JP2023524071A5 - - Google Patents
Info
- Publication number
- JP2023524071A5 JP2023524071A5 JP2022566343A JP2022566343A JP2023524071A5 JP 2023524071 A5 JP2023524071 A5 JP 2023524071A5 JP 2022566343 A JP2022566343 A JP 2022566343A JP 2022566343 A JP2022566343 A JP 2022566343A JP 2023524071 A5 JP2023524071 A5 JP 2023524071A5
- Authority
- JP
- Japan
Links
Applications Claiming Priority (5)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202063019170P | 2020-05-01 | 2020-05-01 | |
| US63/019,170 | 2020-05-01 | ||
| US202063082997P | 2020-09-24 | 2020-09-24 | |
| US63/082,997 | 2020-09-24 | ||
| PCT/US2021/030257 WO2021222801A2 (en) | 2020-05-01 | 2021-04-30 | Nucleic acids and methods of treatment for cystic fibrosis |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2023524071A JP2023524071A (ja) | 2023-06-08 |
| JPWO2021222801A5 JPWO2021222801A5 (https=) | 2024-05-10 |
| JP2023524071A5 true JP2023524071A5 (https=) | 2024-05-10 |
Family
ID=78374030
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022566343A Pending JP2023524071A (ja) | 2020-05-01 | 2021-04-30 | 嚢胞性線維症を治療するための核酸及び方法 |
Country Status (7)
| Country | Link |
|---|---|
| US (2) | US12070509B2 (https=) |
| EP (1) | EP4143217A4 (https=) |
| JP (1) | JP2023524071A (https=) |
| AU (1) | AU2021263590A1 (https=) |
| CA (1) | CA3176844A1 (https=) |
| NZ (1) | NZ794954A (https=) |
| WO (1) | WO2021222801A2 (https=) |
Families Citing this family (19)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2017201347A1 (en) | 2016-05-18 | 2017-11-23 | Modernatx, Inc. | Polynucleotides encoding cystic fibrosis transmembrane conductance regulator for the treatment of cystic fibrosis |
| CN113166783B (zh) | 2018-10-09 | 2024-10-11 | 不列颠哥伦比亚大学 | 包含无有机溶剂和去污剂的转染活性囊泡的组合物和系统以及与之相关的方法 |
| US12070509B2 (en) * | 2020-05-01 | 2024-08-27 | Arcturus Therapeutics, Inc. | Nucleic acids and methods of treatment for cystic fibrosis |
| CN116368226A (zh) | 2020-09-04 | 2023-06-30 | 维乎医疗有限公司 | 用于加帽rna的组合物和方法 |
| IL303195A (en) | 2020-11-25 | 2023-07-01 | Akagera Medicines Inc | Lipid nanoparticles for delivery of nucleic acids and related methods of use |
| JP2024511463A (ja) * | 2021-03-22 | 2024-03-13 | リコード セラピューティクス，インク． | 細胞への標的送達のための組成物および方法 |
| JP2024511437A (ja) | 2021-03-23 | 2024-03-13 | リコード セラピューティクス，インク． | ポリヌクレオチド組成物、関連製剤、およびその使用方法 |
| KR20240006603A (ko) | 2021-05-07 | 2024-01-15 | 헬릭스 나노테크놀로지스, 인코포레이티드 | 변형된 리보핵산 및 이의 용도 |
| MX2024002726A (es) | 2021-09-03 | 2024-03-20 | CureVac SE | Nuevas nanoparticulas lipidicas para la administracion de acidos nucleicos. |
| US20250099614A1 (en) | 2022-01-28 | 2025-03-27 | CureVac SE | Nucleic acid encoded transcription factor inhibitors |
| WO2023227608A1 (en) | 2022-05-25 | 2023-11-30 | Glaxosmithkline Biologicals Sa | Nucleic acid based vaccine encoding an escherichia coli fimh antigenic polypeptide |
