JP2022520437A5 - - Google Patents

Info

Publication number
JP2022520437A5
JP2022520437A5 JP2021547404A JP2021547404A JP2022520437A5 JP 2022520437 A5 JP2022520437 A5 JP 2022520437A5 JP 2021547404 A JP2021547404 A JP 2021547404A JP 2021547404 A JP2021547404 A JP 2021547404A JP 2022520437 A5 JP2022520437 A5 JP 2022520437A5
Authority
JP
Japan
Prior art keywords
expression construct
seq
artificial expression
construct according
aav
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Granted
Application number
JP2021547404A
Other languages
English (en)
Japanese (ja)
Other versions
JP7608348B2 (ja
JP2022520437A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2020/018416 external-priority patent/WO2020168279A2/en
Publication of JP2022520437A publication Critical patent/JP2022520437A/ja
Publication of JP2022520437A5 publication Critical patent/JP2022520437A5/ja
Priority to JP2024220548A priority Critical patent/JP2025041709A/ja
Application granted granted Critical
Publication of JP7608348B2 publication Critical patent/JP7608348B2/ja
Active legal-status Critical Current
Anticipated expiration legal-status Critical

Links

JP2021547404A 2019-02-15 2020-02-14 選択されたニューロン細胞集団における遺伝子発現を選択的に調節するための人工発現コンストラクト Active JP7608348B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2024220548A JP2025041709A (ja) 2019-02-15 2024-12-17 選択されたニューロン細胞集団における遺伝子発現を選択的に調節するための人工発現コンストラクト

Applications Claiming Priority (7)

Application Number Priority Date Filing Date Title
US201962806686P 2019-02-15 2019-02-15
US201962806660P 2019-02-15 2019-02-15
US62/806,660 2019-02-15
US62/806,686 2019-02-15
US201962874859P 2019-07-16 2019-07-16
US62/874,859 2019-07-16
PCT/US2020/018416 WO2020168279A2 (en) 2019-02-15 2020-02-14 Artificial expression constructs for selectively modulating gene expression in selected neuronal cell populations

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2024220548A Division JP2025041709A (ja) 2019-02-15 2024-12-17 選択されたニューロン細胞集団における遺伝子発現を選択的に調節するための人工発現コンストラクト

Publications (3)

Publication Number Publication Date
JP2022520437A JP2022520437A (ja) 2022-03-30
JP2022520437A5 true JP2022520437A5 (https=) 2022-12-28
JP7608348B2 JP7608348B2 (ja) 2025-01-06

Family

ID=72044145

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2021547404A Active JP7608348B2 (ja) 2019-02-15 2020-02-14 選択されたニューロン細胞集団における遺伝子発現を選択的に調節するための人工発現コンストラクト
JP2024220548A Pending JP2025041709A (ja) 2019-02-15 2024-12-17 選択されたニューロン細胞集団における遺伝子発現を選択的に調節するための人工発現コンストラクト

Family Applications After (1)

Application Number Title Priority Date Filing Date
JP2024220548A Pending JP2025041709A (ja) 2019-02-15 2024-12-17 選択されたニューロン細胞集団における遺伝子発現を選択的に調節するための人工発現コンストラクト

Country Status (6)

Country Link
US (1) US20220249703A1 (https=)
EP (1) EP3923995A4 (https=)
JP (2) JP7608348B2 (https=)
AU (1) AU2020223367A1 (https=)
CA (1) CA3142948A1 (https=)
WO (1) WO2020168279A2 (https=)

Families Citing this family (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
AU2021261359A1 (en) * 2020-04-21 2022-12-08 Allen Institute Artificial expression constructs for selectively modulating gene expression in neocortical layer 5 glutamatergic neurons
WO2022103859A1 (en) * 2020-11-10 2022-05-19 Allen Institute Artificial expression constructs for modulating gene expression in chandelier cells
WO2022212585A1 (en) * 2021-03-30 2022-10-06 Allen Institute Artificial expression constructs for modulating gene expression in claustrum neurons
WO2022246276A2 (en) * 2021-05-21 2022-11-24 Allen Institute Artificial expression constructs for modulating gene expression in neurons within the thalamus
EP4413142A4 (en) * 2021-10-05 2025-11-05 Allen Inst ARTIFICIAL EXPRESSION CONSTRUCTIONS TO MODULATE GENE EXPRESSION IN THE CEREBELLUM AND IN A SECONDARY CELL TYPE
AU2024308266A1 (en) * 2023-06-28 2025-12-18 Allen Institute Artificial expression constructs for modulating gene expression in cardiomyocytes

