JP2022546042A5 - - Google Patents
Info
- Publication number
- JP2022546042A5 JP2022546042A5 JP2022513165A JP2022513165A JP2022546042A5 JP 2022546042 A5 JP2022546042 A5 JP 2022546042A5 JP 2022513165 A JP2022513165 A JP 2022513165A JP 2022513165 A JP2022513165 A JP 2022513165A JP 2022546042 A5 JP2022546042 A5 JP 2022546042A5
- Authority
- JP
- Japan
- Prior art keywords
- subject
- composition
- use according
- approximately
- rhtpp1
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2025134120A JP2025165414A (ja) | 2019-08-29 | 2025-08-12 | 小児対象のｃｌｎ２疾患を治療するための方法 |
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201962893535P | 2019-08-29 | 2019-08-29 | |
| US62/893,535 | 2019-08-29 | ||
| PCT/US2020/048704 WO2021042020A1 (en) | 2019-08-29 | 2020-08-31 | Methods for treating cln2 disease in pediatric subjects |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2025134120A Division JP2025165414A (ja) | 2019-08-29 | 2025-08-12 | 小児対象のｃｌｎ２疾患を治療するための方法 |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2022546042A JP2022546042A (ja) | 2022-11-02 |
| JP2022546042A5 true JP2022546042A5 (https=) | 2023-09-08 |
Family
ID=72470612
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022513165A Pending JP2022546042A (ja) | 2019-08-29 | 2020-08-31 | 小児対象のｃｌｎ２疾患を治療するための方法 |
| JP2025134120A Pending JP2025165414A (ja) | 2019-08-29 | 2025-08-12 | 小児対象のｃｌｎ２疾患を治療するための方法 |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2025134120A Pending JP2025165414A (ja) | 2019-08-29 | 2025-08-12 | 小児対象のｃｌｎ２疾患を治療するための方法 |
Country Status (25)
| Country | Link |
|---|---|
| US (1) | US20220273775A1 (https=) |
| EP (2) | EP4021575B1 (https=) |
| JP (2) | JP2022546042A (https=) |
| KR (1) | KR20220054375A (https=) |
| CN (1) | CN114828960A (https=) |
| AR (1) | AR119871A1 (https=) |
| AU (1) | AU2020336984B2 (https=) |
| BR (1) | BR112022003598A2 (https=) |
| CA (1) | CA3152521A1 (https=) |
| CL (1) | CL2022000496A1 (https=) |
| DK (1) | DK4021575T3 (https=) |
| ES (1) | ES2987156T3 (https=) |
| FI (1) | FI4021575T3 (https=) |
| HR (2) | HRP20240871T1 (https=) |
| HU (1) | HUE067135T2 (https=) |
| IL (1) | IL290763A (https=) |
| LT (1) | LT4021575T (https=) |
| MX (1) | MX2022002451A (https=) |
| PL (1) | PL4021575T3 (https=) |
| PT (1) | PT4021575T (https=) |
| RS (1) | RS65763B1 (https=) |
| SI (1) | SI4021575T1 (https=) |
| SM (1) | SMT202400315T1 (https=) |
| TW (1) | TW202122106A (https=) |
| WO (1) | WO2021042020A1 (https=) |
Families Citing this family (1)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US20220323019A1 (en) * | 2021-04-02 | 2022-10-13 | Neuropace, Inc. | Systems and methods for obtaining a clinical response estimate biomarker using machine-learned models trained on implanted neurostimulator data |
Family Cites Families (8)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US6302685B1 (en) | 1997-09-16 | 2001-10-16 | University Of Medicine And Dentistry Of New Jersey | Human lysosomal protein and methods of its use |
| US20020006400A1 (en) * | 2000-05-11 | 2002-01-17 | Peter Lobel | Recombinant human CLN2 protein and methods of its production and use |
| US7442372B2 (en) | 2003-08-29 | 2008-10-28 | Biomarin Pharmaceutical Inc. | Delivery of therapeutic compounds to the brain and other tissues |
| LT2588130T (lt) * | 2010-06-25 | 2016-12-12 | Shire Human Genetic Therapies, Inc. | Terapinės priemonės pristatymas cns |
| US20140377244A1 (en) | 2011-12-23 | 2014-12-25 | Shire Human Genetic Therapies, Inc. | Stable formulations for cns delivery of arylsulfatase a |
| TWI752907B (zh) * | 2015-05-08 | 2022-01-21 | 美商拜奧馬林製藥公司 | 用於治療cln2疾病之tpp1調配物及方法 |
| KR102738860B1 (ko) * | 2015-10-23 | 2024-12-04 | 유니버시티 오브 아이오와 리써치 파운데이션 | 리소좀 축적 질환 (lsd)을 갖는 포유동물의 치료 방법에 사용하기 위한 aav 입자를 포함하는 약제학적 조성물 |
| BR112021009370A2 (pt) * | 2018-11-14 | 2021-08-17 | Regenxbio Inc. | método de tratamento da doença de batten cln2, composição farmacêutica e kit |
-
2020
- 2020-08-31 PT PT207714080T patent/PT4021575T/pt unknown
- 2020-08-31 SM SM20240315T patent/SMT202400315T1/it unknown
- 2020-08-31 PL PL20771408.0T patent/PL4021575T3/pl unknown
- 2020-08-31 HU HUE20771408A patent/HUE067135T2/hu unknown
- 2020-08-31 AU AU2020336984A patent/AU2020336984B2/en active Active
- 2020-08-31 MX MX2022002451A patent/MX2022002451A/es unknown
- 2020-08-31 SI SI202030455T patent/SI4021575T1/sl unknown
- 2020-08-31 HR HRP20240871TT patent/HRP20240871T1/hr unknown
- 2020-08-31 FI FIEP20771408.0T patent/FI4021575T3/fi active
- 2020-08-31 EP EP20771408.0A patent/EP4021575B1/en active Active
- 2020-08-31 AR ARP200102442A patent/AR119871A1/es unknown
- 2020-08-31 LT LTEPPCT/US2020/048704T patent/LT4021575T/lt unknown
- 2020-08-31 DK DK20771408.0T patent/DK4021575T3/da active
- 2020-08-31 BR BR112022003598A patent/BR112022003598A2/pt unknown
- 2020-08-31 TW TW109129724A patent/TW202122106A/zh unknown
- 2020-08-31 CN CN202080068971.3A patent/CN114828960A/zh active Pending
- 2020-08-31 EP EP24177169.0A patent/EP4438120A3/en active Pending
- 2020-08-31 JP JP2022513165A patent/JP2022546042A/ja active Pending
- 2020-08-31 US US17/638,029 patent/US20220273775A1/en active Pending
- 2020-08-31 KR KR1020227010387A patent/KR20220054375A/ko active Pending
- 2020-08-31 HR HRP20220370AA patent/HRP20220370A1/hr not_active Application Discontinuation
- 2020-08-31 ES ES20771408T patent/ES2987156T3/es active Active
- 2020-08-31 CA CA3152521A patent/CA3152521A1/en active Pending
- 2020-08-31 WO PCT/US2020/048704 patent/WO2021042020A1/en not_active Ceased
- 2020-08-31 RS RS20240792A patent/RS65763B1/sr unknown
-
2022
- 2022-02-21 IL IL290763A patent/IL290763A/en unknown
- 2022-02-28 CL CL2022000496A patent/CL2022000496A1/es unknown
-
2025
- 2025-08-12 JP JP2025134120A patent/JP2025165414A/ja active Pending
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