JP2021525083A5 - - Google Patents

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Publication number
JP2021525083A5
JP2021525083A5 JP2020565415A JP2020565415A JP2021525083A5 JP 2021525083 A5 JP2021525083 A5 JP 2021525083A5 JP 2020565415 A JP2020565415 A JP 2020565415A JP 2020565415 A JP2020565415 A JP 2020565415A JP 2021525083 A5 JP2021525083 A5 JP 2021525083A5
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JP
Japan
Prior art keywords
composition
sodium phosphate
methionine
sucrose
composition according
Prior art date
Application number
JP2020565415A
Other languages
English (en)
Japanese (ja)
Other versions
JP2021525083A (ja
JPWO2019227029A5 (https=
JP7497300B2 (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2019/033983 external-priority patent/WO2019227029A1/en
Publication of JP2021525083A publication Critical patent/JP2021525083A/ja
Publication of JPWO2019227029A5 publication Critical patent/JPWO2019227029A5/ja
Publication of JP2021525083A5 publication Critical patent/JP2021525083A5/ja
Priority to JP2024039768A priority Critical patent/JP7832245B2/ja
Application granted granted Critical
Publication of JP7497300B2 publication Critical patent/JP7497300B2/ja
Active legal-status Critical Current
Anticipated expiration legal-status Critical

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JP2020565415A 2018-05-25 2019-05-24 酸性スフィンゴミエリナーゼ欠損症を治療するための医薬組成物 Active JP7497300B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2024039768A JP7832245B2 (ja) 2018-05-25 2024-03-14 酸性スフィンゴミエリナーゼ欠損症を治療するための医薬組成物

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201862676525P 2018-05-25 2018-05-25
US62/676,525 2018-05-25
PCT/US2019/033983 WO2019227029A1 (en) 2018-05-25 2019-05-24 Pharmaceutical compositions for treating acid sphingomyelinase deficiency

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2024039768A Division JP7832245B2 (ja) 2018-05-25 2024-03-14 酸性スフィンゴミエリナーゼ欠損症を治療するための医薬組成物

Publications (4)

Publication Number Publication Date
JP2021525083A JP2021525083A (ja) 2021-09-24
JPWO2019227029A5 JPWO2019227029A5 (https=) 2022-05-26
JP2021525083A5 true JP2021525083A5 (https=) 2022-05-26
JP7497300B2 JP7497300B2 (ja) 2024-06-10

Family

ID=66912954

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2020565415A Active JP7497300B2 (ja) 2018-05-25 2019-05-24 酸性スフィンゴミエリナーゼ欠損症を治療するための医薬組成物
JP2024039768A Active JP7832245B2 (ja) 2018-05-25 2024-03-14 酸性スフィンゴミエリナーゼ欠損症を治療するための医薬組成物

Family Applications After (1)

Application Number Title Priority Date Filing Date
JP2024039768A Active JP7832245B2 (ja) 2018-05-25 2024-03-14 酸性スフィンゴミエリナーゼ欠損症を治療するための医薬組成物

Country Status (15)

Country Link
US (1) US20210145941A1 (https=)
EP (1) EP3802805A1 (https=)
JP (2) JP7497300B2 (https=)
KR (1) KR102852946B1 (https=)
CN (1) CN112424347A (https=)
AU (2) AU2019275109C1 (https=)
BR (1) BR112020023829A2 (https=)
CA (1) CA3101688A1 (https=)
CO (1) CO2020014399A2 (https=)
IL (1) IL278964A (https=)
MX (2) MX2020012700A (https=)
PY (1) PY1939780A (https=)
SG (1) SG11202011488WA (https=)
UY (1) UY38238A (https=)
WO (1) WO2019227029A1 (https=)

Families Citing this family (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
JP2024506860A (ja) * 2021-02-01 2024-02-15 ザ・トラステイーズ・オブ・ザ・ユニバーシテイ・オブ・ペンシルベニア ニーマンピック病a型を治療するための組成物及び方法
TW202403043A (zh) 2022-03-18 2024-01-16 美商健臻公司 重組人類酸性鞘磷脂酶醫藥組合物及方法

Family Cites Families (15)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US5773278A (en) 1991-05-03 1998-06-30 Mount Sinai Medical Center Acid sphingomyelinase gene
ES2351786T3 (es) * 2001-11-13 2011-02-10 Genentech, Inc. Formulaciones con ligando apo2/trail y usos de las mismas.
WO2004112826A1 (en) 2003-06-20 2004-12-29 Ares Trading Sa Freeze-dried fsh / lh formulations
JP2007514661A (ja) * 2003-11-25 2007-06-07 マウント シナイ スクール オブ メディスン オブ ニューヨーク ユニバーシティー ニーマンピック病のシャペロンに基づく治療方法
AR059089A1 (es) 2006-01-20 2008-03-12 Genzyme Corp Administracion intraventricular de una enzima para enfermedades de almacenamiento lisosomal
HRP20120994T1 (hr) 2006-02-07 2012-12-31 Shire Human Genetic Therapies, Inc. Stabilizirana smjesa glukocerebrozidaze
MX2008011842A (es) * 2006-03-13 2008-10-02 Encysive Pharmaceuticals Inc Procedimientos y composiciones para el tratamiento de insuficiencia cardiaca diastolica.
CN102943106A (zh) * 2006-03-13 2013-02-27 珀金埃尔默健康科学股份有限公司 用于质谱法检测的底物和内标
AU2010263058A1 (en) 2009-06-18 2012-01-12 Wyeth Llc Lyophilized formulations for small modular immunopharmaceuticals
SI3998078T1 (sl) 2009-08-28 2026-02-27 Genzyme Corporation Encimsko nadomestno zdravljenje z naraščajočim odmerkom za zdravljenje pomanjkanja kisle sfingomielinaze
NZ605874A (en) 2010-06-25 2015-02-27 Shire Human Genetic Therapies Methods and compositions for cns delivery of heparan n-sulfatase
WO2012134240A2 (ko) * 2011-03-31 2012-10-04 (주)메디톡스 보툴리눔 독소의 동결건조제제
JP6480154B2 (ja) 2014-11-06 2019-03-06 持田製薬株式会社 エタネルセプトの凍結乾燥製剤
FI126979B (en) * 2016-02-29 2017-09-15 Faron Pharmaceuticals Oy Lyophilized pharmaceutical formulation and its use
KR20250025051A (ko) * 2017-08-24 2025-02-20 사노피 산성 스핑고미엘린분해효소 결핍증 환자에서의 비정상적 골병태의 치료

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