Family Cites Families (9)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
DE69918090T2 (de) * 1998-04-24 2005-06-16 University Of Florida, Gainesville Rekombinanter adeno-assoziierter viraler vektor, der alpha-1 antitrypsin kodiert, zur gentherapie
US20070037165A1 (en) * 2000-09-08 2007-02-15 Applera Corporation Polymorphisms in known genes associated with human disease, methods of detection and uses thereof
CA2817256A1 (en) * 2010-11-12 2012-05-18 The General Hospital Corporation Polycomb-associated non-coding rnas
AU2013201287B2 (en) * 2012-03-06 2015-05-14 Duke University Synthetic regulation of gene expression
WO2013155222A2 (en) * 2012-04-10 2013-10-17 The Regents Of The University Of California Brain-specific enhancers for cell-based therapy
US9790490B2 (en) * 2015-06-18 2017-10-17 The Broad Institute Inc. CRISPR enzymes and systems
KR102423442B1 (ko) 2015-12-11 2022-07-20 캘리포니아 인스티튜트 오브 테크놀로지 아데노-관련 바이러스를 지시하기 위한 타겟팅 펩타이드
US10973930B2 (en) * 2016-02-18 2021-04-13 The Penn State Research Foundation Generating GABAergic neurons in brains
WO2020097121A1 (en) * 2018-11-05 2020-05-14 Allen Institute Artificial expression constructs for selectively modulating gene expression in excitatory cortical neurons

Similar Documents

Publication Publication Date Title
JP2022520437A5 (https=)
NO20063026L (no) Antistoffer
NO20043419L (no) Nytt cytokin, zcytor17-ligand
WO2009110952A3 (en) Control of viral-host membrane fusion with hydrogen bond surrogate-based artificial helices
JP2010510315A5 (https=)
JP2003515323A5 (https=)
DK1453850T3 (da) EGVIII-endoglukanase og nukleinsyrer kodende for det samme
CY1106875T1 (el) Αντιγονικα πεπτιδια απο neisseria
CY1118037T1 (el) Αντισωματα εναντι του αβητα και h χρηση τους
JP2004533208A5 (https=)
CO5560624A2 (es) Toxinas de cry3a modificadas y secuencias de acido nucleico que las modifican
JP2004525608A5 (https=)
JP2019214579A5 (https=)
JP2023522708A5 (https=)
ATE493497T1 (de) Verfahren zur herstellung von oligopeptiden
JP2004508843A5 (https=)
ATE469655T1 (de) Bakteriophagenvermittelte impfung
ATE474589T1 (de) Angiogene peptide und ihre verwendungen
WO2003090667A3 (fr) Composition immunogene ou vaccinale non immunosuppressive, comprenant une proteine e7 mutee du virus hpv-16
CY1116756T1 (el) Αιμοκυανινη και κωδικευουσα γι'αυτην ακολουθια νουκλεϊνικου οξεος
DK1368372T3 (da) Peptid med affinitet til det virale gp120-protein samt anvendelse deraf
AU2003244404A1 (en) Retroviral vectors pseudotyped with influenza virus hemagglutinin for gene delivery
CY1110308T1 (el) Μοριο νουκλεϊνικου οξεος, το οποιο περιλαμβανει μια κωδικευσουσα για αιμοκυανινη ακολουθια νουκλεϊνικου οξεος και τουλαχιστον μια ακολουθια ιντρονιου
NZ513549A (en) Malaria vaccine
RU2006142760A (ru) Генная вакцина рекомбинантного хемотаксического антигена