JP2023534951A5 - - Google Patents

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Publication number
JP2023534951A5
JP2023534951A5 JP2023502828A JP2023502828A JP2023534951A5 JP 2023534951 A5 JP2023534951 A5 JP 2023534951A5 JP 2023502828 A JP2023502828 A JP 2023502828A JP 2023502828 A JP2023502828 A JP 2023502828A JP 2023534951 A5 JP2023534951 A5 JP 2023534951A5
Authority
JP
Japan
Application number
JP2023502828A
Other languages
Japanese (ja)
Other versions
JPWO2022016043A5 (https=
JP2023534951A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2021/041946 external-priority patent/WO2022016043A1/en
Publication of JP2023534951A publication Critical patent/JP2023534951A/ja
Publication of JPWO2022016043A5 publication Critical patent/JPWO2022016043A5/ja
Publication of JP2023534951A5 publication Critical patent/JP2023534951A5/ja
Pending legal-status Critical Current

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JP2023502828A 2020-07-16 2021-07-16 組織特異的送達のためのコンジュゲートされたオリゴヌクレオチド Pending JP2023534951A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202063052811P 2020-07-16 2020-07-16
US63/052,811 2020-07-16
PCT/US2021/041946 WO2022016043A1 (en) 2020-07-16 2021-07-16 Conjugated oligonucleotides for tissue specific delivery

Publications (3)

Publication Number Publication Date
JP2023534951A JP2023534951A (ja) 2023-08-15
JPWO2022016043A5 JPWO2022016043A5 (https=) 2024-07-25
JP2023534951A5 true JP2023534951A5 (https=) 2024-07-25

Family

ID=79554340

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023502828A Pending JP2023534951A (ja) 2020-07-16 2021-07-16 組織特異的送達のためのコンジュゲートされたオリゴヌクレオチド

Country Status (7)

Country Link
US (1) US20220042015A1 (https=)
EP (1) EP4181932A4 (https=)
JP (1) JP2023534951A (https=)
CN (1) CN116600817A (https=)
AU (1) AU2021308657A1 (https=)
CA (1) CA3174068A1 (https=)
WO (1) WO2022016043A1 (https=)

Families Citing this family (10)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CA3033368A1 (en) * 2016-08-12 2018-02-15 University Of Massachusetts Conjugated oligonucleotides
JP7627042B2 (ja) 2018-08-23 2025-02-05 ユニバーシティー オブ マサチューセッツ O-メチルリッチ完全安定化オリゴヌクレオチド
US12365894B2 (en) 2019-09-16 2025-07-22 University Of Massachusetts Branched lipid conjugates of siRNA for specific tissue delivery
WO2021242883A1 (en) 2020-05-26 2021-12-02 University Of Massachusetts Synthetic oligonucleotides having regions of block and cluster modifications
US12366070B2 (en) 2021-04-23 2025-07-22 Stephen Cochran Cover for circular-profile downspouts having protection from animal/insect intrusion and damage/debris accumulation
IL317825A (en) 2022-07-25 2025-02-01 Amgen Inc RNA interference constructs and methods for inhibiting fam13a expression
US20260049309A1 (en) * 2022-08-15 2026-02-19 Novo Nordisk A/S Regulation of activity of rnai molecules
WO2024069235A2 (en) 2022-09-30 2024-04-04 Sixfold Bioscience Ltd. Compositions containing oligonucleotides with theranostic applications
WO2025217569A1 (en) * 2024-04-11 2025-10-16 University Of Massachusetts Conjugated chemically-modified dsrna during ex vivo perfusion of organs
WO2025259747A2 (en) * 2024-06-12 2025-12-18 Alnylam Pharmaceuticals, Inc. Dystrophy myotonic protein kinase (dmpk) irna compositions and methods of use thereof

Family Cites Families (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US9745574B2 (en) * 2009-02-04 2017-08-29 Rxi Pharmaceuticals Corporation RNA duplexes with single stranded phosphorothioate nucleotide regions for additional functionality
CA3033368A1 (en) * 2016-08-12 2018-02-15 University Of Massachusetts Conjugated oligonucleotides
EP3517610A4 (en) * 2016-09-23 2020-05-27 National University Corporation Tokyo Medical and Dental University THROUGH HETERODUPLEX NUCLEIC ACID THROUGH BLOOD BRAIN CABINET
WO2019217459A1 (en) * 2018-05-07 2019-11-14 Alnylam Pharmaceuticals, Inc. Extrahepatic delivery
JP2023550485A (ja) * 2020-11-23 2023-12-01 ユニバーシティー オブ マサチューセッツ Dgat2調節のためのオリゴヌクレオチド

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