JP2022526799A5 - - Google Patents

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Publication number
JP2022526799A5
JP2022526799A5 JP2021558657A JP2021558657A JP2022526799A5 JP 2022526799 A5 JP2022526799 A5 JP 2022526799A5 JP 2021558657 A JP2021558657 A JP 2021558657A JP 2021558657 A JP2021558657 A JP 2021558657A JP 2022526799 A5 JP2022526799 A5 JP 2022526799A5
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JP
Japan
Prior art keywords
amino acid
pharmaceutical composition
acid sequence
seq
polypeptide
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Application number
JP2021558657A
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English (en)
Japanese (ja)
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JP7715635B2 (ja
JP2022526799A (ja
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Priority claimed from PCT/US2020/026669 external-priority patent/WO2020206320A1/en
Publication of JP2022526799A publication Critical patent/JP2022526799A/ja
Publication of JP2022526799A5 publication Critical patent/JP2022526799A5/ja
Priority to JP2025120522A priority Critical patent/JP2025148550A/ja
Application granted granted Critical
Publication of JP7715635B2 publication Critical patent/JP7715635B2/ja
Active legal-status Critical Current
Anticipated expiration legal-status Critical

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JP2021558657A 2019-04-03 2020-04-03 イズロン酸2-スルファターゼを含むタンパク質分子の製剤 Active JP7715635B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2025120522A JP2025148550A (ja) 2019-04-03 2025-07-17 イズロン酸2-スルファターゼを含むタンパク質分子の製剤

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201962828859P 2019-04-03 2019-04-03
US62/828,859 2019-04-03
US201962832032P 2019-04-10 2019-04-10
US62/832,032 2019-04-10
PCT/US2020/026669 WO2020206320A1 (en) 2019-04-03 2020-04-03 Formulations of protein molecules comprising iduronate 2-sulfatase

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2025120522A Division JP2025148550A (ja) 2019-04-03 2025-07-17 イズロン酸2-スルファターゼを含むタンパク質分子の製剤

Publications (3)

Publication Number Publication Date
JP2022526799A JP2022526799A (ja) 2022-05-26
JP2022526799A5 true JP2022526799A5 (cg-RX-API-DMAC10.html) 2023-04-03
JP7715635B2 JP7715635B2 (ja) 2025-07-30

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ID=70457135

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2021558657A Active JP7715635B2 (ja) 2019-04-03 2020-04-03 イズロン酸2-スルファターゼを含むタンパク質分子の製剤
JP2025120522A Pending JP2025148550A (ja) 2019-04-03 2025-07-17 イズロン酸2-スルファターゼを含むタンパク質分子の製剤

Family Applications After (1)

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JP2025120522A Pending JP2025148550A (ja) 2019-04-03 2025-07-17 イズロン酸2-スルファターゼを含むタンパク質分子の製剤

Country Status (11)

Country Link
US (1) US12667606B2 (cg-RX-API-DMAC10.html)
EP (1) EP3947661A1 (cg-RX-API-DMAC10.html)
JP (2) JP7715635B2 (cg-RX-API-DMAC10.html)
KR (1) KR20220004651A (cg-RX-API-DMAC10.html)
CN (1) CN113785054A (cg-RX-API-DMAC10.html)
AU (1) AU2020252554B2 (cg-RX-API-DMAC10.html)
BR (1) BR112021019520A2 (cg-RX-API-DMAC10.html)
CA (1) CA3134538A1 (cg-RX-API-DMAC10.html)
MA (1) MA71657A (cg-RX-API-DMAC10.html)
MX (1) MX2021011612A (cg-RX-API-DMAC10.html)
WO (1) WO2020206320A1 (cg-RX-API-DMAC10.html)

Families Citing this family (12)