| EP4531819A2 (en) | 2022-05-25 | 2025-04-09 | Akagera Medicines, Inc. | Lipid nanoparticles for delivery of nucleic acids and methods of use thereof |
| WO2024089229A1 (en) | 2022-10-28 | 2024-05-02 | CureVac SE | Improved formulations comprising lipid-based carriers encapsulating rna |
| KR20250153298A (ko) | 2023-03-08 | 2025-10-24 | 큐어백 에스이 | 핵산 전달을 위한 신규의 지질 나노입자 제형 |
| WO2024230934A1 (en) | 2023-05-11 | 2024-11-14 | CureVac SE | Therapeutic nucleic acid for the treatment of ophthalmic diseases |
| US20250144237A1 (en) * | 2023-11-07 | 2025-05-08 | Cila Therapeutics Inc. | Agents, compositions and methods for enhanced delivery of nucleic acids to the cells within the respiratory system |
| WO2025103803A1 (en) | 2023-11-13 | 2025-05-22 | CureVac SE | Immunotherapy against neuronal and brain tumors |
| US12364773B2 (en) | 2023-12-01 | 2025-07-22 | Recode Therapeutics, Inc. | Lipid nanoparticle compositions and uses thereof |
| WO2026072721A1 (en) * | 2024-09-25 | 2026-04-02 | Carbon Biosciences, Inc. | Parvovirus compositions and methods for gene therapy |
Family Cites Families (32)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US4511069A (en) | 1981-06-04 | 1985-04-16 | The Pharmasol Corporation | Dispensing system |
| US4778810A (en) | 1987-01-08 | 1988-10-18 | Nastech Pharmaceutical Co., Inc. | Nasal delivery of caffeine |
| JP3257675B2 (ja) | 1990-10-12 | 2002-02-18 | マックス−プランク−ゲゼルシャフト ツール フェルデルング デル ビッセンシャフテン エー．ファウ． | 修飾リボザイム |
| US5652094A (en) | 1992-01-31 | 1997-07-29 | University Of Montreal | Nucleozymes |
| US5780014A (en) | 1995-04-14 | 1998-07-14 | Inhale Therapeutic Systems | Method and apparatus for pulmonary administration of dry powder alpha 1-antitrypsin |
| KR20040051450A (ko) * | 2002-12-12 | 2004-06-18 | 주식회사 인비보사이언스 | 알엔에이의 생체내 안정성을 증가시키는 벡터 |
| EP2049665A2 (en) | 2006-07-28 | 2009-04-22 | Applera Corporation | Dinucleotide mrna cap analogs |
| WO2009058911A2 (en) | 2007-10-31 | 2009-05-07 | Applied Biosystems Inc. | Preparation and isolation of 5' capped mrna |
| WO2009086558A1 (en) | 2008-01-02 | 2009-07-09 | Tekmira Pharmaceuticals Corporation | Improved compositions and methods for the delivery of nucleic acids |
| AU2009238175C1 (en) | 2008-04-15 | 2023-11-30 | Arbutus Biopharma Corporation | Novel lipid formulations for nucleic acid delivery |
| CN104119242B (zh) | 2008-10-09 | 2017-07-07 | 泰米拉制药公司 | 改善的氨基脂质和递送核酸的方法 |
| WO2010048536A2 (en) | 2008-10-23 | 2010-04-29 | Alnylam Pharmaceuticals, Inc. | Processes for preparing lipids |
| HUE037082T2 (hu) | 2008-11-10 | 2018-08-28 | Arbutus Biopharma Corp | Új lipidek és készítmények terápiás hatóanyagok szállítására |
| EP3243504A1 (en) | 2009-01-29 | 2017-11-15 | Arbutus Biopharma Corporation | Improved lipid formulation |
