JP2021525083A5 - - Google Patents

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Publication number
JP2021525083A5
JP2021525083A5 JP2020565415A JP2020565415A JP2021525083A5 JP 2021525083 A5 JP2021525083 A5 JP 2021525083A5 JP 2020565415 A JP2020565415 A JP 2020565415A JP 2020565415 A JP2020565415 A JP 2020565415A JP 2021525083 A5 JP2021525083 A5 JP 2021525083A5
Authority
JP
Japan
Prior art keywords
composition
sodium phosphate
methionine
sucrose
composition according
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Granted
Application number
JP2020565415A
Other languages
English (en)
Japanese (ja)
Other versions
JP7497300B2 (ja
JP2021525083A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2019/033983 external-priority patent/WO2019227029A1/en
Publication of JP2021525083A publication Critical patent/JP2021525083A/ja
Publication of JP2021525083A5 publication Critical patent/JP2021525083A5/ja
Priority to JP2024039768A priority Critical patent/JP7832245B2/ja
Application granted granted Critical
Publication of JP7497300B2 publication Critical patent/JP7497300B2/ja
Active legal-status Critical Current
Anticipated expiration legal-status Critical

Links

JP2020565415A 2018-05-25 2019-05-24 酸性スフィンゴミエリナーゼ欠損症を治療するための医薬組成物 Active JP7497300B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2024039768A JP7832245B2 (ja) 2018-05-25 2024-03-14 酸性スフィンゴミエリナーゼ欠損症を治療するための医薬組成物

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201862676525P 2018-05-25 2018-05-25
US62/676,525 2018-05-25
PCT/US2019/033983 WO2019227029A1 (en) 2018-05-25 2019-05-24 Pharmaceutical compositions for treating acid sphingomyelinase deficiency

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2024039768A Division JP7832245B2 (ja) 2018-05-25 2024-03-14 酸性スフィンゴミエリナーゼ欠損症を治療するための医薬組成物

Publications (3)

Publication Number Publication Date
JP2021525083A JP2021525083A (ja) 2021-09-24
JP2021525083A5 true JP2021525083A5 (https=) 2022-05-26
JP7497300B2 JP7497300B2 (ja) 2024-06-10

Family

ID=66912954

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2020565415A Active JP7497300B2 (ja) 2018-05-25 2019-05-24 酸性スフィンゴミエリナーゼ欠損症を治療するための医薬組成物
JP2024039768A Active JP7832245B2 (ja) 2018-05-25 2024-03-14 酸性スフィンゴミエリナーゼ欠損症を治療するための医薬組成物

Family Applications After (1)

Application Number Title Priority Date Filing Date
JP2024039768A Active JP7832245B2 (ja) 2018-05-25 2024-03-14 酸性スフィンゴミエリナーゼ欠損症を治療するための医薬組成物

Country Status (15)

Country Link
US (1) US20210145941A1 (https=)
EP (1) EP3802805A1 (https=)
JP (2) JP7497300B2 (https=)
KR (1) KR102852946B1 (https=)
CN (1) CN112424347A (https=)
AU (2) AU2019275109C1 (https=)
BR (1) BR112020023829A2 (https=)
CA (1) CA3101688A1 (https=)
CO (1) CO2020014399A2 (https=)
IL (1) IL278964A (https=)
MX (2) MX2020012700A (https=)
PY (1) PY1939780A (https=)
SG (1) SG11202011488WA (https=)
UY (1) UY38238A (https=)
WO (1) WO2019227029A1 (https=)

Families Citing this family (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP4284442A4 (en) * 2021-02-01 2025-04-23 The Trustees of The University of Pennsylvania COMPOSITIONS AND METHODS FOR TREATING NIEMANN PICK DISEASE TYPE A
TW202403043A (zh) 2022-03-18 2024-01-16 美商健臻公司 重組人類酸性鞘磷脂酶醫藥組合物及方法

Family Cites Families (15)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US5773278A (en) 1991-05-03 1998-06-30 Mount Sinai Medical Center Acid sphingomyelinase gene
EP1450847B1 (en) 2001-11-13 2010-09-29 Genentech, Inc. APO2 ligand/ TRAIL formulations and uses thereof
EP1638595B1 (en) 2003-06-20 2013-03-20 Ares Trading S.A. Freeze-dried fsh / lh formulations
CN101214249A (zh) * 2003-11-25 2008-07-09 纽约大学西奈山医学院 尼曼-皮克病的基于陪伴分子的治疗
AR059089A1 (es) * 2006-01-20 2008-03-12 Genzyme Corp Administracion intraventricular de una enzima para enfermedades de almacenamiento lisosomal
HRP20120994T1 (hr) 2006-02-07 2012-12-31 Shire Human Genetic Therapies, Inc. Stabilizirana smjesa glukocerebrozidaze
AU2007226582B2 (en) * 2006-03-13 2012-07-05 Revvity Health Sciences, Inc. Substrates and internal standards for mass spectroscopy detection
JP2009530284A (ja) * 2006-03-13 2009-08-27 エンサイシブ・ファーマシューティカルズ・インコーポレイテッド 拡張期心不全を治療するための方法と組成物
JP2012530721A (ja) 2009-06-18 2012-12-06 ワイス・エルエルシー 小モジュール免疫薬のための凍結乾燥製剤
SI3998078T1 (sl) 2009-08-28 2026-02-27 Genzyme Corporation Encimsko nadomestno zdravljenje z naraščajočim odmerkom za zdravljenje pomanjkanja kisle sfingomielinaze
JP6073783B2 (ja) * 2010-06-25 2017-02-01 シャイアー ヒューマン ジェネティック セラピーズ インコーポレイテッド ヘパランn−スルファターゼのcns送達のための方法および組成物
PL3241547T3 (pl) 2011-03-31 2021-02-08 Medy-Tox Inc. Liofilizowany preparat toksyny botulinowej
JP6480154B2 (ja) 2014-11-06 2019-03-06 持田製薬株式会社 エタネルセプトの凍結乾燥製剤
FI126979B (en) * 2016-02-29 2017-09-15 Faron Pharmaceuticals Oy Lyophilized pharmaceutical formulation and its use
KR20250025051A (ko) * 2017-08-24 2025-02-20 사노피 산성 스핑고미엘린분해효소 결핍증 환자에서의 비정상적 골병태의 치료

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