300187A (OSRAM) |
| MX (1) | MX2023000994A (OSRAM) |
| WO (1) | WO2022031756A1 (OSRAM) |
Families Citing this family (8)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| CN109641063B (zh) | 2016-04-20 | 2022-11-15 | 能源环境和技术研究中心O.A., M.P. | 用于增强pklr的基因表达的组合物和方法 |
| SG11202002263TA (en) | 2017-10-16 | 2020-04-29 | Centro De Investigaciones Energeticas Medioambientales Y Tecnologicas | Lentiviral vectors for delivery of pklr to treat pyruvate kinase deficiency |
| JP7576754B2 (ja) | 2018-04-11 | 2024-11-01 | スペースクラフト セブン リミテッド ライアビリティ カンパニー | 幹細胞移植のための組成物および方法 |
| AU2019261646A1 (en) | 2018-04-27 | 2020-11-12 | Spacecraft Seven, Llc | Gene therapy for CNS degeneration |
| MX2022009883A (es) | 2020-02-13 | 2022-10-03 | Tenaya Therapeutics Inc | Vectores de genoterapia para tratar enfermedades cardíacas. |
| IL300263A (en) | 2020-08-07 | 2023-03-01 | Spacecraft Seven Llc | Plakophilin-2 (PKP2) gene therapy using an AAV vector |
| EP4479543A1 (en) * | 2022-02-18 | 2024-12-25 | Ginkgo Bioworks, Inc. | Gene therapy for arrhythmogenic cardiomyopathy |
| WO2023178337A2 (en) * | 2022-03-18 | 2023-09-21 | University Of Florida Research Foundation, Incorporated | Methods and compositions for treating rbm20 related cardiomyopathy with a viral vector |
Family Cites Families (11)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| DE10004857A1 (de) * | 2000-02-03 | 2001-08-16 | Schering Ag | MLP-Gen, Nukleinsäuren, Polypeptide und deren Verwendung |
| US8299215B2 (en) | 2007-07-14 | 2012-10-30 | University Of Iowa Research Foundation | Methods and compositions for treating brain diseases |
| EP2792742A1 (en) * | 2013-04-17 | 2014-10-22 | Universitätsklinikum Hamburg-Eppendorf (UKE) | Gene-therapy vectors for treating cardiomyopathy |
| EP3564379A1 (en) | 2013-09-13 | 2019-11-06 | California Institute of Technology | Selective recovery |
| EP3137497B2 (en) | 2014-05-02 | 2025-03-05 | Genzyme Corporation | Aav vectors for retinal and cns gene therapy |
| EP3875593A1 (en) | 2015-12-11 | 2021-09-08 | California Institute of Technology | Targeting peptides for directing adeno-associated viruses (aavs) |
| DK3596222T5 (da) * | 2017-03-17 | 2024-09-02 | Res Inst Nationwide Childrens Hospital | Adenoassocieret virusvektorfremføring af muskelspecifik mikro-dystrophin til behandling af muskeldystrofi |
| PE20201264A1 (es) * | 2017-09-20 | 2020-11-19 | 4D Molecular Therapeutics Inc | Variantes de capsides de virus adenoasociados y metodos de uso de estas |
| CA3097375A1 (en) * | 2018-04-27 | 2019-10-31 | Universitat Heidelberg | Modified aav capsid polypeptides for treatment of muscular diseases |
| SG11202011061SA (en) * | 2018-06-08 | 2020-12-30 | University Of Florida Research Foundation Incorporated | Aav cardiac gene therapy for cardiomyopathy |
| WO2020205889A1 (en) * | 2019-04-01 | 2020-10-08 | Tenaya Therapeutics, Inc. | Adeno-associated virus with engineered capsid |
-
2021
- 2021-08-03 WO PCT/US2021/044412 patent/WO2022031756A1/en not_active Ceased
- 2021-08-03 MX MX2023000994A patent/MX2023000994A/es unknown
- 2021-08-03 BR BR112023001336A patent/BR112023001336A2/pt unknown
- 2021-08-03 CA CA3184983A patent/CA3184983A1/en active Pending
- 2021-08-03 EP EP21852527.7A patent/EP4192962A4/en active Pending
- 2021-08-03 AU AU2021321410A patent/AU2021321410A1/en active Pending
- 2021-08-03 JP JP2023507388A patent/JP2023536618A/ja active Pending
- 2021-08-03 IL IL300187A patent/IL300187A/en unknown
- 2021-08-03 KR KR1020237003436A patent/KR20230042468A/ko active Pending
- 2021-08-03 US US18/019,396 patent/US20230257431A1/en active Pending
- 2021-08-03 CN CN202180057650.8A patent/CN116234916A/zh active Pending
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