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Publication number Priority date Publication date Assignee Title
RS63818B1 (sr) 2017-02-17 2023-01-31 Denali Therapeutics Inc Konstruisani polipeptidi za vezivanje za receptor transferina
BR112020005271A2 (pt) 2017-10-02 2020-09-15 Denali Therapeutics Inc. proteína, polipeptídeo, polinucleotídeo, vetor, célula hospedeira, método para produção de um polipeptídeo, métodos de tratamento de um distúrbio, de diminuição do acúmulo, de monitoramento, de transporte de um agente e de tratamento de um lsd e composição farmacêutica
RS67656B1 (sr) 2018-05-10 2026-02-27 Regeneron Pharma Formulacije koje sadrže visoke koncentracije fuzionog proteina vegf receptora
EP3699923A1 (de) * 2019-02-20 2020-08-26 Fresenius Medical Care Deutschland GmbH Absicherungsmechanismus fuer den betrieb von medizinischen geraeten unter verwendung von verbrauchsgegenstaenden im umfeld einer dialyse
JP7543290B2 (ja) 2019-02-20 2024-09-02 デナリ セラピューティクス インコーポレイテッド 抗trem2抗体及びその使用方法
BR112022012230A2 (pt) 2019-12-23 2022-08-30 Denali Therapeutics Inc Variantes de progranulina
US11124567B2 (en) 2020-01-13 2021-09-21 Denali Therapeutics Inc. Anti-TREM2 antibodies and methods of use thereof
CR20230178A (es) 2020-10-14 2023-07-26 Denali Therapeutics Inc Proteínas de fusión que comprenden enzimas sulfoglucosamina sulfohidrolasa y métodos de estas
US20250018015A1 (en) 2021-07-23 2025-01-16 Denali Therapeutics Inc. Methods for the treatment of hunter syndrome
IL311003A (en) 2021-08-25 2024-04-01 Denali Therapeutics Inc Anti-2HER antibodies and methods of using them
KR20230134822A (ko) * 2022-03-15 2023-09-22 주식회사 녹십자 α-갈락토시다제 A의 융합단백질을 포함하는 액상 제제
TW202542190A (zh) * 2023-12-20 2025-11-01 美商戴納立製藥公司 包含酸性α—葡萄糖苷酶之融合蛋白及其方法

Family Cites Families (15)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
JP2013507131A (ja) 2009-10-09 2013-03-04 アーメイゲン・テクノロジーズ・インコーポレイテッド Cnsにおけるイズロン酸2−スルファターゼ活性を増加させるための方法および組成物
WO2015009052A1 (ko) * 2013-07-16 2015-01-22 일동제약 주식회사 하이브리드 면역글로불린 fc와 효소의 융합단백질
EP3556399A1 (en) 2016-12-19 2019-10-23 Hanmi Pharm. Co., Ltd. Brain targeting long-acting protein conjugate
MX2019007824A (es) 2016-12-28 2019-09-09 Japan Chem Res Preparacion liofilizada.
RS63818B1 (sr) 2017-02-17 2023-01-31 Denali Therapeutics Inc Konstruisani polipeptidi za vezivanje za receptor transferina
KR20190013615A (ko) * 2017-07-28 2019-02-11 한미약품 주식회사 이두로네이트 2-설파타제 결합체
WO2019032955A1 (en) 2017-08-10 2019-02-14 Denali Therapeutics Inc. MODIFIED TRANSFERRIN RECEPTOR BINDING POLYPEPTIDES
BR112020005271A2 (pt) 2017-10-02 2020-09-15 Denali Therapeutics Inc. proteína, polipeptídeo, polinucleotídeo, vetor, célula hospedeira, método para produção de um polipeptídeo, métodos de tratamento de um distúrbio, de diminuição do acúmulo, de monitoramento, de transporte de um agente e de tratamento de um lsd e composição farmacêutica
WO2019246071A1 (en) 2018-06-18 2019-12-26 Denali Therapeutics Inc. Fusion proteins comprising progranulin
EP3894864A2 (en) 2018-12-10 2021-10-20 Denali Therapeutics Inc. Lysosomal storage disorder biomarkers and methods of use thereof
WO2021158986A1 (en) 2020-02-07 2021-08-12 Denali Therapeutics Inc. Methods for the treatment of hunter syndrome
CR20230178A (es) 2020-10-14 2023-07-26 Denali Therapeutics Inc Proteínas de fusión que comprenden enzimas sulfoglucosamina sulfohidrolasa y métodos de estas
US20250018015A1 (en) 2021-07-23 2025-01-16 Denali Therapeutics Inc. Methods for the treatment of hunter syndrome
AR128003A1 (es) 2021-12-17 2024-03-20 Denali Therapeutics Inc PROTEÍNAS DE FUSIÓN QUE COMPRENDEN ENZIMAS DE a-L-IDURONIDASA Y MÉTODOS PARA LAS MISMAS
TW202542190A (zh) 2023-12-20 2025-11-01 美商戴納立製藥公司 包含酸性α—葡萄糖苷酶之融合蛋白及其方法

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