JP2023522708A5 - - Google Patents

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Publication number
JP2023522708A5
JP2023522708A5 JP2022563930A JP2022563930A JP2023522708A5 JP 2023522708 A5 JP2023522708 A5 JP 2023522708A5 JP 2022563930 A JP2022563930 A JP 2022563930A JP 2022563930 A JP2022563930 A JP 2022563930A JP 2023522708 A5 JP2023522708 A5 JP 2023522708A5
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JP2022563930A
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Japanese (ja)
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JP7721568B2 (ja
JP2023522708A (ja
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Priority claimed from PCT/US2021/028489 external-priority patent/WO2021216778A2/en
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Publication of JP2023522708A5 publication Critical patent/JP2023522708A5/ja
Priority to JP2025127056A priority Critical patent/JP2025163106A/ja
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JP2022563930A 2020-04-21 2021-04-21 新皮質層5グルタミン酸作動性ニューロンにおいて遺伝子発現を選択的に調節する人工発現構築物 Active JP7721568B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2025127056A JP2025163106A (ja) 2020-04-21 2025-07-30 新皮質層5グルタミン酸作動性ニューロンにおいて遺伝子発現を選択的に調節する人工発現構築物

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202063013342P 2020-04-21 2020-04-21
US63/013,342 2020-04-21
PCT/US2021/028489 WO2021216778A2 (en) 2020-04-21 2021-04-21 Artificial expression constructs for selectively modulating gene expression in neocortical layer 5 glutamatergic neurons

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2025127056A Division JP2025163106A (ja) 2020-04-21 2025-07-30 新皮質層5グルタミン酸作動性ニューロンにおいて遺伝子発現を選択的に調節する人工発現構築物

Publications (3)

Publication Number Publication Date
JP2023522708A JP2023522708A (ja) 2023-05-31
JP2023522708A5 true JP2023522708A5 (https=) 2024-02-27
JP7721568B2 JP7721568B2 (ja) 2025-08-12

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ID=78269916

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2022563930A Active JP7721568B2 (ja) 2020-04-21 2021-04-21 新皮質層5グルタミン酸作動性ニューロンにおいて遺伝子発現を選択的に調節する人工発現構築物
JP2025127056A Pending JP2025163106A (ja) 2020-04-21 2025-07-30 新皮質層5グルタミン酸作動性ニューロンにおいて遺伝子発現を選択的に調節する人工発現構築物

Family Applications After (1)

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JP2025127056A Pending JP2025163106A (ja) 2020-04-21 2025-07-30 新皮質層5グルタミン酸作動性ニューロンにおいて遺伝子発現を選択的に調節する人工発現構築物

Country Status (7)

Country Link
US (1) US20230159952A1 (https=)
EP (1) EP4139462A4 (https=)
JP (2) JP7721568B2 (https=)
KR (1) KR20230002788A (https=)
AU (1) AU2021261359A1 (https=)
CA (1) CA3175993A1 (https=)
WO (1) WO2021216778A2 (https=)

Families Citing this family (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP4413142A4 (en) * 2021-10-05 2025-11-05 Allen Inst ARTIFICIAL EXPRESSION CONSTRUCTIONS TO MODULATE GENE EXPRESSION IN THE CEREBELLUM AND IN A SECONDARY CELL TYPE
JP2025520385A (ja) * 2022-06-13 2025-07-03 アレン インスティテュート 中枢神経系の非神経細胞において遺伝子発現を調節するための人工発現コンストラクト
WO2025059552A1 (en) * 2023-09-14 2025-03-20 Allen Institute Artificial expression constructs for modulating gene expression in the basal ganglia
WO2025179180A1 (en) * 2024-02-23 2025-08-28 Allen Institute Artificial expression constructs for modulating gene expression in motor neurons and cerebellar neurons

Family Cites Families (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US9920317B2 (en) * 2010-11-12 2018-03-20 The General Hospital Corporation Polycomb-associated non-coding RNAs
US10973930B2 (en) * 2016-02-18 2021-04-13 The Penn State Research Foundation Generating GABAergic neurons in brains
WO2020076614A1 (en) * 2018-10-08 2020-04-16 Allen Institute Artificial expression constructs for selectively modulating gene expression in interneurons
AU2019357039B2 (en) * 2018-10-12 2025-10-09 Genzyme Corporation Generation of improved human pah for treatment of severe PKU by liver-directed gene replacement therapy
US20220249703A1 (en) * 2019-02-15 2022-08-11 Allen Institute Artificial expression constructs for selectively modulating gene expression in selected neuronal cell populations

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