| KR20180094137A (ko) | 2009-05-05 | 2018-08-22 | 알닐람 파마슈티칼스 인코포레이티드 | 지질 조성물 |
| MX342785B (es) | 2009-06-10 | 2016-10-12 | Alnylam Pharmaceuticals Inc | Formulacion mejorada de lipido. |
| SG186085A1 (en) | 2010-06-03 | 2013-01-30 | Alnylam Pharmaceuticals Inc | Biodegradable lipids for the delivery of active agents |
| AU2013243948A1 (en) * | 2012-04-02 | 2014-10-30 | Moderna Therapeutics, Inc. | Modified polynucleotides for the production of proteins associated with human disease |
| CA2868391A1 (en) * | 2012-04-02 | 2013-10-10 | Stephane Bancel | Polynucleotides comprising n1-methyl-pseudouridine and methods for preparing the same |
| KR20210122917A (ko) | 2013-03-14 | 2021-10-12 | 샤이어 휴먼 지네틱 테라피즈 인크. | Cftr mrna 조성물 및 관련 방법 및 사용 |
| WO2015051169A2 (en) | 2013-10-02 | 2015-04-09 | Moderna Therapeutics, Inc. | Polynucleotide molecules and uses thereof |
| EA034103B1 (ru) | 2013-10-22 | 2019-12-27 | Транслейт Био, Инк. | СПОСОБ ЛЕЧЕНИЯ ФЕНИЛКЕТОНУРИИ С ПРИМЕНЕНИЕМ мРНК |
| US9593077B2 (en) * | 2013-11-18 | 2017-03-14 | Arcturus Therapeutics, Inc. | Ionizable cationic lipid for RNA delivery |
| AU2015338923B2 (en) * | 2014-11-02 | 2021-10-21 | Arcturus Therapeutics, Inc. | Messenger UNA molecules and uses thereof |
| ES2964690T3 (es) | 2015-09-21 | 2024-04-09 | Trilink Biotechnologies Llc | Método para sintetizar ARN con caperuza 5' |
| US10487105B2 (en) | 2016-10-19 | 2019-11-26 | Arcturus Therapeutics, Inc. | Trinucleotide MRNA cap analogs |
| WO2018119163A1 (en) * | 2016-12-21 | 2018-06-28 | Payne Joseph E | Ionizable cationic lipid for rna delivery |
| EA201991747A1 (ru) * | 2017-02-27 | 2020-06-04 | Транслейт Био, Инк. | НОВАЯ КОДОН-ОПТИМИЗИРОВАННАЯ мРНК CFTR |
| WO2018160592A1 (en) | 2017-02-28 | 2018-09-07 | Arcturus Therapeutics, Inc. | Translatable molecules and synthesis thereof |
| ES3039647T3 (en) * | 2017-05-31 | 2025-10-23 | Arcturus Therapeutics Inc | Synthesis and structure of high potency rna therapeutics |
| US12070509B2 (en) * | 2020-05-01 | 2024-08-27 | Arcturus Therapeutics, Inc. | Nucleic acids and methods of treatment for cystic fibrosis |
| EP4426266A4 (en) * | 2021-11-03 | 2025-11-05 | Arcturus Therapeutics Inc | LIPID FORMULATIONS CONTAINING NUCLEIC ACIDS AND METHODS OF TREATMENT OF CYSTIC FIBROSIS |
-
2021
- 2021-04-30 US US17/246,558 patent/US12070509B2/en active Active
- 2021-04-30 WO PCT/US2021/030257 patent/WO2021222801A2/en not_active Ceased
- 2021-04-30 AU AU2021263590A patent/AU2021263590A1/en active Pending
- 2021-04-30 NZ NZ794954A patent/NZ794954A/en unknown
- 2021-04-30 CA CA3176844A patent/CA3176844A1/en active Pending
- 2021-04-30 JP JP2022566343A patent/JP2023524071A/ja active Pending
- 2021-04-30 EP EP21795851.1A patent/EP4143217A4/en active Pending
-
2024
- 2024-06-04 US US18/732,954 patent/US20250049950A1/en active Pending